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Clinical Trials on Inherited Metabolic Storage Diseases in South Africa
Total 2924 results
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Eli Lilly and CompanyCompletedType 2 DiabetesIndia, Mexico, New Zealand, South Africa
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LIB Therapeutics LLCMedpace, Inc.CompletedHeterozygous Familial HypercholesterolemiaUnited States, Israel, Norway, South Africa, Turkey
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Laboratoire français de Fractionnement et de BiotechnologiesLFB USA, Inc.CompletedHemophiliaUnited States, Ukraine, Mexico, Russian Federation, South Africa, Spain
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Genzyme, a Sanofi CompanyApproved for marketingGlycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Glycogenosis 2 | Pompe Disease (Late-Onset)United States
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Novo Nordisk A/SCompletedDiabetes | Diabetes Mellitus, Type 1Germany, South Africa, Russian Federation, Former Serbia and Montenegro, North Macedonia
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Mandos LLCTerminatedNiemann-Pick Disease, Type CCosta Rica
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GlaxoSmithKlineCompletedDiabetes Mellitus, Type 2United States, South Africa
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SanofiCompletedType 2 Diabetes MellitusFrance, Poland, Germany, Italy, Netherlands, Belgium, Denmark, Chile, South Africa, Australia, Argentina
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Novo Nordisk A/SCompletedDiabetes Mellitus, Type 2 | Diabetes | Diabetes Mellitus, Type 1Turkey, Egypt, Philippines, United Arab Emirates, Bangladesh, Colombia, Singapore, South Africa
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University of California, Los AngelesUniversity of Stellenbosch; The ELMA Foundation; Philani Maternal Child Health...CompletedDepression | HIV Infections | Alcohol Drinking | Alcohol; Harmful Use | HIV/AIDS | Depressive Symptoms | Child Development | Alcohol Use Disorder | Stunting | Child Nutrition Disorders | Child Malnutrition | Birth Weight Less Than 10Th PercentileSouth Africa
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PfizerCompletedHemophilia A or BUnited States, Chile, Croatia, Poland, South Africa, Switzerland
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GlaxoSmithKlineCompletedDiphtheria; Haemophilus Influenzae Type b; Hepatitis B; Tetanus; Whole Cell PertussisSouth Africa
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Novo Nordisk A/SCompletedDiabetes | Diabetes Mellitus, Type 1Denmark, Croatia, Australia, South Africa, Italy, Sweden
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SanofiCompletedType 2 Diabetes MellitusSouth Africa, United States, Mexico, United Kingdom
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Sanofi Pasteur, a Sanofi CompanyCompletedPertussis Immunisation | Diphtheria Immunisation | Tetanus Immunisation | Poliomyelitis VaccineSouth Africa
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Aegerion Pharmaceuticals, Inc.FDA Office of Orphan Products DevelopmentCompletedHomozygous Familial HypercholesterolemiaUnited States, Canada, Italy, South Africa
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SanofiCompletedType 2 Diabetes MellitusArgentina, Colombia, Egypt, Hong Kong, India, Indonesia, Lebanon, Malaysia, Peru, Philippines, Saudi Arabia, South Africa, Thailand, Turkey
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University of PennsylvaniaWithdrawn
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Novo Nordisk A/SCompletedDiabetes Mellitus, Type 2 | DiabetesSouth Africa
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncEnrolling by invitationMucopolysaccharidosis III-AUnited States, Australia, Spain
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Novo Nordisk A/SCompletedDiabetes Mellitus, Type 2Bahrain, Egypt, Jordan, Kuwait, Qatar, South Africa, United Arab Emirates
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NovartisCompletedOsteopeniaUnited States, Australia, Canada, Russian Federation, South Africa
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Eli Lilly and CompanyAlkermes, Inc.CompletedDiabetes Mellitus, Type 2United States, Argentina, Portugal, South Africa
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Boehringer IngelheimEli Lilly and CompanyCompletedDiabetes Mellitus, Type 2United States, France, Israel, Mexico, South Africa
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Novartis PharmaceuticalsCompletedA Study of Inclisiran in Participants With Homozygous Familial Hypercholesterolemia (HoFH) (ORION-5)Homozygous Familial HypercholesterolemiaHong Kong, Israel, Russian Federation, Serbia, South Africa, Taiwan, Turkey, Ukraine
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Medexus Pharma, Inc.CompletedHemophilia BTurkey, Brazil, Georgia, Moldova, Republic of, South Africa, Ukraine
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Laboratoire français de Fractionnement et de BiotechnologiesLFB USA, Inc.CompletedA Phase III Study on the Safety, Pharmacokinetics and Efficacy of Coagulation Factor VIIa (PERSEPT2)Hemophilia A With Inhibitors | Hemophilia B With InhibitorsBulgaria, Ukraine, Czechia, United States, Georgia, South Africa
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedMetabolic Diseases | Congenital Abnormalities | Infant, Newborn, Diseases | Genetic Diseases, Inborn | Dyslipidemias | Metabolism, Inborn Errors | Lipid Metabolism Disorders | Hypercholesterolemia | Hyperlipidemias | Hyperlipoproteinemias | Lipid Metabolism, Inborn Errors | Hyperlipoproteinemia Type II | Metabolic... and other conditionsUnited States, Taiwan, Brazil, Canada, South Africa, United Kingdom, Singapore
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University of KwaZuluKing's College London; University of Oxford; University of East Anglia; University... and other collaboratorsRecruitingDepression | Myocardial Infarction | HIV Infections | Stroke | Hypertension | Diabetes Mellitus | AsthmaSouth Africa
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncTerminatedMucopolysaccharidosis III | Sanfilippo Syndrome | MPS IIIA | Sanfilippo AUnited States, Spain, Australia
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PfizerCompletedHemophilia A or BPoland, Switzerland, South Africa, United States, Croatia, Brazil, Chile
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Greenwood Genetic CenterShriners Hospitals for Children; BioMarin PharmaceuticalCompletedMPS IVA | Maroteaux Lamy Syndrome | MPS VI | Morquio Syndrome AUnited States
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Loyola UniversityNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University... and other collaboratorsWithdrawnObesity | Cardiovascular DiseaseSouth Africa, Jamaica, Ghana, United States, Seychelles
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BioMarin PharmaceuticalCompletedMucopolysaccharidosis IVA (Morquio A Syndrome)Australia
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Novartis PharmaceuticalsTerminatedMyelodysplastic Syndrome | Transfusional Iron OverloadSpain, France, Italy, South Africa
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LIB Therapeutics LLCMedpace, Inc.Enrolling by invitationFamilial Hypercholesterolemia | Elevated Cholesterol | Cardiovascular Disease With Mention of ArteriosclerosisUnited States, Israel, Norway, South Africa, Turkey, India
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SanofiCompletedType 2 Diabetes MellitusMexico, South Africa, United States, Mauritius, Spain, Turkey
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CSL BehringTerminatedHemophilia A With Inhibitors | Hemophilia B With InhibitorsGeorgia, Italy, Malaysia, Russian Federation, South Africa, Spain, Thailand, Ukraine, United Kingdom
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PTC TherapeuticsEnrolling by invitationInherited Mitochondrial DiseaseUnited States, France, Spain, United Kingdom, Italy, Poland, Japan
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncActive, not recruitingMucopolysaccharidosis III | Sanfilippo Syndrome | MPS IIIA | Sanfilippo AUnited States, Australia, Spain
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Novartis PharmaceuticalsTerminatedFamilial Chylomicronemia Syndrome (FCS) (HLP Type I)South Africa, Germany, United Kingdom, France, United States, Canada, Netherlands
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LIB Therapeutics LLCCompletedHomozygous Familial HypercholesterolemiaUnited States, Israel, Norway, South Africa, Turkey, India
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Harokopio UniversityCompleted
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Idorsia Pharmaceuticals Ltd.Active, not recruitingFabry DiseaseUnited States, United Kingdom, Norway, Germany, Australia, Canada, Spain, Switzerland, Austria, Belgium, France, Netherlands, Poland
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Harokopio UniversityUniversity of Thessaly; University of Ioannina; University of Patras; CitiesNet; ... and other collaboratorsRecruiting
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Genzyme, a Sanofi CompanyRecruitingGaucher Disease | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency DiseaseHungary, Croatia, United States, Australia, Belgium, Brazil, Bulgaria, Canada, Denmark, Germany, Greece, Hong Kong, India, Indonesia, Italy, Jordan, Korea, Republic of, Kuwait, Lebanon, Malaysia, Pakistan, Philippines, Poland, Saudi Arabia and more
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University of South CarolinaCompletedPhysical Activity | Sedentary Lifestyle | Metabolism Disorder, GlucoseUnited States
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Ionis Pharmaceuticals, Inc.CompletedType 2 Diabetes MellitusCanada, Romania, South Africa
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Idorsia Pharmaceuticals Ltd.CompletedFabry DiseaseUnited States, Spain, Belgium, Australia, Austria, Canada, Germany, Ireland, Italy, Netherlands, Norway, Poland, Switzerland, United Kingdom
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Western Sydney Local Health DistrictCompletedMetabolic Syndrome | HypercholesterolemiaAustralia