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Clinical Trials on Sialic Storage Disease
Total 381762 results
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ShireCompletedGaucher DiseaseIsrael, Romania, Serbia
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ShireCompletedGaucher Disease, Type 3Egypt, India, Tunisia
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ISU Abxis Co., Ltd.CompletedGaucher Disease, Type 1
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1United States, United Kingdom, Bulgaria, Canada, Colombia, India, Israel, Lebanon, Mexico, Russian Federation, Serbia, Tunisia
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1United States, France, Germany, Italy, Brazil, Australia, Argentina, Canada, Egypt, Russian Federation, Spain, United Kingdom
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Genzyme, a Sanofi CompanyWithdrawnGaucher Disease, Type 1United States, India
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ISU Abxis Co., Ltd.Completed
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Amicus TherapeuticsTerminatedType 1 Gaucher DiseaseUnited States, United Kingdom
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Crolll GmbhUniversity of Magdeburg; Estimate, GmbHCompletedNon-alcoholic Steatohepatitis | Increased Iron Storage / Disturbed DistributionGermany
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He HuangLingyi Biotech Co., Ltd.Recruiting
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CANbridge (Suzhou) Bio-pharma Co., Ltd.RecruitingGaucher Disease, Type 1 | Gaucher Disease, Type 3China
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Cambridge University Hospitals NHS Foundation TrustMedical Research Council; National Institute for Health Research, United KingdomRecruitingGaucher Disease, Type III | Gaucher Disease, Type IUnited Kingdom
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SanofiCompleted
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Shaare Zedek Medical CenterCompleted
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Amicus TherapeuticsCompletedGaucher Disease | Gaucher Disease, Type 1 | Type 1 Gaucher DiseaseUnited States
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Amicus TherapeuticsCompletedGaucher Disease | Gaucher Disease, Type 1 | Type 1 Gaucher DiseaseUnited Kingdom, Israel, South Africa, United States
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University of CincinnatiWithdrawnLow Back Pain | Sciatic Radiculopathy | Degenerative Intervertebral DiscsUnited States
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CephalonCompleted
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Massachusetts General HospitalGenzyme, a Sanofi Company; Scott and White Hospital & ClinicTerminatedKidney Diseases | Genetic Diseases, X-Linked | End Stage Renal Disease | ESRD | Fabry Disease | Rare DiseasesUnited States
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National Institute of Neurological Disorders and...CompletedGaucher DiseaseUnited States
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AlexionRecruitingWolman Disease | Cholesterol Ester Storage Disease | Lysosomal Acid Lipase Deficiency | Acid Cholesteryl Ester Hydrolase Deficiency, Type 2 | Acid Lipase Deficiency | LIPA Deficiency | LAL-DeficiencyFrance, Belgium, United States, Spain, Germany, Greece, Israel, Italy, Slovenia, United Kingdom, Brazil, Canada, Denmark, Australia, Croatia, Czechia, Ireland, Mexico, Netherlands, Poland, Portugal, Saudi Arabia
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Freeline TherapeuticsRecruitingGaucher Disease, Type 1Spain, Israel, United States, United Kingdom, Brazil, Germany, Paraguay
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CENTOGENE GmbH RostockCompletedLysosomal Storage Diseases | Sphingolipidoses | Gaucher DiseaseAlbania, Greece, India, Israel, Morocco, Pakistan, Spain
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Lysosomal and Rare Disorders Research and Treatment...UnknownGaucher Disease Type 1United States
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National Center for Research Resources (NCRR)University of PittsburghUnknownGaucher's DiseaseUnited States
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SanofiCompleted
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AVROBIOWithdrawn
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Amicus TherapeuticsCompletedGaucher Disease | Gaucher Disease, Type 1 | Type 1 Gaucher DiseaseUnited Kingdom, United States
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University of HartfordCompleted
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Chengdu University of Traditional Chinese MedicineUnknownSciatica Due to Intervertebral Disc DisorderChina
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Shoshana VilkGenzyme, a Sanofi CompanyCompletedGaucher Disease | Patient Reported OutcomeIsrael
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Lysosomal and Rare Disorders Research and Treatment...RecruitingBone Diseases | Gaucher DiseaseUnited States
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Genzyme, a Sanofi CompanyActive, not recruitingGaucher Disease Type 1 | Gaucher Disease Type 3Germany, United States, Japan, United Kingdom
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KemPharm Denmark A/STerminatedGaucher Disease, Type 1 | Gaucher Disease, Type 3India
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Baylor Research InstituteTexas Scottish Rite Hospital for ChildrenWithdrawnGaucher Disease Type 1 | Gaucher Disease Type 3United States
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IntraBio IncCompletedGM2 Gangliosidosis | Tay-Sachs Disease | Sandhoff DiseaseUnited States, Germany, Spain, United Kingdom
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Terence FlotteMassachusetts General Hospital; University of Massachusetts, WorcesterActive, not recruitingTay-Sachs Disease | Sandhoff DiseaseUnited States
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National Institute of Neurological Disorders and...CompletedGaucher DiseaseUnited States, United Kingdom
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Diskapi Teaching and Research HospitalNot yet recruiting
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Riphah International UniversityRecruiting
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Assistance Publique - Hôpitaux de ParisGelscom SASWithdrawnSciatica | Herniated Disc | Persistent Pain, LegFrance
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Jaseng Medical FoundationTerminatedLumbar Spinal StenosisKorea, Republic of
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University Of PerugiaRecruitingObesity | Ketosis | Lysosomal Acid Lipase Deficiency | Ketogenic DietingItaly
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Riphah International UniversityRecruitingPiriformis SyndromePakistan
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Riphah International UniversityRecruitingPiriformis SyndromePakistan
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Riphah International UniversityCompleted
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Neuro Counsel Hospital, PakistanPhysiotherapy Clinic Iqra University Islamabad (Chak Shahzad); Noor Hospital...Completed
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Riphah International UniversityCompleted
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Riphah International UniversityCompleted