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Clinical Trials on Primary Disease Facioscapulohumeral Dystrophy (FSHD)
Total 54764 results
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Hacettepe UniversityCompletedPerformance | Duchenne Muscular Dystrophy | FlexibilityTurkey
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Hacettepe UniversityCompletedPerformance | Duchenne Muscular Dystrophy | FlexibilityTurkey
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Monica Levy AndersenCompletedOther Diseases or ConditionsBrazil
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Stanford UniversityUniversity of Pennsylvania; University of California, Davis; Oregon Health and... and other collaboratorsRecruitingFuchs' Endothelial Dystrophy | Fuchs Dystrophy | FuchsUnited States
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Michael D. Straiko, MDLions VisionGift Research; Eye Bank Association of AmericaRecruitingFuchs Endothelial DystrophyUnited States
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Trefoil Therapeutics, Inc.CompletedFuchs' Endothelial Dystrophy | Fuchs Dystrophy | FuchsUnited States
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Hope Biosciences Stem Cell Research FoundationHope BiosciencesNo longer availableCongenital Muscular Dystrophy Due to Lamin A/C MutationUnited States
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PTC TherapeuticsTerminatedLimb-Girdle Muscular DystrophyUnited States, Norway, Canada, Sweden, Russian Federation, Denmark, France, Germany
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Rigshospitalet, DenmarkCompletedLimb-girdle Muscular DystrophyDenmark
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Başak Çağla ArslanHacettepe UniversityRecruitingDuchenne Muscular Dystrophy | Occupational Therapy | GamificationTurkey
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Edgewise Therapeutics, Inc.Worldwide Clinical TrialsCompletedBecker Muscular Dystrophy | Healthy VolunteerUnited States
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Dokuz Eylul UniversityCompletedDuchenne Muscular Dystrophy | Upper Extremity ProblemTurkey
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Hacettepe UniversityCompletedPerformance | Duchenne Muscular Dystrophy | Gait | EnergyTurkey
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Santhera PharmaceuticalsCompletedMuscular Dystrophy, Duchenne | Ambulatory CareUnited States, Spain, Austria, Belgium, France, Germany, Italy, Netherlands, Sweden, Switzerland
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Assiut UniversityNot yet recruitingLimb-girdle Muscular Dystrophy
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Sarepta Therapeutics, Inc.RecruitingLimb-girdle Muscular DystrophyUnited States
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Rigshospitalet, DenmarkCompleted
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Istituto Ortopedico RizzoliCompletedBethlem Myopathy | Ullrich Congenital Muscular DystrophyItaly
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Astellas Institute for Regenerative MedicineCompletedStargardt's Macular DystrophyUnited States
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Astellas Institute for Regenerative MedicineCompletedStargardt's Macular DystrophyUnited States
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Benitec Biopharma, Inc.RecruitingOculopharyngeal Muscular DystrophyUnited States
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Assistance Publique - Hôpitaux de ParisNot yet recruitingDuchenne Muscular DystrophyFrance
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University of FloridaCompleted
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Barcelona Macula FoundationRecruitingRetinitis Pigmentosa | Choroideremia | Stargardt Disease 1 | Best Disease | Pattern Dystrophy of MaculaSpain
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Seoul National University HospitalNot yet recruitingMuscular Dystrophy, Duchenne | Upper Extremity | Orthotic DevicesKorea, Republic of
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Virginia Commonwealth UniversityRadboud University Medical Center; University of California, Los Angeles; University... and other collaboratorsRecruitingMyotonic Dystrophy 1United States, Netherlands, United Kingdom, New Zealand, Germany, Italy, Canada, France
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University of MalagaCompletedMuscular Dystrophy, Duchenne and Becker TypesSpain
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Vrije Universiteit BrusselCompletedMyotonic Dystrophy 1Belgium
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Élise DuchesneFondation du Grand défi Pierre LavoieCompletedMyotonic Dystrophy 1Canada
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Cooperative International Neuromuscular Research...United States Department of Defense; National Institutes of Health (NIH); U.S... and other collaboratorsUnknownDuchenne Muscular DystrophyUnited States, Canada, Australia, India, Israel, Argentina, Italy, Sweden
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National Center for Research Resources (NCRR)National Institute of Neurological Disorders and Stroke (NINDS); University...CompletedDuchenne Muscular Dystrophy
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Sarepta Therapeutics, Inc.Active, not recruiting
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University of RochesterLivionex IncCompletedCorneal Dystrophy, Band-ShapedUnited States
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University Hospital, RouenCompleted
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Astellas Pharma Global Development, Inc.Active, not recruitingStargardt's Macular DystrophyItaly, United States, Israel, United Kingdom, Germany, Spain, Hungary, France
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CHABiotech CO., LtdCompletedStargardt's Macular DystrophyKorea, Republic of
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Astellas Institute for Regenerative MedicineCompleted
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University of SouthamptonUnknownKeratoconus | Fuchs Dystrophy | Corneal DiseaseUnited Kingdom
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Astellas Institute for Regenerative MedicineCompleted
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Spark TherapeuticsActive, not recruitingConfirmed Biallelic RPE65 Mutation-associated Retinal DystrophyUnited States
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Bioblast Pharma Ltd.WithdrawnOculopharyngeal Muscular DystrophyCanada
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IRCCS Eugenio MedeaRecruiting
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingDuchenne Muscular Dystrophy | Natural History | Motor Function; RetardationItaly
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Oslo University HospitalUniversity of Oslo; Haukeland University HospitalRecruitingMyotonic Dystrophy 1Norway
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Lokman Hekim ÜniversitesiCompletedParents | Duchenne Muscular Dystrophy | Psychoeducation | Psychological WellnessTurkey
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Avidity Biosciences, Inc.Enrolling by invitationDuchenne Muscular Dystrophy | DMD | Exon 44 | DuchenneUnited States
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Children's Hospital Medical Center, CincinnatiActive, not recruitingMusculoskeletal Abnormalities | Duchenne Muscular DystrophyUnited States
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Université de SherbrookeRare Disease FoundationCompletedMyotonic Dystrophy 1Canada
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Hacettepe UniversityCompletedDuchenne Muscular Dystrophy | Gait Disorders in ChildrenTurkey
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LMU KlinikumCompleted