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Clinical Trials on Sialic Acid Storage Disease
Total 8576 results
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Karabuk UniversityCompletedNeural Tube Defects | Folic AcidTurkey
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SciVision Biotech Inc.TerminatedTrigger Finger | Hyaluronic AcidTaiwan
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University of FloridaPrometheus LaboratoriesCompletedInflammatory Bowel Disease | Glycogen Storage Disease Type IaUnited States
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Rambam Health Care CampusUnknown
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Genzyme, a Sanofi CompanyApproved for marketingGlycogen Storage Disease Type II | Glycogenosis 2
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Rennes University HospitalRecruitingFecal Continence Disorders | Posterior Pelvic Static DisordersFrance
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NorgineCompletedAcid Reflux | Gastro Oesophageal Reflux DiseaseUnited Kingdom
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AstraZenecaCompletedNausea | Heartburn | Acid Regurgitation | Upper Abdominal Pain
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Astellas Gene TherapiesRecruitingPompe Disease (Late-onset)United States, France, Spain, Taiwan
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Amicus TherapeuticsCompletedPompe Disease (Late-onset)United States, Australia, Korea, Republic of, Japan, Taiwan, Belgium, Slovenia, New Zealand, United Kingdom, France, Argentina, Canada, Spain, Bosnia and Herzegovina, Germany, Sweden, Hungary, Austria, Bulgaria, Denmark, Greece, I... and more
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Duke UniversityCompleted
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Amicus TherapeuticsTerminatedLate-onset Pompe DiseaseUnited States, Canada, Australia, Belgium
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BioMarin PharmaceuticalTerminatedLate-onset Pompe DiseaseUnited States, United Kingdom, Germany, France, Italy, Portugal, Belgium, Netherlands
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GeneCradle IncRecruitingPompe Disease (Late-onset)China
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GeneCradle IncRecruitingPompe Disease Infantile-OnsetChina
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Seventh Medical Center of PLA General HospitalGeneCradle Therapeutics, IncRecruiting
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Fundació Institut de Recerca de l'Hospital de la...Genzyme, a Sanofi CompanyUnknownPompe Disease | Late Onset Pompe DiseaseSpain
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Radboud University Medical CenterStichting Bevordering Tandheelkundige Kennis of the Nederlands Tijdschrift...CompletedReflux Acid | Bruxism | Tooth WearNetherlands
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University of California, San DiegoCompletedLactic AcidosisUnited States
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Azienda Sanitaria ASL Avellino 2Unknown
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Genzyme, a Sanofi CompanyCompletedPompe DiseaseBelgium, United States, Czechia, Germany, Italy, Taiwan
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University of FloridaAmicus TherapeuticsTerminatedPompe Disease | Hypersensitivity Reaction
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Glycogenosis 2United States
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Chinese University of Hong KongQueen Elizabeth Hospital, Hong Kong; Alice Ho Miu Ling Nethersole Hospital; Tseung...CompletedColitis, Ulcerative | Aminosalicylic AcidHong Kong
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Chinese University of Hong KongRecruiting
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Western University, CanadaUnknownMental Fatigue | Ketosis | KetonemiaCanada
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Universitätsklinikum Hamburg-EppendorfRecruiting
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American University of Beirut Medical CenterWithdrawnCatheter-Associated Urinary Tract Infection, Ascorbic AcidLebanon
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State University of New York at BuffaloTerminatedDiabetic KetoacidosisUnited States
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Marshall UniversityCompletedDiabetic KetoacidosisUnited States
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CUF Santarém HospitalUnknownKnee Osteoarthritis | Bleeding | Ankle Osteoarthritis | Tranexamic Acid
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Purdue UniversityCompleted
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The George InstituteNot yet recruitingDiabetic KetoacidosisAustralia
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MetroHealth Medical CenterCompleted
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University of ManitobaCo-Investigator - Dr. Cheryl Rockman-GreenbergCompletedHypoglycemia | Glycogen Storage Disorder Type 1 | Cornstarch | GlycosadeCanada
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National Institute of Allergy and Infectious Diseases...National Center for Advancing Translational Sciences (NCATS); Primary Immune...Enrolling by invitationADA-SCID | Omenn Syndrome | SCID | Reticular Dysgenesis | XSCID | Leaky SCIDUnited States, Canada
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National Taiwan University HospitalRecruitingPeripheral Neuropathy | Lactic Acidosis | MyelosuppressionTaiwan
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University Hospital, RouenUniversity Hospital, CaenRecruitingLysosomal Storage Diseases | Neonatal ScreeningFrance
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BioMarin PharmaceuticalTerminatedLate-onset Pompe Patients Untreated or Treated With rhGAASpain, Slovenia, Serbia, Korea, Republic of, Greece, Australia, Singapore, Brazil, Canada, Taiwan, Ireland, Poland, Romania
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University of AarhusUnknownGlycogen Storage Disease Type 2 | Dystrophia MyotonicaDenmark
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Beth Israel Deaconess Medical CenterNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Recruiting
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Central Hospital, Nancy, FranceRecruitingPompe's Disease Juvenile OnsetFrance
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National...CompletedFecal Incontinence | Bile Acid MalabsorptionUnited States
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Medical University of LodzCompletedUric Acid Concentration, Serum, Quantitative Trait Locus 7
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Translational Research Center for Medical Innovation...TerminatedPrimary Triglyceride Deposit Cardiomyovasculopathy (TGCV) | Neutral Lipid Storage Disease With Myopathy (NLSD-M)Italy, Japan
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Karolinska InstitutetMidsona AB; Forskningsrådet för arbetsliv och socialvetenskap, FASCompletedOverweight and Obesity | Lifestyle-related Condition | Essential Fatty Acid DeficiencySweden
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Ain Shams UniversityDar EL Salam Cancer HospitalRecruitingBreast Cancer | Chemotherapy | Neurologic Disorder | Paclitaxel | Alpha Lipoic AcidEgypt
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Duke UniversityCompleted
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University Children's Hospital, ZurichSanofiCompleted
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Royal Brompton & Harefield NHS Foundation TrustGenzyme, a Sanofi CompanyUnknownPompe's Disease