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Clinical Trials on Optic Atrophy, Hereditary, Leber
Total 162 results
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Medical University of BialystokUniversity of BialystokRecruitingOptic Neuritis | Ischemic Optic Neuropathy | Traumatic Optic Neuropathy | Toxic Optic Neuropathy | Compressive Optic Neuropathy | Hereditary Optic NeuropathiesPoland
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Eyecure Therapeutics Inc.Beijing Tongren HospitalUnknownLeber Congenital Amaurosis, Retinitis PigmentosaChina
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Editas Medicine, Inc.Active, not recruitingRetinal Degeneration | Eye Diseases, Hereditary | Vision Disorders | Leber Congenital Amaurosis 10 | Inherited Retinal Dystrophies | Retinal Disease | Eye Disorders CongenitalUnited States
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QLT Inc.CompletedLCA (Leber Congenital Amaurosis) | RP (Retinitis Pigmentosa)Canada, United States, Germany, Netherlands, United Kingdom
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QLT Inc.CompletedLCA (Leber Congenital Amaurosis) | RP (Retinitis Pigmentosa)United States, Canada, Germany, Netherlands, United Kingdom
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University of Campania "Luigi Vanvitelli"Retina Italia OnlusCompletedLeber Congenital Amaurosis 2 | Retinitis Pigmentosa 20Italy
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QLT Inc.CompletedLeber Congenital Amaurosis (LCA) | Retinitis Pigmentosa (RP)United States, Canada, Denmark, Germany, Netherlands, Switzerland, United Kingdom
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Nova Southeastern UniversityRecruitingGlaucoma, Suspect | Optic Nerve Hypoplasia and Abnormalities of the Central Nervous System | Congenital Coloboma of the Optic Nerve | Optic Nerve Head Pits, Bilateral CongenitalUnited States
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NGoggleNational Eye Institute (NEI); Duke UniversityEnrolling by invitationGlaucoma | Retinal Degeneration | Age Related Macular Degeneration | Optic NeuropathyUnited States
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Yale UniversityChildren's Hospital Los AngelesCompletedBiological Clock Dysfunction | Optic Nerve HypoplasiaUnited States
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ProQR TherapeuticsRecruitingEye Diseases | Neurologic Manifestations | Retinal Degeneration | Retinal Dystrophies | Sensation Disorders | Vision Disorders | Blindness | Leber Congenital Amaurosis | Leber Congenital Amaurosis 10 | Retinal Disease | Eye Disorders CongenitalBelgium, Brazil, Canada, Germany, Italy, Netherlands, United Kingdom
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Spark TherapeuticsActive, not recruitingLeber Congenital AmaurosisUnited States
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MeiraGTx UK II LtdCompletedNatural History Study of Patients With Leber Congenital Amaurosis Associated With Mutations in RPE65Leber Congenital AmaurosisUnited Kingdom, United States
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HuidaGene Therapeutics Co., Ltd.Xinhua Hospital, Shanghai Jiao Tong University School of MedicineRecruitingLeber Congenital AmaurosisChina
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Xinhua Hospital, Shanghai Jiao Tong University...HuidaGene Therapeutics Co., Ltd.RecruitingLeber Congenital AmaurosisChina
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Assistance Publique - Hôpitaux de ParisCompletedLeber Congenital AmaurosisFrance
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Spark TherapeuticsCompleted
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Applied Genetic Technologies CorpOregon Health and Science University; University of Massachusetts, WorcesterCompletedLeber Congenital AmaurosisUnited States
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MeiraGTx UK II LtdCompletedLeber Congenital AmaurosisUnited Kingdom, United States
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Atsena Therapeutics Inc.Active, not recruitingLeber Congenital Amaurosis | LCA | LCA1United States
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Hadassah Medical OrganizationWithdrawnWolfram Syndrome | Diabetes Mellitus Associated With Genetic Syndrome
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Washington University School of MedicineEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedDiabetes Mellitus | Type 1 Diabetes | Diabetes Insipidus | Wolfram SyndromeUnited States
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Hadassah Medical OrganizationCompletedLeber Congenital AmaurosisIsrael
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ProQR TherapeuticsCompletedLeber's Congenital AmaurosisUnited States, Belgium
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Centre d'Etude des Cellules SouchesGenethonRecruitingWolfram SyndromeFrance, Spain
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Amylyx Pharmaceuticals Inc.Active, not recruiting
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University of BirminghamActive, not recruitingWolfram SyndromeFrance, United Kingdom, Poland, Spain
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University of MiamiNational Eye Institute (NEI)CompletedGlaucoma | Macular Degeneration | Retinal Degeneration | Optic Neuropathy | Glaucoma Suspect | Visual Pathway DisorderUnited States
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Ospedale San RaffaeleRecruiting
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Washington University School of MedicineEnrolling by invitation
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Nantes University HospitalCompletedLeber Congenital AmaurosisFrance
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National Eye Institute (NEI)Completed
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Children's Hospital Los AngelesGenentech, Inc.CompletedGrowth Hormone Deficiency | Hypopituitarism | Septo-Optic DysplasiaUnited States
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Hadassah Medical OrganizationUnknownDiabetes Mellitus | Iron Metabolism Disorders | Optic Atrophy | Sensorineural Hearing Loss | Platelet Dysfunction | Gastroduodenal UlcerIsrael
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HuidaGene Therapeutics Co., Ltd.Cholgene Therapeutics, Inc.RecruitingLeber Congenital Amaurosis | Inherited Retinal Diseases Caused by RPE65 MutationsUnited States, China
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Jaeb Center for Health ResearchDepartment of Health and Human Services; Food and Drug Administration (FDA); Conquering...RecruitingGyrate Atrophy | Gyrata of Choroid and Retina; Atrophy | Ornithine-δ-aminotransferase | OAT | Chorioretinal DegenerationUnited States, Canada, Finland, France, United Kingdom, Germany, Brazil
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Fundacion para la Investigacion Biomedica del Hospital...Sociedad Española De Medicina InternaActive, not recruitingHereditary Hemorrhagic Telangiectasia | HHT | Rendu Osler Weber DiseaseSpain
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MD Stem CellsUnknownGlaucoma | Macular Degeneration | Retinal Disease | Hereditary Retinal Dystrophy | Optic Nerve DiseaseUnited States
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University College London HospitalsCompletedDistal Hereditary Motor Neuropathy, Type II | Distal Hereditary Motor Neuropathy, Type V | Distal Hereditary Motor Neuronopathy Type I | Distal Hereditary Motor Neuronopathy Type VIUnited Kingdom
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University of South FloridaUniversity of Miami; National Institutes of Health (NIH); University of KansasCompletedAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Progressive Muscular Atrophy | Hereditary Spastic Paraplegia
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National Human Genome Research Institute (NHGRI)CompletedTelangiectasia, Hereditary Hemorrhagic | Osler-Rendu-Weber Disease | Osler-Rendu DiseaseUnited States
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OcugenRecruitingRetinitis Pigmentosa | Leber Congenital AmaurosisUnited States
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Sun Yat-sen UniversityUnknown
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Gemini Therapeutics, Inc.CompletedMacular Degeneration | Retinal Degeneration | Geographic Atrophy | Dry Age-related Macular Degeneration | Retinal DiseaseUnited States
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Gemini Therapeutics, Inc.TerminatedMacular Degeneration | Retinal Degeneration | Geographic Atrophy | Dry Age-related Macular Degeneration | Retinal DiseaseUnited States
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PfizerCompletedEye Diseases | Macular Degeneration | Retinal Degeneration | Age-Related Maculopathies | Age-Related MaculopathyUnited States
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Gyroscope Therapeutics LimitedNovartis PharmaceuticalsActive, not recruitingMacular Degeneration | Retinal Degeneration | Geographic Atrophy | Dry Age-related Macular Degeneration | Retinal Disease | Macular AtrophyUnited States, Spain, United Kingdom, France, Germany, Australia, Netherlands, Poland
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McGill University Health Centre/Research Institute...RecruitingDiabetes Mellitus, Type 1 | Wolfram Syndrome | Neonatal Diabetes | Monogenic Diabetes | Maturity-onset Diabetes in the Young (MODY) | Wolcott-Rallison Syndrome | Mitochondrial DiabetesCanada
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Gyroscope Therapeutics LimitedNovartis PharmaceuticalsActive, not recruitingEye Diseases | Macular Degeneration | Retinal Degeneration | Geographic Atrophy | Dry Age-related Macular Degeneration | Retinal Disease | Macular AtrophyUnited States, United Kingdom