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Clinical Trials on Spinocerebellar Ataxia Autosomal Recessive 7
Total 257 results
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University of FloridaNational Institutes of Health (NIH); National Institute on Deafness and Other...WithdrawnStroke | Dysphagia | Spinocerebellar Ataxia | Dysarthria | Cerebral Stroke
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Matrix Biomed, Inc.The University of Texas Health Science Center, HoustonNot yet recruitingAtaxia Telangiectasia | Ataxia Telangiectasia Louis-Bar | Ataxia Telangiectasia in ChildrenUnited States
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Otsuka Pharmaceutical Development & Commercialization...RecruitingAutosomal Recessive Polycystic Kidney Disease (ARPKD)United States, Belgium, Spain, Germany, United Kingdom, Poland
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Johns Hopkins UniversityTerminatedAtaxia-Telangiectasia (A-T)United States
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NHS TaysideUniversity of DundeeCompletedAtaxia-TelangiectasiaUnited Kingdom
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St. Jude Children's Research HospitalNational Cancer Institute (NCI); Children's Hospital of PhiladelphiaCompletedAtaxia-TelangiectasiaUnited States
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Institute of Child HealthGreat Ormond Street Hospital for Children NHS Foundation TrustCompletedAtaxia Telangiectasia (AT)United Kingdom
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The University of QueenslandNational Health and Medical Research Council, AustraliaCompletedAtaxia TelangiectasiaAustralia
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Kadmon Corporation, LLCCompletedPolycystic Kidney, Autosomal RecessiveUnited States
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Quince Therapeutics S.p.A.BiotrialNot yet recruitingAtaxia TelangiectasiaBelgium, United States, Denmark, Germany, Italy, Norway, Poland, Spain, United Kingdom
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ErydelRecruitingAtaxia TelangiectasiaUnited States, Australia, Belgium, Germany, India, Italy, Poland, Spain, Tunisia
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Acasti Pharma Inc.Active, not recruitingAtaxia TelangiectasiaCanada
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University Hospital, AkershusOslo University Hospital; University Hospital of North Norway; University of... and other collaboratorsActive, not recruitingAtaxia TelangiectasiaNorway
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Johann Wolfgang Goethe University HospitalUnknown
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ErydelCompletedAtaxia TelangiectasiaItaly, United States, India, Israel
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The University of QueenslandNot yet recruitingAtaxia TelangiectasiaAustralia
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University of NottinghamNottingham University Hospitals NHS Trust; Action for A-TCompleted
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University of NottinghamNottingham University Hospitals NHS Trust; Royal Papworth HospitalActive, not recruitingAtaxia TelangiectasiaUnited Kingdom
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Johns Hopkins UniversityCompleted
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Johann Wolfgang Goethe University HospitalCompletedAtaxia Telangiectasia
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Sheba Medical CenterUnknownAtaxia TelangiectasiaIsrael
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Sheba Medical CenterUnknownAtaxia TelangiectasiaIsrael
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Johann Wolfgang Goethe University HospitalCompletedAtaxia TelangiectasiaGermany
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University of PlymouthRecruitingAtaxia Telangiectasia | Ataxia Telangiectasia in ChildrenUnited Kingdom
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Radboud University Medical CenterA-T Children's Project; Twan foundation (https://twanfoundation.nl)CompletedAtaxia Telangiectasia | ATM Gene MutationNetherlands
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Federal Research Institute of Pediatric Hematology...CompletedAtaxia Telangiectasia | DysmetriaRussian Federation
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IntraBio IncRecruitingAtaxia Telangiectasia | Louis Bar SyndromeSpain, United States, Germany, United Kingdom
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General Hospital of Chinese Armed Police ForcesUnknownHereditary Cerebellar Ataxia.China
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Quince Therapeutics S.p.A.CompletedGenetic Syndrome | Nervous System DiseaseIndia, United States, Australia, Germany, Italy, Norway, Poland, Spain, Tunisia, United Kingdom, Israel, Belgium
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Santhera PharmaceuticalsCompletedFreidreich's AtaxiaGermany, Netherlands, France, Austria, Belgium
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Institut National de la Santé Et de la Recherche...Not yet recruiting
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PTC TherapeuticsActive, not recruitingFriedreich AtaxiaUnited States
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PTC TherapeuticsEnrolling by invitationFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain
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PTC TherapeuticsCompletedFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain
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Children's Hospital of PhiladelphiaFriedreich's Ataxia Research Alliance; Stealth BioTherapeutics Inc.Active, not recruitingFriedreich AtaxiaUnited States
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Metro International Biotech, LLCChildren's Hospital of PhiladelphiaCompleted
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Santhera PharmaceuticalsCompletedFriedreich's AtaxiaUnited States
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Design TherapeuticsCompleted
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Minoryx Therapeutics, S.L.CompletedFriedreich AtaxiaSpain, Belgium, France, Germany
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Larimar Therapeutics, Inc.Veristat, Inc.; Metrum Research Group, LLCCompletedFriedreich AtaxiaUnited States
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ShireCompletedFriedreich's AtaxiaUnited States
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National Institute of Neurological Disorders and...Completed
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University of South FloridaFriedreich's Ataxia Research Alliance; Edison Pharmaceuticals IncCompleted
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University of South FloridaUnknownFriedreich's AtaxiaUnited States
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Penwest Pharmaceuticals Co.CompletedFriedreich's AtaxiaUnited States
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Federico II UniversityCompleted
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National Institute of Neurological Disorders and...Completed
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Newcastle-upon-Tyne Hospitals NHS TrustRecruitingBethlem Myopathy | Ullrich Congenital Muscular Dystrophy 1, Digenic, Col6A1/Col6A2 | Ullrich Congenital Muscular Dystrophy 1, Autosomal Recessive | Ullrich Congenital Muscular Dystrophy 1, Autosomal Dominant | Bethlem Myopathy 1, Autosomal Recessive | UCMD | BTHLM1United Kingdom
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Shenzhen Beike Bio-Technology Co., Ltd.The Affiliated Nanjing Drum Tower Hospital of Nanjing University Medical... and other collaboratorsUnknown
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Johann Wolfgang Goethe University HospitalUnknownGrowth Failure | Ataxia TelangiectasiaGermany