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Clinical Trials on Myotonic Dystrophy 1
Total 7041 results
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Centre Hospitalier Universitaire de NiceCompletedFacioscapulohumeral Muscular DystrophyFrance
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Nationwide Children's HospitalMyonexus TherapeuticsRecruitingLimb-Girdle Muscular Dystrophy, Type 2EUnited States
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Aerie PharmaceuticalsCompleted
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Trefoil Therapeutics, Inc.CompletedCorneal Endothelial DystrophyUnited States
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Nationwide Children's HospitalBoston Children's Hospital; University of California, Davis; University of Minnesota and other collaboratorsCompletedCardiomyopathy | Duchenne Muscular Dystrophy (DMD)United States
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University Hospital, AngersFederico II University; University of Modena and Reggio EmiliaNot yet recruitingFacioscapulohumeral Muscular Dystrophy
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PYC TherapeuticsRecruitingRetinitis Pigmentosa | Eye Diseases, Hereditary | Retinal Dystrophies | Retinal Dystrophy Rod | Retinal Dystrophy Rod ProgressiveUnited States, Australia
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Centre Hospitalier Universitaire de NiceCompletedMuscular DystrophiesFrance
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University of RochesterCompletedFacioscapulohumeral Muscular DystrophyUnited States
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University of UtahCompletedMacular Dystrophy, CornealUnited States
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National Eye Institute (NEI)Bausch & Lomb Incorporated; Eye Bank Association of America; Midwest Eye Banks; Tissue Banks International and other collaboratorsCompletedCorneal Disease | Fuch's Dystrophy | Pseudophakic Corneal EdemaUnited States
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University of Kansas Medical CenterNational Institutes of Health (NIH)CompletedFacioscapulohumeral Muscular DystrophyUnited States
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, United Kingdom
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, Belgium, Australia, Canada, France, Germany, Israel, Italy, Spain, Sweden, United Kingdom
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University of British ColumbiaTerminatedJuvenile Myoclonic Epilepsy | Childhood Absence Epilepsy | Juvenile Absence EpilepsyCanada
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Columbia UniversityNational Eye Institute (NEI); Centre Hospitalier National d'Ophtalmologie des... and other collaboratorsRecruitingRetinitis Pigmentosa | Best Vitelliform Macular DystrophyUnited States, Germany, France
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Cumberland PharmaceuticalsVanderbilt University Medical CenterRecruitingCardiomyopathy, Dilated | Duchenne Muscular Dystrophy CardiomyopathyUnited States
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Institut de Myologie, FranceAssociation Française contre les Myopathies (AFM), ParisNot yet recruitingMerosin Deficient Congenital Muscular DystrophyFrance
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Prothelia, Inc.Cure CMD; The Bönnemann Laboratory, NINDS, National Institutes of Health; Oscar... and other collaboratorsCompletedMerosin Deficient Congenital Muscular DystrophyUnited States
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Neil LagaliLinkoeping University; Sahlgrenska University Hospital, Sweden; Region Östergötland and other collaboratorsTerminatedCorneal Dystrophy, Epithelial Basement Membrane | Epithelial Recurrent Erosion Dystrophy | Corneal ErosionsSweden
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IRCCS San Camillo, Venezia, ItalyUniversita di Verona; Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico and other collaboratorsEnrolling by invitationCalpain-3 Deficiency Limb Girdle Muscular Dystrophy Type 2AItaly
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National Institute of Neurological Disorders and...CompletedPeripheral Nervous System Disease | Focal DystoniaUnited States
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Istanbul University - Cerrahpasa (IUC)CompletedFacioscapulohumeral Muscular DystrophyTurkey
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Hugo W. Moser Research Institute at Kennedy Krieger...Active, not recruitingFacioscapulohumeral Muscular DystrophyUnited States
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aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular DystrophyUnited States, Italy, Netherlands
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Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedFacioscapulohumeral Muscular DystrophyUnited States, Spain, Canada
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University of New MexicoUniversity of FloridaWithdrawnOculopharyngeal Muscular Dystrophy
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Bioblast Pharma Ltd.CompletedOculopharyngeal Muscular DystrophyUnited States, Israel, Canada
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Fondazione G.B. Bietti, IRCCSRecruitingMacular Edema | Inherited Retinal Dystrophy | Laser RetinopathyItaly
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IRCCS San RaffaeleRecruiting
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ENCellNot yet recruitingDuchenne Muscular DystrophyKorea, Republic of
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.Not yet recruiting
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Sqy TherapeuticsBiotrialRecruitingDuchenne Muscular DystrophyFrance
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The Emmes Company, LLCUltragenyx Pharmaceutical Inc; Parent Project Muscular Dystrophy; Department...RecruitingDuchenne Muscular DystrophyUnited States
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REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
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PfizerRecruitingDuchenne Muscular DystrophyUnited States
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Gülsena UtkuRecruiting
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Anne M. ConnollyAnn & Robert H Lurie Children's Hospital of Chicago; Children's Hospital Medical... and other collaboratorsRecruiting
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Samsung Medical CenterRecruitingDuchenne Muscular DystrophyKorea, Republic of
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Sohag UniversityNot yet recruitingDuchenne Muscular DystrophyEgypt
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Massachusetts General HospitalBoston Children's HospitalRecruitingDuchenne Muscular DystrophyUnited States
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University of PittsburghRecruitingDuchenne Muscular DystrophyUnited States
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Ning Wang, MD., PhD.Recruiting
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CHU de Quebec-Universite LavalRecruitingDuchenne Muscular DystrophyCanada
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Percheron TherapeuticsActive, not recruitingDuchenne Muscular DystrophyUnited Kingdom, Australia, Serbia, Turkey, Bulgaria
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.Hoffmann-La RocheEnrolling by invitationDuchenne Muscular DystrophyUnited States
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FibroGenTerminatedDuchenne Muscular DystrophyUnited States, Belgium, Israel, Spain, Canada, Australia, Switzerland, United Kingdom, France, China, Netherlands, Italy, Austria, Czechia
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Daiichi Sankyo Co., Ltd.Orphan Disease Treatment Institute Co., Ltd.Completed
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Sarepta Therapeutics, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Belgium, Spain, United Kingdom, Netherlands, Germany, Canada, Italy