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- US Clinical Trials Registry
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Clinical Trials on Myotonic Dystrophy 1 in United States
Total 3404 results
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Eledon PharmaceuticalsWithdrawnBrittle Type 1 Diabetes MellitusUnited States
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Kevin FlaniganMuscular Dystrophy AssociationTerminated
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FibroGenTerminatedDuchenne Muscular DystrophyUnited States, Belgium, Israel, Spain, Canada, Australia, Switzerland, United Kingdom, France, China, Netherlands, Italy, Austria, Czechia
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Sarepta Therapeutics, Inc.Active, not recruitingMuscular Dystrophy, DuchenneUnited States, Korea, Republic of, India, Slovenia, Turkey, United Kingdom, Germany, Switzerland, Spain, Czechia, France, Serbia, Taiwan, Netherlands, Mexico, Colombia, Denmark, New Zealand, Norway, Greece, Hungary, Ireland, Italy, Jo... and more
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University of MiamiNot yet recruitingMental Health Wellness 1United States
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Massachusetts General HospitalCompleted
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Milton S. Hershey Medical CenterThe Hollister Confidence FundCompleted
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University of Texas at AustinCompleted
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Wayne State UniversityBlue Cross Blue Shield of Michigan FoundationCompleted
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Tarsa Therapeutics, Inc.CompletedPhase 1 Pharmacodynamic StudyUnited States
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University College, LondonUniversity of North Carolina, Chapel Hill; NYU Grossman School of MedicineRecruitingDentatorubral-Pallidoluysian AtrophyUnited States, United Kingdom
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Sarepta Therapeutics, Inc.TerminatedAn Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular DystrophyDuchenne Muscular DystrophyUnited States, Belgium, Canada, Spain, United Kingdom, Czechia, Germany, Israel, Bulgaria, France, Italy, Poland, Sweden
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Stony Brook UniversityCompleted
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Sarepta Therapeutics, Inc.Hoffmann-La RocheActive, not recruitingDuchenne Muscular DystrophyUnited States, Japan, Taiwan, Belgium, Spain, Germany, Hong Kong, Italy, United Kingdom
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PfizerActive, not recruitingDuchenne Muscular DystrophyUnited States, Spain, Belgium, Korea, Republic of, Taiwan, Canada, Australia, Germany, Japan, France, Italy, United Kingdom, Russian Federation, Israel, Switzerland
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Percheron TherapeuticsRecruitingDuchenne Muscular DystrophyTurkey, United Kingdom, Australia, Serbia, Bulgaria
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University of Wisconsin, MadisonCompletedMental Health Wellness 1United States
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NYU Silver School of Social WorkCompletedMental Health Wellness 1United States
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International Rescue CommitteeJohns Hopkins University; World Health OrganizationCompleted
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University of SouthamptonUnknownKeratoconus | Fuchs Dystrophy | Corneal DiseaseUnited Kingdom
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Columbia UniversityMuscular Dystrophy Association; Stevens Institute of TechnologyCompletedDuchenne Muscular Dystrophy | Spinal Muscular Atrophy Type 3United States
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PTC TherapeuticsParexel; Dohmen Life Science ServicesApproved for marketingDuchenne Muscular DystrophyUnited States
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Hoffmann-La RocheCompletedDuchenne Muscular DystrophyUnited States, Belgium, Canada, Australia, Japan, France, Netherlands, Spain, Argentina, Germany, Italy, United Kingdom, Sweden
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Santhera PharmaceuticalsCompletedMuscular Dystrophy, Duchenne | Ambulatory CareUnited States, Spain, Austria, Belgium, France, Germany, Italy, Netherlands, Sweden, Switzerland
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Cooperative International Neuromuscular Research...United States Department of Defense; National Institutes of Health (NIH); U.S... and other collaboratorsUnknownDuchenne Muscular DystrophyUnited States, Canada, Australia, India, Israel, Argentina, Italy, Sweden
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National Eye Institute (NEI)TerminatedInherited Retinal Degeneration | Inherited Ophthalmic DiseasesUnited States
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University of Colorado, DenverCompleted
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University of Illinois at Urbana-ChampaignUniversity of Illinois at Chicago; National Institute on Aging (NIA)Recruiting
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University of NebraskaCompleted
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University of IdahoCompletedMental Health Wellness 1United States
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Northwest Portland Area Indian Health BoardmHealth Impact LabCompletedMental Health Wellness 1United States
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University Hospital, Basel, SwitzerlandCompletedDuchenne Muscular DystrophyFrance, Spain, Germany, Netherlands, Switzerland, United Kingdom
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Eli Lilly and CompanyTerminatedMuscular Dystrophy, DuchenneGermany, United States, Spain, Belgium, France, Italy, Taiwan, Netherlands, Turkey, Korea, Republic of, Argentina, Canada, Japan, Puerto Rico, Russian Federation, United Kingdom
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University of California, Los AngelesRecruiting
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Astellas Institute for Regenerative MedicineCompleted
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Ranjani IyerCompletedStress | Mental Health Wellness 1United States
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Cleveland Medical Devices IncNational Institute of Neurological Disorders and Stroke (NINDS)CompletedELECTROENCEPHALOGRAPHIC VARIANT PATTERN 1 (Disorder)United States
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Hassane M. Zarour, MDNational Cancer Institute (NCI)Completed
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FibroGenActive, not recruitingDuchenne Muscular DystrophyUnited States, Spain, Canada, Australia, China, Italy, Belgium, France, Netherlands, Austria, United Kingdom
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ML Bio Solutions, Inc.Active, not recruiting
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Astellas Institute for Regenerative MedicineCompleted
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Colorado State UniversityRecruiting
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University of ArkansasCompletedBuilding Partnerships With First Responders to Improve Delivery and Access of Mental Health ServicesMental Health Wellness 1United States
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Pacific UniversityNational Center for Complementary and Integrative Health (NCCIH)CompletedMental Health Wellness 1United States
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ItalfarmacoRecruitingDuchenne Muscular DystrophyCanada, Italy, France, Belgium, Germany, Netherlands, United Kingdom
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Benha UniversityUnknownDystrophy, RetinalUnited Arab Emirates
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GlaxoSmithKlineCompletedMuscular DystrophiesGermany, Belgium, Turkey, Netherlands, Spain, Israel, Australia, France, United Kingdom
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University of PennsylvaniaCompletedMental Health Wellness 1 | LonelinessUnited States
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National Institute of Nursing Research (NINR)CompletedCerebral Palsy | Neuromuscular DiseaseUnited States