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Clinical Trials on Myotonic Dystrophy Type 1
Total 4256 results
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Fundacion para la Investigacion Biomedica del Hospital...University of Alcala; Hospital Universitario Ramon y Cajal; Instituto de Salud... and other collaboratorsRecruitingPolycystic Ovary Syndrome | Hyperandrogenism | Type 1 Diabetes | Hirsutism | Oligomenorrhea | Ovulation DisorderSpain
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National Cancer Institute (NCI)Active, not recruitingChronic Myelomonocytic Leukemia | Myelodysplastic Syndrome | Myelodysplastic Syndrome With Excess Blasts | Chronic Myelomonocytic Leukemia-1 | Chronic Myelomonocytic Leukemia-2 | Myelodysplastic Syndrome With Excess Blasts-1 | Myelodysplastic Syndrome/Acute Myeloid LeukemiaCanada, United States
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Roswell Park Cancer InstituteNational Cancer Institute (NCI)CompletedExtranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue | Nodal Marginal Zone B-cell Lymphoma | Recurrent Grade 1 Follicular Lymphoma | Recurrent Grade 2 Follicular Lymphoma | Recurrent Grade 3 Follicular Lymphoma | Recurrent Marginal Zone Lymphoma | Splenic Marginal Zone... and other conditionsUnited States
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The First Affiliated Hospital of Zhengzhou UniversityNot yet recruitingEsophageal Squamous Cell Carcinoma (ESCC) | PD-1 InhibitorsChina
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Beijing Friendship HospitalNot yet recruitingLymphoma | Hemophagocytic Lymphohistiocytosis | PD-1 Antibody | Epstein-Barr VirusChina
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National Cancer Institute (NCI)RecruitingRecurrent WHO Grade 2 Glioma | Recurrent Low Grade Astrocytoma | Refractory Low Grade Astrocytoma | Refractory Low Grade Glioma | Refractory WHO Grade 1 GliomaUnited States, Canada
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Janssen-Cilag International NVCompletedHuman Immunodeficiency Virus-type 1 InfectionSouth Africa, Kenya, Thailand, Uganda, Cameroon, Senegal
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Janssen PharmaceuticaWithdrawn
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Tibotec Pharmaceuticals, IrelandCompletedHuman Immunodeficiency Virus Type 1United States, France, United Kingdom, China, Germany, South Africa, Russian Federation, Argentina, Brazil, Puerto Rico, Austria, Thailand, Mexico, Uganda
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Tibotec Pharmaceuticals, IrelandCompletedHuman Immunodeficiency Virus Type 1Germany
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ENCellRecruitingCharcot-Marie-Tooth Disease Type 1AKorea, Republic of
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Odense University HospitalRecruitingType 1 Diabetes | Type 2 Diabetes | Parents | Fetal Complications | Family | Birth Injuries | Pregnancy in Diabetic | Maternal DiabetesDenmark
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Pharnext SACompletedPhase III Trial Assessing the Efficacy and Safety of PXT3003 in CMT1A Patients (PLEO-CMT) (PLEO-CMT)Charcot-Marie-Tooth Disease Type 1AUnited States, United Kingdom, Belgium, Canada, France, Netherlands, Spain, Germany
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Aarhus University HospitalUniversity of Southern DenmarkCompletedDiabetes Mellitus, Type 2 | Diabetes Mellitus, Type 1 | Diabetic Polyneuropathy | Hereditary Axonal Neuropathy | Hereditary Demyelinated Neuropathy | Polyneuropathy, Inflammatory Demyelinating, ChronicDenmark, Germany
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Johns Hopkins UniversityJuvenile Diabetes Research Foundation; National Eye Institute (NEI)RecruitingType 1 Diabetes | Type 2 Diabetes | Cystic Fibrosis-related DiabetesUnited States
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Assistance Publique Hopitaux De MarseilleRecruitingCharcot-Marie-Tooth Disease Type 1AFrance
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Passage Bio, Inc.Active, not recruitingGM1 Gangliosidosis | GM1 Gangliosidosis, Type I | GM1 Gangliosidosis, Type 2 | Beta-Galactosidase-1 (GLB1) DeficiencyUnited States, Canada, United Kingdom, Turkey, Brazil
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Jens Rikardt AndersenNutricia, Inc.; Nordsjaellands HospitalUnknownKidney Diseases | Hypertension | Diabetes Mellitus, Type 2 | Diabetes Mellitus | Diabetes Complications | Diabetes Mellitus, Type 1 | Glomerulonephritis | Kidney Disease, Chronic | Kidney InsufficiencyDenmark
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Odense University HospitalUniversity of Southern DenmarkCompletedDiabetes Mellitus, Type 2 | Diabetic Foot | Diabetes Complications | Diabetes Mellitus, Type 1Denmark
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Gloucestershire Hospitals NHS Foundation TrustSuspendedLichen Sclerosus | Squamous Cell Carcinoma | Normal Vulval Skin | High Grade Dysplasia - Usual Type ('VIN 2-3') | High Grade Dysplasia - Differentiated Type ('VIN 2-3') | Epithelial Hyperplasia Without Atypia | Atypia Not Otherwise Specified/ Low Grade Dysplasia ('VIN 1') | Pagets Disease of the...United Kingdom
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Mario Negri Institute for Pharmacological ResearchWithdrawnDiabetes Mellitus, Type 2 | Diabetes Mellitus, Type 1 | Ulcer Foot
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Nemours Children's ClinicRecruitingCharcot-Marie-Tooth Disease | Motor Neuron Disease | Amyotrophic Lateral Sclerosis | Muscular Dystrophy | Spinal Muscular Atrophy | Neuromuscular Disease | Spinal Muscular Atrophy With Respiratory Distress 1 | Peroneal Muscular AtrophyUnited States
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Institut National de la Santé Et de la Recherche...RecruitingNeurofibromatosis Type 1 | Ichthyosis | Ectodermal Dysplasia | Albinism | Pemphigus | Mucous Membrane Pemphigoid | Inherited Epidermolysis Bullosa | Palmoplantar Keratoderma | Incontinentia PigmentiFrance
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Sanguine BiosciencesCompletedDepression | Melanoma | Epilepsy | Lymphoma | Multiple Sclerosis | Kidney Cancer | Cervical Cancer | Diabetes Mellitus | Leukemia | Breast Cancer | Chronic Kidney Diseases | Chronic Obstructive Pulmonary Disease | Parkinson's Disease | Systemic Lupus Erythematosus | Multiple Myeloma | Hepatitis B | Insomnia | Colorectal Cancer | HIV/AID... and other conditionsUnited States
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Institut Paoli-CalmettesRecruitingNeuroendocrine Tumor Grade 1 | Neuroendocrine Tumor of Pancreas (Disorder)France
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National Cancer Institute (NCI)Active, not recruitingRecurrent Grade 1 Follicular Lymphoma | Recurrent Grade 2 Follicular Lymphoma | Recurrent Grade 3 Follicular Lymphoma | Refractory Follicular Lymphoma | Grade 3a Follicular LymphomaUnited States, Canada, Singapore
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Alnylam PharmaceuticalsActive, not recruitingPrimary Hyperoxaluria Type 1 | Primary HyperoxaluriaUnited States, Italy, France, Lebanon, Belgium, Netherlands, Israel, United Arab Emirates, Australia, Jordan, Turkey
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TakedaActive, not recruiting
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University Hospital, GrenobleResMed; VitalAireCompleted
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Shaare Zedek Medical CenterShireCompletedGaucher Disease, Type 1
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Shaare Zedek Medical CenterPfizerCompletedGaucher Disease, Type 1
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ShireCompletedGaucher Disease, Type 1Israel, Paraguay, Argentina, Russian Federation, Tunisia
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ShireCompletedGaucher Disease, Type 1Spain, Israel, United States, India, Paraguay, United Kingdom, Russian Federation, Tunisia, Argentina
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PfizerWithdrawnType 1 Gaucher DiseaseUnited States
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ActelionCompletedGaucher Disease Type 1United States, Taiwan, Canada, Spain, Australia, France, Brazil, Hungary, Czechia, Germany, Italy, Netherlands, United Kingdom
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National Institute of Allergy and Infectious Diseases...CompletedImmunoproliferative DisorderUnited States
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Assistance Publique - Hôpitaux de ParisCompletedTendinopathy | Cervical Radiculopathy | Post-herpetic Neuralgia | Chronic Back Pain | Limbs Arthrosis | Non Arthrosic Limbs Arthralgia | Chronic Lomboradiculalgia | Post-surgical Peripheral Neuropathic Pain | Post Trauma Neuropathic Pain | Complex Regional Pain Syndrome Type I or IIFrance
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UNC Lineberger Comprehensive Cancer CenterCompletedOptic Glioma | Plexiform Neurofibroma | Neurofibromatosis-1United States
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Qilu Hospital of Shandong UniversityLanZhou University; First Affiliated Hospital, Sun Yat-Sen University; Wuhan... and other collaboratorsRecruitingPancreatic Neoplasms | Pancreatic Diseases | Pancreatitis | Pancreatic Ductal Adenocarcinoma | Pancreatic Neuroendocrine Tumor | Pancreatic Elastase 1China
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Joseph TuscanoNational Cancer Institute (NCI); Genentech, Inc.; Pharmacyclics LLC.RecruitingAnn Arbor Stage II Follicular Lymphoma | Ann Arbor Stage III Follicular Lymphoma | Ann Arbor Stage IV Follicular Lymphoma | Grade 1 Follicular Lymphoma | Grade 2 Follicular Lymphoma | Grade 3a Follicular LymphomaUnited States
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Janssen Sciences Ireland UCActive, not recruitingHuman Immunodeficiency Virus Type 1Portugal, South Africa, Thailand, Uganda, Spain
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Oslo University HospitalUniversity Hospital, AkerCompletedDiabetes Mellitus, Type 1 | Coronary Heart Disease | ComplicationsNorway
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Medical College of WisconsinNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsTerminatedFollicular Lymphoma | Recurrent Grade 1 Follicular Lymphoma | Recurrent Grade 2 Follicular Lymphoma | Recurrent Grade 3 Follicular LymphomaUnited States
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ShireCompletedGaucher DiseaseUnited States, Spain, United Kingdom, Israel
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ShireCompletedGaucher DiseaseIsrael, Romania, Serbia
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ISU Abxis Co., Ltd.CompletedGaucher Disease, Type 1
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1United States, United Kingdom, Bulgaria, Canada, Colombia, India, Israel, Lebanon, Mexico, Russian Federation, Serbia, Tunisia
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1United States, France, Germany, Italy, Brazil, Australia, Argentina, Canada, Egypt, Russian Federation, Spain, United Kingdom
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AstraZenecaWithdrawnCore: Relapsed or Refractory Diffuse Large B-Cell Lymphoma | Module 1: Non-GCB Diffuse Large B-Cell Lymphoma
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Genzyme, a Sanofi CompanyWithdrawnGaucher Disease, Type 1United States, India