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Clinical Trials on Neurodegenerative Disease, Hereditary
Total 376910 results
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University College London HospitalsCompletedDistal Hereditary Motor Neuropathy, Type II | Distal Hereditary Motor Neuropathy, Type V | Distal Hereditary Motor Neuronopathy Type I | Distal Hereditary Motor Neuronopathy Type VIUnited Kingdom
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Neurophth Therapeutics IncActive, not recruitingLeber Hereditary Optic Neuropathy (LHON)United States
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Santhera PharmaceuticalsCompletedLeber's Hereditary Optic Neuropathy (LHON)United States, United Kingdom, Spain, Poland, Austria, Belgium, Bulgaria, Germany, Italy, Portugal
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Santhera PharmaceuticalsCompletedLeber's Hereditary Optic Neuropathy (LHON)Belgium, Netherlands, France, Germany, Norway, United Kingdom, Italy
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Mahidol UniversityCompletedOptic Atrophy, Hereditary, LeberThailand
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GenSight BiologicsNo longer availableLeber Hereditary Optic Neuropathy (Optic, Atrophy, Hereditary, Leber)
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GenSight BiologicsCompletedLeber Hereditary Optic NeuropathyUnited States, France, Italy, United Kingdom, Germany
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GenSight BiologicsActive, not recruitingLeber Hereditary Optic NeuropathyBelgium, Spain, United States, France, United Kingdom, Taiwan, Italy
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Santhera PharmaceuticalsCompletedLeber's Hereditary Optic Neuropathy (LHON)Italy, Germany, France, Austria, Greece, Netherlands
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GenSight BiologicsCompletedLeber Hereditary Optic NeuropathyUnited States, France, Italy, Spain, United Kingdom
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Huazhong University of Science and TechnologyShiyan Taihe HospitalActive, not recruitingLeber Hereditary Optic NeuropathyChina
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GenSight BiologicsCompletedLeber Hereditary Optic NeuropathyFrance
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Santhera PharmaceuticalsEuropean Vision Institute Clinical Research NetworkCompletedLeber Hereditary Optic Neuropathy (LHON)Belgium, France, Denmark, Italy, Slovenia
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Neurophth Therapeutics IncRecruitingLeber Hereditary Optic Neuropathy (LHON)China, United States
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Wuhan Neurophth Biotechnology Limited CompanyRecruitingLeber's Hereditary Optic Neuropathy (LHON)China
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Medical College of WisconsinTerminatedLeber's Hereditary Optic Neuropathy (LHON)United States
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University Hospital, AngersUnknownLeber Hereditary Optic NeuropathyFrance
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State University of New York at BuffaloHadley Jo FoundationCompletedMitochondrial Diseases | Optic Atrophy | Neurodegenerative Disease, HereditaryUnited States
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State University of New York at BuffaloThe Callum McKeefery and Nikki Albano McKeefery Pediatric Division of Genetics...CompletedMitochondrial Diseases | Optic Atrophy | Neurodegenerative Disease, HereditaryUnited States
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Massachusetts General HospitalCompletedHereditary Sensory and Autonomic Neuropathy Type IUnited States
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University of ExeterRecruitingParkinson Disease | Neurodegenerative Diseases | Neurodegenerative Disease, Hereditary | Parkinson's | Nervous System DisorderUnited Kingdom
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Santhera PharmaceuticalsWithdrawnLeber's Hereditary Optic Neuropathy
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University College, LondonRecruitingHereditary Sensory Neuropathy Type IUnited Kingdom
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Santhera PharmaceuticalsNo longer availableLeber's Hereditary Optic Neuropathy
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Stealth BioTherapeutics Inc.CompletedLeber's Hereditary Optic NeuropathyUnited States
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Bin LiHuazhong University of Science and TechnologyCompletedLeber Hereditary Optic NeuropathyChina
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Byron LamNational Eye Institute (NEI)Active, not recruitingLeber's Hereditary Optic NeuropathyUnited States
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Santhera PharmaceuticalsCompletedLeber's Hereditary Optic NeuropathyCanada, Germany, United Kingdom
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Edison Pharmaceuticals IncNo longer availableLeber's Hereditary Optic NeuropathyUnited States
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Hôpital Necker-Enfants MaladesEuropean Georges Pompidou Hospital; CLAIROPCompletedSafety Issues | Efficacy, SelfFrance
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Santhera PharmaceuticalsCompletedLeber's Hereditary Optic NeuropathyCanada, Germany, United Kingdom
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First Affiliated Hospital of Fujian Medical UniversityRecruiting
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Argo SanteGenSight BiologicsCompleted
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Centre Hospitalier National d'Ophtalmologie des...StreetlabCompletedRetinitis Pigmentosa | Leber's Hereditary Optic Neuropathy | Stargardt DiseaseFrance
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Boston Children's HospitalCureAP4 FoundationRecruitingHereditary Spastic Paraplegia | SPG50 | SPG47 | SPG51 | SPG52 | AP4-related Hereditary Spastic Paraplegia | Early Onset Hereditary Spastic Paraplegia | SPG4 | SPG3A | SPG15 | SPG11United States
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Spaulding Rehabilitation HospitalMassachusetts General HospitalWithdrawnHereditary Spastic Paraplegia
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University Hospital TuebingenRecruitingHereditary Spastic Paraplegia | Hereditary, Spastic Paraplegia, Autosomal DominantGermany
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University Hospital TuebingenCompleted
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Radboud University Medical CenterJacques and Gloria Gossweiler FoundationCompletedHereditary Spastic Paraplegia | Strumpell DiseaseNetherlands
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National Institute of Neurological Disorders and...RecruitingMuscular Dystrophies | Inherited Neuromuscular Conditions | Inherited Neuropathies | Muscle Myopathies | Hereditary Spastic ParaplegiasUnited States
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NYU Langone HealthCompletedAtunomic NeuropathyUnited States
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Dr. Rebecca SchuleGerman Federal Ministry of Education and Research; German Center for Neurodegenerative...RecruitingHereditary Spastic ParaplegiaAustria, Germany, Italy
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University Hospital TuebingenCompleted
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Assistance Publique - Hôpitaux de ParisCompletedHereditary Spastic ParaplegiaFrance
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European University of LefkeCompletedHereditary Spastic ParaplegiaCyprus
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National Institute of Neurological Disorders and...TerminatedHereditary Spastic ParaplegiaUnited States
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University of Campinas, BrazilConselho Nacional de Desenvolvimento Científico e Tecnológico; Cristália Produtos...CompletedHereditary Spastic ParaplegiaBrazil
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Academisch Medisch Centrum - Universiteit van Amsterdam...CompletedCharcot-Marie-Tooth Disease | Hereditary Motor and Sensory NeuropathiesNetherlands
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Xuanwu Hospital, BeijingRecruitingGait | Motor FunctionChina
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NYU Langone HealthRecruitingHereditary Sensory and Autonomic Neuropathies | Familial Dysautonomia (Riley-Day Syndrome) | Hereditary Sensory and Autonomic Neuropathy 3United States, Israel