- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Ornithine Carbamoyltransferase Deficiency Disease in United States
Total 4452 results
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American Regent, Inc.WithdrawnIron Deficiency, AnaemiaUnited States
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Juan PascualNational Institute of Neurological Disorders and Stroke (NINDS)CompletedGlucose Metabolism Disorders | Epilepsy | Glucose Transporter Type 1 Deficiency Syndrome | Glut1 Deficiency Syndrome 1, Autosomal Recessive | Glucose Transporter Protein Type 1 Deficiency Syndrome | Glucose Transport Defect | GLUT1DS1United States
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Shield TherapeuticsUnknownFour-Way Crossover Study to Compare Ferric Maltol Capsules and Oral Suspension in Healthy VolunteersAnemia, Iron DeficiencyUnited States
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Sutter Gould Medical FoundationWithdrawnAnemia, Iron DeficiencyUnited States
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National Cancer Institute (NCI)CompletedLymphoma | Leukemia | Neoplasm | Immunologic Deficiency SyndromeUnited States
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The University of Texas Health Science Center,...National Center for Advancing Translational Sciences (NCATS); The Gerber FoundationRecruiting
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Garcia, Jose M., MD, PhDCompletedAdult-Onset Growth Hormone DeficiencyUnited States
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Green Cross CorporationAtlantic Research GroupRecruitingPrimary Immune DeficiencyUnited States
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Children's Mercy Hospital Kansas CityGenentech, Inc.CompletedGrowth Hormone DeficiencyUnited States
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Columbia UniversityRecruiting
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Vanderbilt UniversityCompletedPhosphoglycerate Kinase (PGK) DeficiencyUnited States
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American Regent, Inc.Completed
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American Regent, Inc.Completed
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VA Office of Research and DevelopmentCompleted
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University of Rhode IslandBrown University; Women and Infants Hospital of Rhode IslandCompleted
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National Institutes of Health (NIH)Completed
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National Institutes of Health (NIH)CompletedIron DeficiencyUnited States
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CSL BehringCompletedExtension Study of Subcutaneous Immunoglobulin Human in Patients With Primary Immunodeficiency (PID)Primary Immune DeficiencyUnited States
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Glasgow Royal InfirmaryNHS Greater Glasgow and ClydeCompletedInflammation | Iron-deficiency | Magnesium Deficiency | Thiamine DeficiencyUnited Kingdom
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Rocket Pharmaceuticals Inc.Enrolling by invitationLeukocyte Adhesion DeficiencySpain, United States, United Kingdom
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Massachusetts General HospitalNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Completed
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Pennington Biomedical Research CenterThe Wright Group in Crowley, LACompletedIron Deficiency AnemiaUnited States
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University of Texas Southwestern Medical CenterNational Institute of Neurological Disorders and Stroke (NINDS)Active, not recruitingGlucose Metabolism Disorders | Epilepsy | Glucose Transporter Type 1 Deficiency Syndrome | Glut1 Deficiency Syndrome 1, Autosomal Recessive | Glucose Transporter Protein Type 1 Deficiency Syndrome | Glucose Transport Defect | GLUT1DS1United States
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New York City Health and Hospitals CorporationMontefiore Medical Center; Foundation of Orthopedic TraumaSuspendedVitamin D Deficiency | Orthopedic Disorder | PolytraumaUnited States
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Eunice Kennedy Shriver National Institute of Child...University of IowaCompleted
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Cornell UniversityUniversity of RochesterCompletedIron DeficiencyUnited States
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Prometic Biotherapeutics, Inc.CompletedHypoplasminogenemia | Type I Plasminogen DeficiencyUnited States
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Baylor College of MedicineGrace Science FoundationRecruiting
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MedicureRecruitingPyridox(am)Ine 5'-Phosphate Oxidase DeficiencyUnited States, Australia
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CSL BehringCompletedPrimary Immune DeficiencyUnited States
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Stockton UniversityNova Southeastern UniversityCompletedCommon Variable Immunodeficiency | Hypergammaglobulinemia | Primary Immune Deficiency Disorder | Specific Antibody DeficiencyUnited States
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AmgenCompleted
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QOL Medical, LLCCompletedCongenital Sucrase-Isomaltase DeficiencyUnited States
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Dr Anthony HobsonAnglia Ruskin UniversityCompletedIron-deficiency | Microbial Colonization | Iron Deficiency Anemia | Iron Deficiency Anemia TreatmentUnited Kingdom
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American Regent, Inc.Completed
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Northwestern UniversityCompletedCongenital Leptin Deficiency (Disorder)United States
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OPKO Health, Inc.CompletedGrowth Hormone Deficiency (GHD)United States, Belarus, Greece, Hungary, Russian Federation, Ukraine
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Indiana UniversityCompletedAnemia, Iron DeficiencyUnited States
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Pharmacosmos A/SCompletedIron Deficiency Anemia | Iron Deficiency AnaemiaUnited States
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National Human Genome Research Institute (NHGRI)National Institutes of Health Clinical Center (CC); National Cancer Institute... and other collaboratorsCompletedADA-SCID | Adenosine Deaminase DeficiencyUnited States
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Changchun GeneScience Pharmaceutical Co., Ltd.Not yet recruiting
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Perrin C White, MDCompletedObesity | Vitamin D Deficiency | Insulin ResistanceUnited States
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CAMC Health SystemUnknown
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Mayo ClinicRecruiting
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Agency for Healthcare Research and Quality (AHRQ)University of WashingtonCompletedRicketsUnited States
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Sidero Bioscience, LLCCompleted
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Ultragenyx Pharmaceutical IncCompletedLong-chain Fatty Acid Oxidation Disorders (LC-FAOD) | Very Long Chain Acyl-CoA Dehydrogenase (VLCAD) Deficiency | Trifunctional Protein (TFP) Deficiency | Carnitine Palmitoyltransferase (CPT II) Deficiency | Longchain 3-hydroxy-acyl-CoA Dehydrogenase (LCHAD) DeficiencyUnited States, United Kingdom
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University of California, Los AngelesCompleted
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Indiana UniversityNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)TerminatedChronic Kidney Disease | Iron-deficiency AnemiaUnited States
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Baltimore VA Medical CenterNational Institute on Aging (NIA); Nutrition Obesity Research Center (NORC)TerminatedMetabolic Syndrome | Vitamin D DeficiencyUnited States