- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Laurence-Moon Syndrome in United States
Total 17378 results
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Marshfield Clinic Research FoundationRecruiting
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National Human Genome Research Institute (NHGRI)Terminated
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Rhythm Pharmaceuticals, Inc.CompletedBardet-Biedl Syndrome | POMC DeficiencyNetherlands, United States, Germany, Canada, Puerto Rico, United Kingdom
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Rhythm Pharmaceuticals, Inc.CompletedBardet-Biedl Syndrome | POMC Deficiency Obesity | PCSK1 Deficiency Obesity | LEPR Deficiency ObesityUnited States, Australia, Spain, United Kingdom
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Rhythm Pharmaceuticals, Inc.CompletedBardet Biedl Syndrome (BBS) | Alström Syndrome (AS)United States, United Kingdom, France, Canada, Puerto Rico, Spain
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Lisa Guay WoodfordNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingNephronophthisis | Joubert Syndrome | Bardet Biedl Syndrome | Autosomal Recessive Polycystic Kidney Disease | Congenital Hepatic Fibrosis | Hepato/Renal Fibrocystic Disease | Meckel-Gruber Syndrome | Caroli Syndrome | Oro-Facial-Digital Syndrome Type I | Glomerulocystic Kidney DiseaseUnited States
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Massachusetts General HospitalWithdrawnPremenstrual Dysphoric Disorder | Premenstrual Syndrome | Premenstrual Tension | Menstrual Related Mood DisorderUnited States
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National Institute of Mental Health (NIMH)Recruiting
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National Cancer Institute (NCI)CompletedPreviously Treated Myelodysplastic Syndromes | Secondary Myelodysplastic Syndromes | de Novo Myelodysplastic SyndromesUnited States
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedPreviously Treated Myelodysplastic Syndromes | Secondary Myelodysplastic Syndromes | de Novo Myelodysplastic SyndromesUnited States
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PersImmune, IncUniversity of California, San DiegoUnknown
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Foundation Fighting BlindnessRecruitingRetinitis Pigmentosa | Choroideremia | Usher Syndrome | Batten Disease | Leber Congenital Amaurosis | Goldmann-Favre Syndrome | Kearns-Sayre Syndrome | Retinal Disease | Bardet-Biedl Syndrome | Stargardt Disease | Cone Dystrophy | Retinoschisis | Achromatopsia | Gyrate Atrophy | Eye Diseases Hereditary | Bassen-Kornzweig... and other conditionsUnited States
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Benjamin TomlinsonRecruitingMyelodysplastic Syndromes | MDS/MPN Crossover SyndromesUnited States
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Dana-Farber Cancer InstituteCompletedMyelodysplastic Syndromes (MDS)United States
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Yale UniversityNational Institute of Mental Health (NIMH)CompletedPremenstrual SyndromeUnited States
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University of Colorado, DenverActive, not recruitingHigh Grade Myelodysplastic SyndromesUnited States
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The University of Texas Health Science Center,...RecruitingNeuropsychiatric SyndromesUnited States
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Brian JonasNational Cancer Institute (NCI); Celgene; Pharmacyclics LLC.CompletedPreviously Treated Myelodysplastic Syndrome | Myelodysplastic Syndrome | Therapy-Related Myelodysplastic Syndrome | Secondary Myelodysplastic Syndrome | Refractory High Risk Myelodysplastic SyndromeUnited States
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National Cancer Institute (NCI)CompletedDepressive Disorder | HIV Infections | Acquired Immunodeficiency SyndromeUnited States
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Wake Forest University Health SciencesNational Cancer Institute (NCI)TerminatedPreviously Treated Myelodysplastic SyndromesUnited States
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Rockefeller UniversityCompleted
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Mayo ClinicCompletedCongenital Myasthenic SyndromeUnited States
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University of PennsylvaniaEli Lilly and CompanyCompletedPain | Major Depressive Disorder | Soft Tissue Discomfort SyndromeUnited States
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National Pediatric Neuroinflammation Organization...CompletedOpsoclonus-myoclonus SyndromeUnited States
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University of FloridaCompletedSmall Intestinal Bacterial Overgrowth Syndrome (SIBO) | Small Bowel Bacterial Overgrowth Syndrome (SBBOS)United States
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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National Pediatric Neuroinflammation Organization...Genentech, Inc.CompletedAtaxia | Myoclonus | Opsoclonus-myoclonus Syndrome | OpsoclonusUnited States
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SCRI Development Innovations, LLCNovartis PharmaceuticalsTerminated
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Case Comprehensive Cancer CenterRecruitingMyelodysplastic Syndrome (MDS)United States
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Weill Medical College of Cornell UniversityNovartis PharmaceuticalsCompletedMyelodysplastic Syndrome (MDS)United States
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University of Texas Southwestern Medical CenterChildren's Hospital of PhiladelphiaEnrolling by invitationShort Gut SyndromeUnited States
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The Champ FoundationChildren's Hospital of Philadelphia; The Cleveland ClinicRecruitingPearson Syndrome | Single Large Scale Mitochondrial DNA Deletion Syndromes (SLSMDS)United States
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Thomas Jefferson UniversityAbbVieRecruitingMyelodysplastic Syndrome | Recurrent Myelodysplastic Syndrome | Refractory Myelodysplastic SyndromeUnited States
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Oncology Specialties, AlabamaTerminatedMyelodysplastic Syndrome (MDS)United States
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Ricardo MaselliCatalyst Pharmaceuticals, Inc.No longer availableCongenital Myasthenic SyndromeUnited States
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J&M ShulerUnited States Department of Defense; Nonin MedicalUnknownAcute Compartment SyndromeUnited States
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Arizona Kidney Disease and Hypertension CenterCompletedNephrotic SyndromesUnited States
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Northwestern UniversityCompletedIrritable Bowel Syndrome | SIBO | Bacterial Overgrowth SyndromeUnited States
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University of Wisconsin, MadisonTerminatedCompartment Syndrome of LegUnited States
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Jasper Therapeutics, Inc.Recruiting
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Children's Hospital of PhiladelphiaUniversity of PennsylvaniaRecruiting
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingLeukemia | Myelodysplastic Syndrome | Recurrent Myelodysplastic SyndromeUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingHigh Risk Myelodysplastic SyndromeUnited States
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Hospital for Special Surgery, New YorkRecruitingCRPS (Complex Regional Pain Syndromes)United States
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Scripps HealthJ. Craig Venter InstituteCompletedLi-Fraumeni Syndrome | Hereditary Cancer Syndromes | TP53 Gene Germline Mutation CarrierUnited States
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Peter L GreenbergAmgenCompletedMyelodysplastic Syndromes | Myelodysplastic Syndromes (MDS) | Blood CancerUnited States
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Rockefeller UniversityCompletedParaneoplastic SyndromesUnited States
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Sumitomo Pharma America, Inc.TerminatedAnemia in Myelodysplastic SyndromesUnited States
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Vern C. Juel, M.D.No longer available
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TelikCompletedMyelodysplastic Syndrome (MDS)United States