Clinical Trials on Lysosomal Storage Diseases, Nervous System
Total 194036 results
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AVROBIOTerminatedType 1 Gaucher DiseaseUnited States, Canada
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Shaare Zedek Medical CenterCompletedGaucher Disease, Type 1Israel
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Ari ZimranPfizerActive, not recruitingGaucher Disease, Type 3Israel, Turkey, India
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CEN BiotechTakeda; BioClinica, Inc.Completed
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ShireCompletedGaucher Disease, Type 1United States, Israel, Argentina, India, Korea, Republic of, Paraguay, Poland, Russian Federation, Spain, Tunisia, United Kingdom
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ShireCompletedGaucher DiseaseUnited States, Israel, United Kingdom, Poland, Spain
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ShireApproved for marketingGaucher Disease, Type 1United States
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University Research Foundation for Lysosomal Storage...University of PittsburghCompletedGaucher DiseaseUnited States
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Shaare Zedek Medical CenterCompletedGaucher Disease Type 1Israel
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Nantes University HospitalCompletedPatients With Gaucher's DiseaseFrance
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National Institute of Mental Health (NIMH)Completed
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Massachusetts General HospitalRecruiting
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CENTOGENE GmbH RostockWithdrawnSkeletal Abnormalities | Psychomotor RetardationGermany, India, Sri Lanka, Egypt
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University of PennsylvaniaPassage Bio, Inc.RecruitingGM1 GangliosidosisUnited States, Turkey, Brazil, Canada, United Kingdom
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CENTOGENE GmbH RostockCompletedLysosomal Storage Diseases | Sphingolipidoses | Gaucher DiseaseAlbania, Greece, India, Israel, Morocco, Pakistan, Spain
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SanofiCompletedPompe Disease | Mucopolysaccharidosis Type I (MPS I)Italy
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LYSOGENETerminatedGM1 GangliosidosisUnited Kingdom, United States, France
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LYSOGENECasimir, LLC; Cure GM1 FoundationCompleted
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He HuangLingyi Biotech Co., Ltd.Recruiting
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CANbridge (Suzhou) Bio-pharma Co., Ltd.RecruitingGaucher Disease, Type 1 | Gaucher Disease, Type 3China
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Cambridge University Hospitals NHS Foundation TrustMedical Research Council; National Institute for Health Research, United KingdomRecruitingGaucher Disease, Type III | Gaucher Disease, Type IUnited Kingdom
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SanofiCompleted
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Shaare Zedek Medical CenterCompleted
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Amicus TherapeuticsCompletedGaucher Disease | Gaucher Disease, Type 1 | Type 1 Gaucher DiseaseUnited States
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Amicus TherapeuticsCompletedGaucher Disease | Gaucher Disease, Type 1 | Type 1 Gaucher DiseaseUnited Kingdom, Israel, South Africa, United States
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CENTOGENE GmbH RostockWithdrawnFructose Metabolism, Inborn Errors | Glycogen Storage Disease Type II | Glycogen Storage Disease | Glycogen Storage Disease Type V | Glycogen Storage Disease Type I | Glycogen Storage Disease Type III | Glycogen Storage Disease Type VII | Glycogen Storage Disease Type IV | Glycogen Storage Disease Type... and other conditionsGermany, India, Sri Lanka
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Centre Hospitalier Universitaire de NiceCompletedPompe's DiseaseFrance
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Lysosomal and Rare Disorders Research and Treatment...UnknownGaucher Disease Type 1United States
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National Center for Research Resources (NCRR)University of PittsburghUnknownGaucher's DiseaseUnited States
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Genzyme, a Sanofi CompanyCompletedPompe Disease (Late-onset) | Glycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Glycogenosis 2United States, France, Netherlands
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SanofiCompleted
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AVROBIOWithdrawn
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Amicus TherapeuticsCompletedGaucher Disease | Gaucher Disease, Type 1 | Type 1 Gaucher DiseaseUnited Kingdom, United States
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State University of New York at BuffaloEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruiting
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National Institute of Neurological Disorders and...CompletedLysosomal Storage DiseaseUnited States, France, Israel, Netherlands
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Assiut UniversityNot yet recruiting
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Tehran University of Medical SciencesMashhad University of Medical Sciences; Kashan University of Medical SciencesRecruitingEffects of Miglustat Therapy on Infantile Type of Sandhoff and Taysachs Diseases (EMTISTD) (EMTISTD)Supportive Care | GM2 GangliosidosisIran, Islamic Republic of
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SanofiCompletedGaucher Disease | SplenomegalyFrance
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The Hospital for Sick ChildrenActelionCompletedGangliosidoses GM2Canada
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Rambam Health Care CampusUnknown
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National Institute of Neurological Disorders and...CompletedGaucher's DiseaseUnited States
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The Hospital for Sick ChildrenCompletedGangliosidoses, GM2 | Tay-Sachs Disease | Sandhoff DiseaseCanada
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National Center for Research Resources (NCRR)National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University...Completed
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National Institute of Arthritis and Musculoskeletal...CompletedMyositis | Dermatomyositis | Polymyositis | Glycogen Storage Disease Type II | Glycogen Storage Disease Type VIIUnited States
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Forge Biologics, IncNot yet recruitingKrabbe DiseaseUnited States
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Forge Biologics, IncActive, not recruiting
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University of PittsburghNational Institute of Neurological Disorders and Stroke (NINDS)Active, not recruiting
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AldagenTerminatedMucopolysaccharidosis | Inborn Errors of Metabolism | Lysosomal Storage Disorders | Inherited Metabolic Diseases | Peroxisomal Storage DiseasesUnited States
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NYU Langone HealthGenzyme, a Sanofi CompanyCompleted
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Freeline TherapeuticsRecruitingGaucher Disease, Type 1Spain, Israel, United States, United Kingdom, Brazil, Germany, Paraguay