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Clinical Trials on SCID
Total 1200 results
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Dr. Loges & Co. GmbHBioTeSys GmbHCompletedEndothelial Dysfunction | Hyperhomocysteinemia | Hypertension Grade I, Subgroup "Borderline" (WHO)Germany
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Pamlab, Inc.Clionsky Neuro Systems Inc.UnknownMild Cognitive ImpairmentUnited States
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Vitaflo International, LtdUniversity College London HospitalsRecruiting
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National Institute of Allergy and Infectious Diseases...RecruitingX-linked Severe Combined Immunodeficiency (XSCID)United States
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Advicenne PharmaTerminatedDistal Renal Tubular AcidosisUnited States, Canada
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Advicenne PharmaWithdrawn
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Andrea GropmanChildren's National Research InstituteCompletedOrnithine Transcarbamylase Deficiency
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Johann Wolfgang Goethe University HospitalMedical University of Graz; University Hospital, Angers; Medical University of... and other collaboratorsCompletedIron-deficiency | Anemia | Vitamin B 12 Deficiency | Folic Acid Deficiency | Anaemia of Renal Disease | Anemia of Chronic InflammationGermany
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Emma Marie Caroline SlackUniversity Children's HospitalCompletedInborn Errors of Metabolism | Propionic Aciduria | Methylmalonic Aciduria | Urea Cycle DisorderSwitzerland
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Horizon Pharma Ireland, Ltd., Dublin IrelandUcyclyd Pharma, Inc.CompletedHepatic Encephalopathy | Urea Cycle DisordersUkraine
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Fundación Española de Hematología y HemoterapíaRecruitingGaucher Disease | Acid SphingoMyelinase DeficiencySpain
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Vitaflo International, LtdRecruitingPhenylketonurias | PKU | Maple Syrup Urine Disease | Homocystinuria | Glutaric Acidemia I | Hereditary TyrosinemiaUnited Kingdom
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Bambino Gesù Hospital and Research InstituteCatholic University of the Sacred HeartCompletedGenetic Disease | Retinopathy | Methylmalonic Aciduria and Homocystinuria,Cblc TypeItaly
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DLR German Aerospace CenterUniversity of Aarhus; University of Trieste; European Space AgencyCompletedSprains and Strains | Body Weight Changes | Muscular Atrophy | Bone Diseases, Metabolic | Cardiovascular Abnormalities | Acid-Base Imbalance | Protein MetabolismGermany
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DLR German Aerospace CenterUniversity Hospital, Angers; University of Zurich; University Hospital, Bonn; European... and other collaboratorsCompletedSprains and Strains | Body Weight Changes | Muscular Atrophy | Bone Diseases, Metabolic | Cardiovascular Abnormalities | Acid-Base Imbalance | Protein MetabolismGermany
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Vapotherm, Inc.University of Maryland; George Washington University; The Cooper Health System; Valley Presbyterian Hospital and other collaboratorsActive, not recruitingChronic Obstructive Pulmonary Disease | Dyspnea | Hypercapnic Respiratory Failure | Hypercapnic AcidosisUnited States
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Bezmialem Vakif UniversityCompleted
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Uta Lichter-KoneckiMedical College of Wisconsin; Children's National Research InstituteCompletedUrea Cycle Disorders | Organic AcidemiasUnited States
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Medical University of ViennaCompletedHyperemesis Gravidarum | Nausea Gravidarum | Vitamin C DeficiencyAustria
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Nutrition Institute, SloveniaNational Institute of Public Health, Slovenia; University Medical Centre Ljubljana and other collaboratorsEnrolling by invitationObesity | Iron-deficiency | Vitamin D Deficiency | Nutritional Status | Sarcopenia | Vitamin B 12 Deficiency | Folic Acid Deficiency | Diet | Nutrient Deficiency | Micronutrient Deficiency | Protein DeficiencySlovenia
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Genzyme, a Sanofi CompanyCompletedPompe Disease | Glycogen Storage Disease Type II (GSD II) | Acid Maltase DeficiencyUnited States, Belgium, Denmark, France, Germany, Netherlands, United Kingdom
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Uppsala UniversityCompletedFibromyalgia | Respiratory Alkalosis and Metabolic Acidosis | Chronic HyperventilationSweden
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Assiut UniversityCompletedCognitive Dysfunction | Hypercholesterolemia | HyperhomocysteinemiaEgypt
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Hoffmann-La RocheCompletedRenal Tubular Acidosis, Distal, With Hemolytic AnemiaSerbia
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metaX Institut fuer Diatetik GmbHGreat Ormond Street Hospital for Children NHS Foundation Trust; Birmingham...Not yet recruitingAlkaptonuria | Homocystine; Metabolic Disorder | Tyrosinemia, Type I | Tyrosinemia, Type II | Tyrosinemia, Type III | MSUD (Maple Syrup Urine Disease)
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II (GSD-II) | Pompe Disease | Glycogenesis 2 Acid Maltase DeficiencyUnited States, Canada, Australia
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Hospital Universitario Dr. Jose E. GonzalezLaboratorios Valdecasas S.A.CompletedDiabetic Nephropathies | HyperhomocysteinemiaMexico
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Eunice Kennedy Shriver National Institute of Child...Children's National Research InstituteTerminatedPhase I Pilot Study of Liver-Directed Gene Therapy for Partial Ornithine Transcarbamylase DeficiencyOrnithine Transcarbamylase Deficiency Disease
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Central Hospital, Nancy, FranceNot yet recruitingAlzheimer Disease | Homocystinemia
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University of Roma La SapienzaAlexion PharmaceuticalsRecruitingNon-Alcoholic Fatty Liver DiseaseItaly
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Humanitas Hospital, ItalyRecruitingCoronary Artery Disease | Diabetes Mellitus | Contrast-induced Nephropathy | Lactic Acidosis With Diabetes Mellitus | Metformin Associated Lactic AcidosisItaly
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University of Colorado, DenverCompletedCognitive Dysfunction | Chronic Kidney Disease | Metabolic AcidosisUnited States
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Genzyme, a Sanofi CompanyTerminatedGlycogen Storage Disease Type II (GSD-II) | Pompe Disease | Glycogenesis 2 Acid Maltase DeficiencyUnited States, Israel
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Universidade Estadual de LondrinaCompletedCardiovascular Disease | Hemodialysis | Chronic Renal Failure | Uremia | HyperhomocysteinemiaBrazil
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Acid Maltase Deficiency Disease | Glycogenosis 2 | Pompe DiseaseUnited States
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University Hospitals Cleveland Medical CenterTerminatedChronic Kidney Disease | Sickle Cell Anemia | Metabolic AcidosisUnited States
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National Institute of Allergy and Infectious Diseases...TerminatedGrowth Failure | X-linked Severe Combined Immunodeficiency (XSCID) | Growth Hormone ResistenceUnited States
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University of PennsylvaniaTerminatedOrnithine Transcarbamylase Deficiency Disease
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VA Office of Research and DevelopmentDetroit VARecruitingSleep Apnea | Hypercapnia | SCI/DUnited States
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TakedaRecruitingMultiple Myeloma | Secondary Immunodeficiency (SID)Greece, Spain, Italy, Romania, Argentina, Czechia, France, Germany, Poland, Sweden, Turkey
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National Heart, Lung, and Blood Institute (NHLBI)CompletedSickle Cell Disease (SCD)United States
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Uro-Research, LLCUnknownUrinary Incontinence | Spinal Cord Injury (SCI) | Chronic Urinary Retention
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University Hospital, MontpellierFisher and Paykel HealthcareNot yet recruitingAcute Exacerbation of Chronic Obstructive Pulmonary Disease | Hypercapnic Acidosis | Respiratory Failure With HypercapniaFrance
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University of MilanRecruitingCOPD | Dyspnea | ArgininemiaItaly
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Marmara UniversityBulent Ecevit University; Mustafa Kemal University; TC Erciyes University; Kahramanmaras... and other collaboratorsUnknownObstructive Sleep Apnea | Acid-Base Imbalance | Hypercapnia | Obesity Hypoventilation Syndrome | Post-Op ComplicationTurkey
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Cytonet GmbH & Co. KGCompletedOrnithine Transcarbamylase Deficiency | Urea Cycle Disorders | Citrullinemia | Carbamoylphosphate Synthetase I DeficiencyGermany
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Genzyme, a Sanofi CompanyTerminatedGlycogenosis 2 | Glycogen Storage Disease Type II (GSD II) | Acid Maltase Deficiency | Pompe Disease (Infantile-Onset)United States, Taiwan, Germany
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Georgetown UniversityCompletedEnd Stage Renal Disease | HyperhomocysteinemiaUnited States
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Genzyme, a Sanofi CompanyCompletedGlycogenesis 2 Acid Maltase Deficiency | Pompe Disease (Late-Onset) | Glycogen Storage Disease Type II (GSD II)United States, Netherlands, United Kingdom, Germany
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Genzyme, a Sanofi CompanyCompletedGlycogenesis 2 Acid Maltase Deficiency | Pompe Disease (Late-Onset) | Glycogen Storage Disease Type II (GSD II)France