- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Inherited Metabolic Storage Diseases
Total 61303 results
-
Baylor College of MedicineThe Methodist Hospital Research InstituteTerminatedInherited Metabolic Storage DiseasesUnited States
-
AldagenTerminatedMucopolysaccharidosis | Inborn Errors of Metabolism | Lysosomal Storage Disorders | Inherited Metabolic Diseases | Peroxisomal Storage DiseasesUnited States
-
Bellicum PharmaceuticalsNo longer availableHurler Syndrome | Inborn Errors of Metabolism | Metachromatic Leukodystrophy | Inherited Metabolic Disorder | Lysosomal Storage DisorderUnited States
-
Academisch Medisch Centrum - Universiteit van Amsterdam...Stichting MetakidsCompletedInherited Metabolic DisordersNetherlands
-
University of FloridaAmicus TherapeuticsCompletedLysosomal Storage Diseases | Glycogen Storage Disease Type II | Pompe DiseaseUnited States
-
Duke UniversityKriya TherapeuticsRecruitingGlycogen Storage Disease VI | GLYCOGEN STORAGE DISEASE IXa1 | GLYCOGEN STORAGE DISEASE IXa2 | Glycogen Storage Disease IXB | Glycogen Storage Disease IXC | GSD 9 (All Subtypes) | GSD 6United States
-
Hospital de Clinicas de Porto AlegreConselho Nacional de Desenvolvimento Científico e Tecnológico; Fundação Médica...CompletedGlycogen Storage Disease Type IBrazil
-
University Medical Center GroningenUniversity of Oxford; University of the Faroe Islands; Stichting Stofwisselkracht and other collaboratorsCompleted
-
Duke UniversitySuspendedLysosomal Storage Diseases | Genetic Disease | Inborn Errors of Metabolism | Glycogen Storage Disease | Storage DiseaseUnited States
-
University Medical Center GroningenUltragenyx Pharmaceutical IncCompletedGlycogen Storage Disease Type IANetherlands
-
Ultragenyx Pharmaceutical IncActive, not recruitingGlycogen Storage Disease Type IAUnited States, Brazil, Canada, Denmark, Germany, Italy, Netherlands, Spain
-
Sanguine BiosciencesTerminatedGlycogen Storage Disease Type IBUnited States
-
Rigshospitalet, DenmarkDanish Research Center for Magnetic ResonanceRecruitingGlycogen Storage Disease | Pompe Disease (Late-onset) | McArdle DiseaseDenmark
-
Amicus TherapeuticsRecruitingGlycogen Storage Disease Type II Infantile OnsetTaiwan, United States, France, Germany, Italy, United Kingdom
-
Duke UniversityCompleted
-
SanofiRecruitingGlycogen Storage Disease Type IIBelgium, United States, China, Germany, Italy, Netherlands, Spain, Taiwan, United Kingdom
-
Taipei Veterans General Hospital, TaiwanUnknownGlycogen Storage Disease Type IITaiwan
-
Taipei Veterans General Hospital, TaiwanNot yet recruitingGlycogen Storage Disease Type II
-
SanofiRecruitingGlycogen Storage Disease Type IIBelgium, United States, Italy, Spain, Taiwan, United Kingdom, Netherlands, France, Germany
-
Genzyme, a Sanofi CompanyActive, not recruitingGlycogen Storage Disease Type IIFrance
-
Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type IIChina
-
Duke UniversityNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)CompletedGlycogen Storage Disease Type IIUnited States
-
Columbia UniversityWithdrawnGlycogen Storage Disease Type IIUnited States
-
Areeg El-GharbawyUltragenyx Pharmaceutical IncCompletedGlycogen Storage Disease Type IUnited States
-
Ultragenyx Pharmaceutical IncCompletedGlycogen Storage Disease Type IANetherlands, United States
-
Ankara UniversityAlexion PharmaceuticalsCompleted
-
Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II Pompe DiseaseUnited States, Belgium, Denmark, France, Germany, Netherlands, United Kingdom
-
Genzyme, a Sanofi CompanyActive, not recruitingGlycogen Storage Disease Type II-Pompe's DiseaseUnited States, France, Japan, Taiwan, United Kingdom
-
Medical University of ViennaRecruitingPompe Disease | McArdle DiseaseAustria
-
CENTOGENE GmbH RostockWithdrawnFructose Metabolism, Inborn Errors | Glycogen Storage Disease Type II | Glycogen Storage Disease | Glycogen Storage Disease Type V | Glycogen Storage Disease Type I | Glycogen Storage Disease Type III | Glycogen Storage Disease Type VII | Glycogen Storage Disease Type IV | Glycogen Storage Disease Type... and other conditionsGermany, India, Sri Lanka
-
Ultragenyx Pharmaceutical IncCompletedGlycogen Storage Disease Type IIIUnited States
-
Rigshospitalet, DenmarkUniversity of Texas Southwestern Medical Center; Groupe Hospitalier Pitie-Salpetriere and other collaboratorsCompletedGlycogen Storage Disease Type VDenmark
-
Centre for Analytical Biochemistry and Biomedical...University of GiessenRecruiting
-
University of FloridaCompleted
-
Eunice Kennedy Shriver National Institute of Child...Completed
-
ModernaTX, Inc.RecruitingGlycogen Storage DiseaseUnited States, Canada
-
Orpha LabsUnknownGlycogen Storage Disease, Type 14Turkey
-
Genzyme, a Sanofi CompanyActive, not recruiting
-
Centre Hospitalier de CayenneCompleted
-
Assistance Publique - Hôpitaux de ParisRecruiting
-
Xinhua Hospital, Shanghai Jiao Tong University...Recruiting
-
Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II;Pompe's DiseaseCzechia, Taiwan, Belgium, Germany, Korea, Republic of, United States, Argentina, Australia, Austria, Brazil, Canada, Denmark, France, Hungary, Italy, Japan, Mexico, Netherlands, Poland, Portugal, Russian Federation, Spain, Switzerland, Turk... and more
-
National Taiwan University HospitalRecruiting
-
National Taiwan University HospitalRecruiting
-
Amicus TherapeuticsActive, not recruitingPompe DiseaseUnited States, Netherlands, United Kingdom, Australia, Germany, New Zealand
-
University of FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development...Completed
-
Asklepios Biopharmaceutical, Inc.Active, not recruiting
-
University of FloridaLacerta TherapeuticsCompletedPompe DiseaseUnited States
-
University of FloridaBioMarin PharmaceuticalCompleted