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Clinical Trials on Macular Dystrophy With Flecks, Type 1 in Canada
Total 37 results
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McMaster UniversityCompletedMuscular Dystrophies | Myotonic Dystrophy 1Canada
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Vertex Pharmaceuticals IncorporatedRecruitingMyotonic Dystrophy Type 1 (DM1)Canada
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Université du Québec à ChicoutimiRecruitingMyotonic Dystrophy Type 1 (DM1)Canada
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Élise DuchesneFondation du Grand défi Pierre LavoieCompletedMyotonic Dystrophy 1Canada
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Université de SherbrookeRare Disease FoundationCompletedMyotonic Dystrophy 1Canada
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Cynthia GagnonFondation du Grand défi Pierre LavoieCompletedEffects of a Multiple Component Training Program on Muscles in Adults With Myotonic Dystrophy Type 1Myotonic Dystrophy 1Canada
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Laval UniversityCompleted
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Avidity Biosciences, Inc.RecruitingPhase 1/2 Study of AOC 1020 in Adults With Facioscapulohumeral Muscular Dystrophy (FSHD) (FORTITUDE)Muscular Dystrophies | Muscular Dystrophy, Facioscapulohumeral | FSHD | Facio-Scapulo-Humeral Dystrophy | FMD | Facioscapulohumeral Muscular Dystrophy 1 | FSHD2 | FSHD1 | FMD2 | Fascioscapulohumeral Muscular Dystrophy | Fascioscapulohumeral Muscular Dystrophy Type 1 | Fascioscapulohumeral Muscular Dystrophy... and other conditionsUnited States, United Kingdom, Canada
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PepGen IncRecruitingMyotonic Dystrophy 1United States, Canada
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Centre Hospitalier Universitaire de NiceRecruitingFacioscapulohumeral Muscular Dystrophy 1France, Canada
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Virginia Commonwealth UniversityRadboud University Medical Center; University of California, Los Angeles; University... and other collaboratorsRecruitingMyotonic Dystrophy 1United States, Netherlands, United Kingdom, New Zealand, Germany, Italy, Canada, France
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McMaster UniversityNot yet recruiting
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McGill UniversityJuvenile Diabetes Research Foundation; Canadian Institutes of Health Research... and other collaboratorsEnrolling by invitationType 1 Diabetes Mellitus With HypoglycemiaCanada
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Harmony Biosciences, LLCActive, not recruitingMyotonic Dystrophy 1 | Excessive Daytime SleepinessUnited States, Canada
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Zucara Therapeutics Inc.RecruitingType 1 Diabetes Mellitus With HypoglycemiaUnited States, Canada
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Université de SherbrookeCentre de recherche du Centre hospitalier universitaire de Sherbrooke; Interdisciplinary... and other collaboratorsEnrolling by invitationUrinary Incontinence | Myotonic Dystrophy Type 1Canada
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ViaCyteCalifornia Institute for Regenerative Medicine (CIRM); Horizon 2020 - European...CompletedType 1 Diabetes Mellitus With HypoglycemiaUnited States, Canada, Belgium
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University Medical Center GroningenJuvenile Diabetes Research Foundation; Lexicon PharmaceuticalsNot yet recruitingType 1 Diabetes Mellitus With Diabetic NephropathyNetherlands, United States, Canada, Denmark, Finland
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National Cancer Institute (NCI)CompletedParents of Children With Cancer | Parents of Children With NF1 | Parents of Children With Neurofibromatosis Type IUnited States, Canada
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Regeneron PharmaceuticalsBayerActive, not recruitingType 2 Diabetes Mellitus | Diabetic Macular Edema | Type 1 Diabetes MellitusUnited States, Puerto Rico, Japan, United Kingdom, Canada, Czechia, Germany, Hungary
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Pharvaris Netherlands B.V.Active, not recruitingHereditary Angioedema | Hereditary Angioedema Type I | Hereditary Angioedema Type II | Hereditary Angioedema Types I and II | Hereditary Angioedema Attack | Hereditary Angioedema With C1 Esterase Inhibitor Deficiency | Hereditary Angioedema - Type 1 | Hereditary Angioedema - Type 2 | C1 Esterase Inhibitor... and other conditionsUnited States, Poland, Germany, Austria, Bulgaria, Canada, Ireland, Italy, United Kingdom
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Pharvaris Netherlands B.V.CompletedHereditary Angioedema | Hereditary Angioedema Type I | Hereditary Angioedema Type II | Hereditary Angioedema Types I and II | Hereditary Angioedema Attack | Hereditary Angioedema With C1 Esterase Inhibitor Deficiency | Hereditary Angioedema - Type 1 | Hereditary Angioedema - Type 2 | C1 Esterase Inhibitor... and other conditionsBulgaria, United States, Spain, Israel, Germany, Canada, Czechia, France, Hungary, Italy, Netherlands, Poland, United Kingdom
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National Cancer Institute (NCI)Active, not recruitingChronic Myelomonocytic Leukemia | Myelodysplastic Syndrome | Myelodysplastic Syndrome With Excess Blasts | Chronic Myelomonocytic Leukemia-1 | Chronic Myelomonocytic Leukemia-2 | Myelodysplastic Syndrome With Excess Blasts-1 | Myelodysplastic Syndrome/Acute Myeloid LeukemiaCanada, United States
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Pharvaris Netherlands B.V.RecruitingHereditary Angioedema | Hereditary Angioedema Type I | Hereditary Angioedema Type II | Hereditary Angioedema Types I and II | Hereditary Angioedema Attack | Hereditary Angioedema With C1 Esterase Inhibitor Deficiency | Hereditary Angioedema - Type 1 | Hereditary Angioedema - Type 2 | C1 Esterase Inhibitor... and other conditionsUnited States, Bulgaria, Czechia, Hungary, Spain, France, Germany, Poland, Canada, Israel
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Canadian Medical and Surgical Knowledge Translation...Unity Health Toronto; Western University, CanadaCompletedCardiovascular Diseases | Diabetes | Ischemic Stroke | Peripheral Vascular Diseases | Type 1 Diabetes | Type 2 Diabetes | Ischemic Heart DiseaseCanada
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Ultragenyx Pharmaceutical IncTerminatedHereditary Inclusion Body Myopathy | GNE Myopathy | Inclusion Body Myopathy 2 | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing MyopathyCanada, United States, Bulgaria
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Lawson Health Research InstituteThe Ottawa Hospital; Hamilton Health Sciences Corporation; Dalhousie University; Niagara Health SystemActive, not recruitingMultiple Myeloma in Relapse | Multiple Myeloma With Failed Remission | Multiple Myeloma Stage I | Multiple Myeloma Progression | Multiple Myeloma Stage II | Multiple Myeloma Stage IIICanada
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Ultragenyx Pharmaceutical IncCompletedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka TypeUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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University of British ColumbiaVancouver Coastal Health Research Institute; Genome British ColumbiaRecruitingAcute Coronary Syndrome | Familial Hypercholesterolemia | STEMI | NSTEMI - Non-ST Segment Elevation MI | Familial Hypercholesterolemia - Heterozygous | Familial Hypercholesterolemia Due to Genetic Defect of Apolipoprotein B | Familial Hypercholesterolemia Due to Heterozygous LDL Receptor Mutation and other conditionsCanada
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Ultragenyx Pharmaceutical IncTerminatedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing MyopathyUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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LMC Diabetes & Endocrinology Ltd.CompletedDiabetes Mellitus, Type 2 | Diabetes Mellitus, Type 1 | Onychomycosis | Foot Deformities | Neuropathy, Diabetic | Foot Ulcer, Diabetic | Hyperkeratosis | OnychauxisCanada
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Spanish Society of CardiologyRecruitingAdherence, Medication | Gender Differences | Therapeutic Adherence | Type 1 Acute Myocardial InfarctionSpain
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National Cancer Institute (NCI)CompletedRecurrent Adult Acute Myeloid Leukemia | Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue | Nodal Marginal Zone B-cell Lymphoma | Recurrent Adult Burkitt Lymphoma | Recurrent Adult Diffuse Large Cell Lymphoma | Recurrent Adult Diffuse Mixed Cell Lymphoma | Recurrent... and other conditionsCanada
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Ixaka LtdAndalusian Network for Design and Translation of Advanced TherapiesTerminatedCardiovascular Disease | Diabetes Mellitus, Type 2 | Diabetes Mellitus, Type 1 | Critical Limb Ischemia (CLI) | Peripheral Arterial Disease (PAD) | Diabetes Mellitus (DM)Spain, Czechia, Portugal, Hungary, Germany, Poland
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National Cancer Institute (NCI)CompletedIris Melanoma | Stage IV Uveal Melanoma | Medium/Large Size Posterior Uveal Melanoma | Recurrent Uveal Melanoma | Ocular Melanoma With Extraocular Extension | Small Size Posterior Uveal MelanomaUnited States, Canada
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National Cancer Institute (NCI)CompletedExtranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue | Nodal Marginal Zone B-cell Lymphoma | Recurrent Adult Burkitt Lymphoma | Recurrent Adult Diffuse Large Cell Lymphoma | Recurrent Adult Diffuse Mixed Cell Lymphoma | Recurrent Adult Diffuse Small Cleaved Cell Lymphoma and other conditionsUnited States, Canada
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National Cancer Institute (NCI)CompletedUnspecified Childhood Solid Tumor, Protocol Specific | Chronic Myelomonocytic Leukemia | Juvenile Myelomonocytic Leukemia | Recurrent Grade 1 Follicular Lymphoma | Recurrent Grade 2 Follicular Lymphoma | Recurrent Grade 3 Follicular Lymphoma | Recurrent Mantle Cell Lymphoma | Recurrent Marginal Zone... and other conditionsUnited States, Canada