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- US Clinical Trials Registry
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Clinical Trials on Smith-Magenis Syndrome in United States
Total 14292 results
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University of VirginiaRecruitingMyelodysplastic Syndromes | AML, Adult | ALL, Adult | Leukemia, AcuteUnited States
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Walter Reed National Military Medical CenterUniformed Services University of the Health SciencesActive, not recruitingChronic Exertional Compartment SyndromeUnited States
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TearLab CorporationCompleted
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Mitotech, SAORA, Inc.CompletedDry Eye SyndromeUnited States
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Eisai Inc.CompletedMyelodysplastic SyndromeUnited States
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkUnknownMyelodysplastic SyndromeUnited States
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ShireCompletedShort Bowel SyndromeUnited States
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CHU de Quebec-Universite LavalCompletedChronic Pain | Complex Regional Pain Syndrome | Failed Back Surgery SyndromeUnited States, Canada
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University of ChicagoTerminatedObstructive Sleep Apnea SyndromeUnited States
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NeuroPaceNational Institute of Neurological Disorders and Stroke (NINDS); University...RecruitingEpilepsy | Seizures | Lennox Gastaut Syndrome | Lennox-Gastaut Syndrome, Intractable | Seizures, GeneralizedUnited States
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Mirati Therapeutics Inc.CompletedMyelodysplastic Syndromes | LeukemiaCanada, United States
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Washington University School of MedicineCompletedMyelodysplastic Syndromes | Leukemia, Myeloid, AcuteUnited States
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National Cancer Institute (NCI)RecruitingNeoplasms | Li-Fraumeni Syndrome | Tp53 MutationsUnited States
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Eli Lilly and CompanyDaiichi Sankyo, Inc.CompletedCoronary Arteriosclerosis | Acute Coronary SyndromesUnited States
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Sidney Kimmel Comprehensive Cancer Center at Johns...TerminatedMyelodysplastic SyndromeUnited States
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National Cancer Institute (NCI)CompletedLymphoma | Leukemia | Neoplasm | Immunologic Deficiency SyndromeUnited States
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Luye Pharma Group Ltd.CompletedMental Disorders | Psychotic Disorders | Mood Disorders | Schizophrenia | Schizophrenia Spectrum and Other Psychotic Disorders | Molecular Mechanisms of Pharmacological Action | Tranquilizing Agents | Physiological Effects of Drugs | Psychotropic Drugs | Antipsychotic Agents | Neurotransmitter Agents | Central...United States
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Eric Stephen Winer, MDRecruitingAcute Myeloid Leukemia | Myelodysplastic Syndrome With Excess Blasts-2United States
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The Cleveland ClinicBristol-Myers SquibbWithdrawnRheumatoid Arthritis | Inflammatory Arthritis | Primary Sjogren's Syndrome | Secondary Sjogren's SyndromeUnited States
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Crinetics Pharmaceuticals Inc.RecruitingCushing Syndrome | Cushing Disease | Ectopic ACTH SyndromeUnited States
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TetraLogic PharmaceuticalsCompletedMyelodysplastic SyndromeUnited States
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University of MichiganNational Center for Complementary and Integrative Health (NCCIH)RecruitingChronic Pain | Complex Regional Pain Syndromes | Neuropathic Pain | Failed Back Surgery SyndromeUnited States
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Albany Medical CollegeCompletedChronic Pain | Complex Regional Pain Syndromes | Neuropathic Pain | Failed Back Surgery SyndromeUnited States
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Diane GeorgeActive, not recruitingSickle Cell Disease | Hemoglobinopathies | Severe Congenital Neutropenia | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Macrophage Activation Syndrome | Bone Marrow Failure Syndrome | Amegakaryocytic Thrombocytopenia | Schwachman Diamond Syndrome | Primary Immunodeficiency Syndromes | Acquired Immunodeficiency... and other conditionsUnited States
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Remix TherapeuticsRecruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | Acute Myeloid Leukemia Refractory | Higher Risk Myelodysplastic SyndromesUnited States
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Johnson & Johnson Pharmaceutical Research & Development...TerminatedMyelodysplastic Syndromes | Advanced or Refractory LeukemiaUnited States
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University of California, San DiegoRecruitingComplex Regional Pain SyndromeUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)RecruitingAcute Myeloid Leukemia | Recurrent Acute Myeloid Leukemia | Recurrent Myelodysplastic Syndrome | Refractory Acute Myeloid Leukemia | Refractory Myelodysplastic Syndrome | High Risk Myelodysplastic Syndrome | Blasts More Than 10 Percent of Bone Marrow Nucleated CellsUnited States
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Fred Hutchinson Cancer CenterCompletedChronic Myelomonocytic Leukemia | Myelodysplastic Syndrome | Secondary Myelodysplastic Syndrome | de Novo Myelodysplastic SyndromeUnited States
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Washington University School of MedicineCompletedMyelodysplastic Syndromes | Leukemia, Myeloid, AcuteUnited States
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OHSU Knight Cancer InstituteOregon Health and Science University; Oryzon Genomics S.A.Not yet recruitingAcute Myeloid Leukemia | Myelodysplastic Syndrome/Acute Myeloid LeukemiaUnited States
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Masonic Cancer Center, University of MinnesotaTerminatedMyelodysplastic Syndromes | LeukemiaUnited States
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Boston Children's HospitalWithdrawnShort Bowel Syndrome | Catheter Related InfectionsUnited States
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M.D. Anderson Cancer CenterIncyte CorporationCompletedLeukemiaUnited States
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NYU Langone HealthPTC TherapeuticsCompleted
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Rush University Medical CenterCelgene CorporationTerminated
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M.D. Anderson Cancer CenterBristol-Myers SquibbTerminatedLeukemiaUnited States
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M.D. Anderson Cancer CenterCTI BioPharmaTerminated
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M.D. Anderson Cancer CenterS*BIOTerminated
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H. Lee Moffitt Cancer Center and Research InstituteCelgene CorporationCompleted
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UConn HealthCompletedOrofacial Pain | Myofascial Pain Dysfunction Syndrome | Temporomandibular Joint SyndromeUnited States
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H. Lee Moffitt Cancer Center and Research InstitutePfizerCompletedChronic Myelomonocytic Leukemia (CMML) | Myelodysplastic Syndrome (MDS)United States
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Emory UniversityGrady Health SystemCompleted
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Wake Forest University Health SciencesNational Cancer Institute (NCI)WithdrawnMyelodysplastic Syndromes | Progressive DiseaseUnited States
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Children's Hospital of PhiladelphiaCompletedBone Marrow Failure Syndromes | Immunodeficiencies | Immune Dysregulation SyndromesUnited States
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Luye Pharma Group Ltd.CompletedMental Disorders | Psychotic Disorders | Mood Disorders | Schizophrenia | Molecular Mechanisms of Pharmacological Action | Tranquilizing Agents | Physiological Effects of Drugs | Psychotropic Drugs | Antipsychotic Agents | Central Nervous System Depressants | Neurotransmitter Agents | Schizophrenia SpectrumUnited States
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Washington University School of MedicineWithdrawnBruxism | Temporomandibular Joint Disorders | Temporomandibular Joint Dysfunction Syndrome | Myofascial Pain Dysfunction Syndrome, Temporomandibular JointUnited States
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Ohio State UniversityPfizer; PTEN ResearchActive, not recruitingCowden Syndrome | Polyposis | PTEN Gene Mutation | PTEN Hamartoma Tumor Syndrome | PTEN Hamartoma Syndrome | Bannayan Syndrome | Bannayan Zonana SyndromeUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI); Genentech, Inc.RecruitingRecurrent Chronic Myelomonocytic Leukemia | Recurrent Myelodysplastic Syndrome | Refractory Chronic Myelomonocytic Leukemia | Refractory Myelodysplastic Syndrome | Therapy-Related Myelodysplastic SyndromeUnited States
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Johns Hopkins UniversityVascular Birthmarks FoundationCompletedEpilepsy | Sturge Weber SyndromeUnited States