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Clinical Trials on Lipid Storage Disease in Portugal
Total 2758 results
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Universidade do PortoHospital da Luz, Lisboa; Hospital Pedro Hispano; Centro Hospitalar de Leiria; Centro... and other collaboratorsRecruitingFabry DiseasePortugal
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Escola Superior de Tecnologia da Saúde do PortoCompleted
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CENTOGENE GmbH RostockShire Human Genetic Therapies, Inc.CompletedFabry Disease | Cerebrovascular AccidentAustria, Croatia, France, Germany, Poland, Portugal, Georgia
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Hospital Pedro HispanoNorthwestern UniversityCompleted
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ShireTerminatedFabry DiseaseSpain, Greece, Germany, Portugal, Canada, Finland, Poland, Sweden
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Genzyme, a Sanofi CompanyCompletedGaucher DiseaseUnited States, Sweden, India, Netherlands, Austria, Japan, China, Serbia, France, Croatia, Australia, Portugal, Canada, Brazil, Greece, Romania, Russian Federation
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Unidade Local de Saúde de Matosinhos, EPERecruitingPalliative Care | End Stage Liver DIseasePortugal
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Idorsia Pharmaceuticals Ltd.CompletedGM2 Gangliosidosis | GM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff Disease | Gaucher Disease, Type 2 | AB Variant Gangliosidosis GM2United States, Spain, Germany, Italy, Belgium, Brazil, France, Portugal, Switzerland, United Kingdom
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Genzyme, a Sanofi CompanyActive, not recruitingTay-Sachs Disease | Sandhoff DiseaseUnited States, Argentina, Czechia, Portugal, Russian Federation, Turkey, United Kingdom, Brazil, France, Germany, Italy, Japan, Spain
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Amicus TherapeuticsRecruitingFabry DiseaseSpain, United States, Japan, Australia, France, Portugal
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AlexionRecruitingWolman Disease | Cholesterol Ester Storage Disease | Lysosomal Acid Lipase Deficiency | Acid Cholesteryl Ester Hydrolase Deficiency, Type 2 | Acid Lipase Deficiency | LIPA Deficiency | LAL-DeficiencyFrance, Belgium, United States, Spain, Germany, Greece, Israel, Italy, Slovenia, United Kingdom, Brazil, Canada, Denmark, Australia, Croatia, Czechia, Ireland, Mexico, Netherlands, Poland, Portugal, Saudi Arabia
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CENTOGENE GmbH RostockShire Human Genetic Therapies, Inc.CompletedCerebrovascular AccidentAustria, Belgium, Croatia, Finland, France, Georgia, Germany, Ireland, Italy, Malta, Poland, Portugal, Spain, United Kingdom
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University of Trás-os-Montes and Alto DouroCompletedLipid Metabolism Disorders | Sarcopenia | Osteoporosis | Overweight and Obesity | Personal Satisfaction | Hypertension With Complications and Secondary HypertensionPortugal
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SanofiCompletedSphingomyelin LipidosisItaly, Czechia, Belgium, France, Portugal, Turkey, United States, Argentina, Brazil, Chile, Germany, Romania, Spain
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Associação para o Desenvolvimento do Centro Académico...European Regional Development Fund; Loulé Municipal Council; Albufeira Municipal... and other collaboratorsRecruitingHypertension | Osteoarthritis, Knee | Dyslipidemias | Type 2 Diabetes | Myocardial Infarction, Acute | Smoking HabitPortugal
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisUnited States, Argentina, Australia, Belgium, Brazil, Bulgaria, Chile, France, Germany, Italy, Japan, Netherlands, Portugal, Spain, Tunisia, Turkey, United Kingdom
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Genzyme, a Sanofi CompanyRecruitingFabry DiseaseCroatia, United States, Argentina, Australia, Belgium, Bulgaria, Canada, Germany, Hong Kong, India, Indonesia, Korea, Republic of, Kuwait, Malaysia, Philippines, Poland, Romania, Singapore, Slovakia, Taiwan, Thailand, United Kingdom, Vietn... and more
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Inventiva PharmaCompletedMucopolysaccharidosis VIUnited Kingdom, France, Germany, Portugal
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Genzyme, a Sanofi CompanyRecruitingGaucher Disease | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency DiseaseHungary, Croatia, United States, Australia, Belgium, Brazil, Bulgaria, Canada, Denmark, Germany, Greece, Hong Kong, India, Indonesia, Italy, Jordan, Korea, Republic of, Kuwait, Lebanon, Malaysia, Pakistan, Philippines, Poland, Saudi Arabia and more
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BioMarin PharmaceuticalTerminatedLate-onset Pompe DiseaseUnited States, United Kingdom, Germany, France, Italy, Portugal, Belgium, Netherlands
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SanofiTerminatedObesity | DyslipidemiasGermany, Netherlands, Turkey, Slovakia, United Kingdom, Finland, Hungary, Ireland, Italy, Norway, Greece, Sweden, Czech Republic, Portugal, Switzerland
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BioMarin PharmaceuticalCompletedMucopolysaccharidosis VI | Maroteaux-Lamy SyndromeUnited States, Portugal, France
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University College, LondonEuropean UnionCompletedEarly-Stage Breast CarcinomaUnited Kingdom, Netherlands, Portugal
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University of UlmUniversity of Pisa; IRCCS Azienda Ospedaliero-Universitaria di Bologna; Medical... and other collaboratorsRecruitingLipodystrophy Acquired | Lipodystrophy CongenitalAustria, France, Germany, Hungary, Italy, Portugal, Spain, Netherlands, Russian Federation, Slovenia, Switzerland, Turkey, United Kingdom
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Universidade do PortoFundação para a Ciência e a Tecnologia; Administração Regional de Saúde do... and other collaboratorsCompletedOverweight and ObesityPortugal
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Ionis Pharmaceuticals, Inc.Active, not recruitingFamilial Chylomicronemia SyndromeSpain, United Kingdom, France, Canada, United States, Italy, Netherlands, Norway, Portugal, Slovakia, Sweden
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Aveiro UniversityFundação para a Ciência e a TecnologiaCompletedChronic Obstructive Pulmonary Disease (COPD)Portugal
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Centro Hospitalar Tondela-ViseuRecruitingInflammatory Bowel DiseasesPortugal
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University of CoimbraCompletedCoronary Artery DiseasePortugal
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Portuguese Society of CardiologyPortuguese Association of Interventional CardiologyUnknown
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Aveiro UniversityFundação para a Ciência e a TecnologiaNot yet recruitingChronic Respiratory DiseasePortugal
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Aveiro UniversityPrograma Operacional Inclusão Social e Emprego (POISE); Programa Operacional... and other collaboratorsCompletedLung Diseases | Chronic Obstructive Pulmonary Disease | Pulmonary Disease | Interstitial Lung Disease | Chronic Respiratory DiseasePortugal
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Aveiro UniversityCentro Hospitalar do Baixo VougaRecruitingChronic Obstructive Pulmonary Disease | Interstitial Lung DiseasePortugal
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Universidade do PortoUniversity of Oxford; University of EdinburghNot yet recruitingCoronary Artery Disease | Coronary AtherosclerosesPortugal
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Campus Neurológico SéniorCompletedParkinson DiseasePortugal
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Universidade Católica PortuguesaAssociação para o Desenvolvimento do Centro Académico de Investigação e Formação...Active, not recruitingCardiovascular Disease RiskPortugal
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Polytechnic Institute of PortoNippon Gases PortugalRecruiting
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Centro Hospitalar de Lisboa CentralNot yet recruitingParkinson Disease | Botulinum Toxin | Freezing of GatePortugal
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Centro Hospitalar do PortoUniversity of Trás-os-Montes and Alto Douro; Foundation for Science and Technology... and other collaboratorsRecruitingIntermittent Claudication | Peripheral Arterial Disease (PAD)Portugal
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University of CoimbraCompletedInflammatory Bowel DiseasesPortugal
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University of CoimbraCentro Hospitalar e Universitário de Coimbra, E.P.E.CompletedInflammatory Bowel DiseasesPortugal
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Ultragenyx Pharmaceutical IncCompletedMucopolysaccharidosis | Sly Syndrome | Mucopolysaccharidosis VII | MPS VIISpain, United States, Portugal
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Hospital Sao JoaoUnknownChronic Obstructive Pulmonary Disease | Obesity Hypoventilation Syndrome | Neuromuscular Disease | Chest Wall DisordersPortugal
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Universidade do PortoUnknownAsthma | Lung Disease | GenotoxicityPortugal
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Universidade do PortoFundação para a Ciência e a Tecnologia; Centro Hospitalar De São João, E.P.E.UnknownObesity | Metabolic Bone Disease | Accidental FallsPortugal
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Portuguese Society of CardiologyAbbott Medical Devices; Portuguese Association of Interventional CardiologyCompletedCoronary Artery DiseasePortugal
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Portuguese Society of CardiologyUnknown
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II;Pompe's DiseaseCzechia, Taiwan, Belgium, Germany, Korea, Republic of, United States, Argentina, Australia, Austria, Brazil, Canada, Denmark, France, Hungary, Italy, Japan, Mexico, Netherlands, Poland, Portugal, Russian Federation, Spain, Switzerland, Turk... and more
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Ultragenyx Pharmaceutical IncCompletedMucopolysaccharidosis | Sly Syndrome | Mucopolysaccharidosis VII | MPS VIIUnited States, Brazil, Mexico, Portugal