Clinical Trials on Lipid Metabolism, Inborn Errors in United States
Total 3370 results
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Alexion PharmaceuticalsCompletedHypophosphatasiaUnited States, Canada
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ModernaTX, Inc.RecruitingPropionic AcidemiaUnited States, Canada, United Kingdom
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Cambridge University Hospitals NHS Foundation TrustRecruitingDiabetes | Diet Modification | LipodystrophyUnited Kingdom
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University of Alabama at BirminghamCompletedProteinuria | Fabry DiseaseUnited States, Slovenia
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Baylor Research InstituteCompleted
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Alexion PharmaceuticalsCompletedHypophosphatasia | Bone DiseaseUnited States
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Selecta Biosciences, Inc.National Human Genome Research Institute (NHGRI)SuspendedMethylmalonic Acidemia (MMA)United States
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Alexion PharmaceuticalsApproved for marketingHypophosphatasiaUnited States, France
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Alexion PharmaceuticalsCompletedHypophosphatasia (HPP)United States, Canada
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Alexion PharmaceuticalsCompletedHypophosphatasia (HPP)United States, Canada
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Mayo ClinicRecruitingCongenital Disorder of GlycosylationUnited States
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Tulane UniversityCompletedCongenital Disorders of GlycosylationUnited States
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CENTOGENE GmbH RostockShire Human Genetic Therapies, Inc.CompletedCerebrovascular AccidentAustria, Belgium, Croatia, Finland, France, Georgia, Germany, Ireland, Italy, Malta, Poland, Portugal, Spain, United Kingdom
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisUnited States, Belgium, Brazil, France, Germany, Italy, United Kingdom
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Origin BiosciencesCompletedMolybdenum Cofactor DeficiencyUnited States, Australia, United Kingdom, Germany, Netherlands, Turkey
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Baylor Research InstituteShireUnknownQuality of Life | Renal Insufficiency | Cardiac EventUnited States
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Children's Hospital of Orange CountyActive, not recruitingNeuronal Ceroid-Lipofuscinoses | Neuronal Ceroid Lipofuscinosis CLN2 | Spinocerebellar Ataxia, Autosomal Recessive 7United States
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Chiesi Farmaceutici S.p.A.Active, not recruitingFabry DiseaseBelgium, United States, United Kingdom, Italy, Czechia, Denmark, Norway
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Alexion PharmaceuticalsCompletedHypophosphatasiaUnited States, United Arab Emirates, United Kingdom
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University of Wisconsin, MadisonJohns Hopkins University; National Institute of Diabetes and Digestive and... and other collaboratorsEnrolling by invitationIron Overload | Hemosiderosis | HemochromatosisUnited States
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Alexion PharmaceuticalsCompletedHypophosphatasia (HPP)United States, Canada
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University College, LondonUniversity of Sydney; University Hospital BirminghamUnknownFabry DiseaseUnited Kingdom, Australia
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University of Wisconsin, MadisonNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Stanford...Completed
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Joanne Kurtzberg, MDAldagenWithdrawnLysosomal Storage Diseases | Inborn Errors of MetabolismUnited States
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Grace Science, LLCRecruitingNGLY1 DeficiencyUnited States
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Genzyme, a Sanofi CompanyCompletedFabry DiseaseUnited States, United Kingdom, Canada, Hungary, Poland, Czech Republic
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National Human Genome Research Institute (NHGRI)RecruitingMitochondrial Disorders | Leigh Disease | Oxidative Phosphorylation Deficiencies | Electron Transport Chain Disorders, MitochondrialUnited States
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Dr. Schär AG / SPACompletedPhenylketonurias | Inborn Errors of Metabolism | Metabolic Disease | PKUUnited Kingdom
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CENTOGENE GmbH RostockCompletedFabry Disease | Anderson-Fabry Disease | Fabry´s DiseaseArgentina, Belgium, Croatia, Czechia, Denmark, France, Germany, United Kingdom
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Augusta UniversityCompletedGlucose Intolerance | Fructose Intolerance | Lactose Intolerance | Small Intestinal Bacterial OvergrowthUnited States
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SanofiRecruitingFabry DiseaseItaly, United States, Austria, China, Czechia, Denmark, France, Germany, Greece, Japan, Korea, Republic of, Netherlands, Norway, Spain, Taiwan, Turkey, United Kingdom, Canada, Poland
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Vanderbilt University Medical CenterHarvard UniversityRecruitingAlbright Hereditary Osteodystrophy | PseudohypoparathyroidismUnited States
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University of CambridgeSanofiRecruiting
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Mayo ClinicCompletedHemochromatosisUnited States
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AlexionRecruiting
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Sheffield Teaching Hospitals NHS Foundation TrustNational Institute for Health Research, United Kingdom; Alexion Pharmaceuticals...Completed
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Genzyme, a Sanofi CompanyRecruitingFabry DiseaseCroatia, United States, Argentina, Australia, Belgium, Bulgaria, Canada, Germany, Hong Kong, India, Indonesia, Korea, Republic of, Kuwait, Malaysia, Philippines, Poland, Romania, Singapore, Slovakia, Taiwan, Thailand, United Kingdom, Vietn... and more
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Dr. Schär AG / SPACompletedPhenylketonurias | Inborn Errors of Metabolism | Metabolic Disease | PKUUnited Kingdom
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Sheffield Teaching Hospitals NHS Foundation TrustUniversity of SheffieldActive, not recruiting
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Lumos DiagnosticsAptatek BiosciencesRecruiting
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Emory UniversityBioMarin PharmaceuticalRecruitingPhenylketonuriasUnited States
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Rubius TherapeuticsTerminated
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Boston Children's HospitalBrigham and Women's HospitalCompletedPhenylketonuriaUnited States
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Boston Children's HospitalBeth Israel Deaconess Medical Center; Brigham and Women's HospitalCompletedPhenylketonuriaUnited States
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University of Missouri-ColumbiaBioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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Emory UniversityAtlanta Clinical and Translational Science InstituteCompleted
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The University of Texas Health Science Center,...BioMarin PharmaceuticalTerminatedPhenylketonuria | HyperphenylalaninemiaUnited States
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Boston Children's HospitalBeth Israel Deaconess Medical Center; Brigham and Women's HospitalCompletedPhenylketonuriaUnited States
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The University of Texas Health Science Center,...BioMarin PharmaceuticalCompleted
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Emory UniversityTerminated