- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Syndrome d'immunodéficience hyper-IgM, type 1
Total 478 results
-
University of UtahUniversity of British Columbia; Children's Hospital Medical Center, Cincinnati and other collaboratorsTerminatedNeurofibromatosis Type 1 (NF1)United States, Canada
-
National Cancer Institute (NCI)Active, not recruitingChronic Myelomonocytic Leukemia | Myelodysplastic Syndrome | Myelodysplastic Syndrome With Excess Blasts | Chronic Myelomonocytic Leukemia-1 | Chronic Myelomonocytic Leukemia-2 | Myelodysplastic Syndrome With Excess Blasts-1 | Myelodysplastic Syndrome/Acute Myeloid LeukemiaCanada, United States
-
University of PadovaUnknownCirrhosis | Type 1 Hepatorenal SyndromeItaly
-
University of Alabama at BirminghamCompletedNeurofibromatosis Type 1 and Growing or Symptomatic, Inoperable PNUnited States
-
Freeman-Sheldon Research Group, Inc.TerminatedCraniofacial Abnormalities | Arthrogryposis | Freeman-Sheldon Syndrome | Arthrogryposis Distal Type 2A | Whistling Face Syndrome | Craniocarpotarsal Dysplasia | Craniocarpotarsal Dystrophy | Freeman-Sheldon Syndrome Variant | Sheldon-Hall Syndrome | Arthrogryposis Distal Type 2B | Gordon Syndrome | Arthrogryposis... and other conditionsUnited States
-
Merck Sharp & Dohme LLCCompletedMyelodysplastic Syndromes | Anemia | Chronic Myelomonocytic Leukemia | Myelodysplastic Syndromes (MDS) | Chronic Myelomonocytic Leukemia (CMML) | Low to Intermediate-1 MDSUnited States, France
-
Vitaflo International, LtdWithdrawnEpilepsy | Glucose Transporter Type 1 Deficiency Syndrome | Ketogenic Dieting
-
SpringWorks Therapeutics, Inc.Active, not recruitingPlexiform Neurofibroma | Neurofibromatosis Type 1 (NF1)United States
-
Fondazione TelethonUnknownUsher Syndrome, Type 1BItaly, Netherlands, Spain
-
Novartis PharmaceuticalsTerminatedPlexiform Neurofibroma Associated With Neurofibromatosis Type 1Israel
-
Hospices Civils de LyonUnknownBrugada Syndrome Type 1France
-
Washington University School of MedicineRecruitingSevere Combined Immunodeficiency | Chronic Granulomatous Disease | DiGeorge Syndrome | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | X-linked Lymphoproliferative Syndrome | X-linked Agammaglobulinemia | Chediak-Higashi Syndrome | IPEX | Autoimmune Lymphoproliferative Syndrome | Common Variable... and other conditionsUnited States
-
University of California, IrvineDoris Duke Charitable FoundationWithdrawnMetabolic Syndrome | Type 1 Diabetes | Type 2 DiabetesUnited States
-
MacroGenicsNational Institute of Allergy and Infectious Diseases (NIAID); National Institutes... and other collaboratorsActive, not recruitingHuman Immunodeficiency Virus I Infection | Immunodeficiency Virus Type 1, Human | Human Immunodeficiency Virus Type 1United States
-
Dufresne, Craig, MD, PCRecruitingFreeman-Sheldon Syndrome | Whistling Face Syndrome | Freeman-Sheldon Syndrome Variant | Sheldon-Hall Syndrome | Gordon Syndrome | Arthrogryposis Distal Type 3 | Arthrogryposis Distal Type 1 | Freeman-Burian SyndromeUnited States
-
ViiV HealthcareJanssen Research and DevelopmentCompletedHuman Immunodeficiency Virus Type 1 (HIV-1)Germany, Spain, United States, Italy, Canada, Argentina, Sweden
-
Janssen PharmaceuticaWithdrawnHuman Immunodeficiency Virus Type 1 (HIV-1) Infection
-
Joslin Diabetes CenterImmusanT, Inc.CompletedType 1 Diabetes | Celiac DiseaseUnited States
-
AstraZenecaCompletedHealthy Participants | Neurofibromatosis Type 1 (NF1)-Related Plexiform Neurofibromas (PNs)United States
-
TC Erciyes UniversityRecruitingType1diabetes | Metabolic Syndrome | Nursing CariesTurkey
-
Reata, a wholly owned subsidiary of BiogenCompletedFocal Segmental Glomerulosclerosis | IgA Nephropathy | Autosomal Dominant Polycystic Kidney | CKD Associated With Type 1 DiabetesUnited States
-
ViiV HealthcareGlaxoSmithKline; Janssen PharmaceuticalsCompletedHuman Immunodeficiency Virus Type 1 (HIV-1)United States, Spain, Canada, United Kingdom, South Africa, Japan
-
Pacific Northwest Research InstituteUniversity of ExeterEnrolling by invitationType 1 Diabetes | Celiac DiseaseUnited States
-
Centre Hospitalier Universitaire DijonUnknownType 1-Multiple Endocrine Neoplasia SyndromeFrance
-
Mozart Therapeutics Australia Pty LtdNot yet recruitingType 1 Diabetes | Celiac Disease | Healthy VolunteersAustralia
-
University Hospital, GrenobleResMed; VitalAireCompleted
-
National Cancer Institute (NCI)RecruitingNeurofibromatosis 1 | Noonan Syndrome | Legius Syndrome | Cardiofaciocutaneous Syndrome | Costello SyndromeUnited States
-
SpringWorks Therapeutics, Inc.AvailableNeurofibromatosis Type 1-Associated Plexiform Neurofibromas | Histiocytic Neoplasm | Other MAP-K Pathway Driven Diseases
-
Gilead SciencesTerminatedHuman Immunodeficiency Virus Type 1 (HIV-1) InfectionUnited States
-
AstraZenecaApproved for marketingNF type1 With Inoperable Plexiform NeurofibromasUnited States
-
Sanford HealthUniversity of Exeter; The Leona M. and Harry B. Helmsley Charitable Trust; Pacific...RecruitingType 1 Diabetes | Celiac DiseaseUnited States
-
Children's Hospital Medical Center, CincinnatiRecruitingNeurofibromatosis 1 | Noonan Syndrome | Legius Syndrome | Cardiofaciocutaneous Syndrome | Costello Syndrome | SYNGAP1-Related Intellectual Disability | DLG4 | RAS Mutation | Noonan Syndrome With Multiple Lentigines | Noonan Neurofibromatosis Syndrome | Smith-Kingsmore Syndrome | MTOR Gene Mutation | GATOR-1 Gene... and other conditionsUnited States
-
Ultragenyx Pharmaceutical IncTerminatedGlucose Transporter Type 1 Deficiency SyndromeUnited States, Spain, Denmark, United Kingdom, Australia
-
Vitaflo International, LtdCompletedIntractable Epilepsy | Glucose Transporter Type 1 Deficiency Syndrome | Ketogenic DietingUnited Kingdom
-
Vitaflo International, LtdCompletedGlucose Transporter Type 1 Deficiency Syndrome | Ketogenic Dieting | Epilepsy IntractableUnited Kingdom
-
Ann & Robert H Lurie Children's Hospital of ChicagoNational Institute of Neurological Disorders and Stroke (NINDS); Children's...RecruitingNeurofibromatosis 1 | Neurofibromatosis Type 1 | NF1United States
-
Guy's and St Thomas' NHS Foundation TrustRecruitingNeurofibromatosis Type 1United Kingdom
-
University Hospital, Strasbourg, FranceRecruitingNeurofibromatosis Type 1France
-
National Cancer Institute (NCI)CompletedNeurofibroma | Neurofibromatosis Type 1United States
-
Joergen SerupSahlgrenska University Hospital, SwedenActive, not recruitingCutaneous NeurofibromaDenmark, Sweden
-
Centre Leon BerardRecruitingNeurofibroma | Neurofibroma, PlexiformFrance
-
AstraZenecaMerck Sharp & Dohme LLCActive, not recruitingNeurofibromatosis Type 1United States, Spain, Germany, Netherlands, Russian Federation, Italy, Japan
-
Shriners Hospitals for ChildrenCompletedNeurofibromatosis Type 1United States
-
Washington University School of MedicineCompleted
-
Ann & Robert H Lurie Children's Hospital of ChicagoCompleted
-
KU LeuvenUnknownNeurofibromatosis Type 1Belgium
-
Instituto Nacional de Cardiologia Ignacio ChavezEchoNous Inc.RecruitingCardiorenal Syndrome Type 1Mexico
-
Chulalongkorn UniversityNot yet recruitingEmpagliflozin in Cardiorenal Syndrome Type 1Thailand
-
AstraZenecaRecruitingNeurofibromatosis Type 1Portugal, Spain, United Kingdom, Israel, France, Italy, Switzerland, Germany, Austria