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Clinical Trials on Thalassemia
Total 425 results
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Emmaus Medical, Inc.FDA Office of Orphan Products DevelopmentCompletedSickle Cell Anemia | ThalassemiaUnited States
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Gamida Cell ltdTerminatedSickle Cell Disease | ThalassemiaFrance, United States
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National Heart, Lung, and Blood Institute (NHLBI)Children's National Research InstituteRecruitingSickle Cell Disease | Thalassemia | HemoglobinopathyUnited States
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Sohag UniversityNot yet recruiting
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HaEmek Medical Center, IsraelCompletedSickle Cell Anemia | ThalassemiaIsrael
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Assiut UniversityNot yet recruiting
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Baylor College of MedicineThe Methodist Hospital Research InstituteTerminatedSickle Cell Anemia | Thalassemia | HemoglobinopathyUnited States
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...TerminatedSickle Cell Anemia | Thalassemia | HemoglobinopathyUnited States
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The Hospital for Sick ChildrenLabatt Family Heart CentreRecruitingAtrial Flutter | Tachycardia, Supraventricular | Tachycardia, Atrioventricular Nodal Reentry | Tachycardia Atrial | Tachycardia, Reciprocating | Tachycardia, Paroxysmal | Fetal Hydrops | Tachycardia, Atrial EctopicUnited States, Hong Kong, Canada, Netherlands, Sweden, Australia, Brazil, Finland, France, Russian Federation, Spain, Czechia, Switzerland, United Kingdom
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Beni-Suef UniversityBenha UniversityCompletedSickle Cell Disease | Hemoglobinopathies | Thalassemia | Nurse's RoleEgypt
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Dana-Farber Cancer InstituteMassachusetts General Hospital; Beth Israel Deaconess Medical Center; Emory University and other collaboratorsCompletedSickle Cell Disease | Hemoglobinopathies | ThalassemiaUnited States
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WestatEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingSickle Cell Disease | Thalassemia | Pediatric CancerUnited States, Brazil
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City of Hope Medical CenterCalifornia Institute for Regenerative Medicine (CIRM)Active, not recruitingSickle Cell Disease | Anemia, Sickle Cell | Hemoglobinopathies | Thalassemia | Sickle Cell DisorderUnited States
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Aga Khan UniversityCompleted
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Imperial College LondonCompleted
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Imara, Inc.CompletedSickle Cell DiseaseUnited States, United Kingdom
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UCSF Benioff Children's Hospital OaklandCompleted
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Swiss Federal Institute of TechnologyMahidol UniversityNot yet recruitingIron Overload | ThalassemiaThailand
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HaEmek Medical Center, IsraelCompletedIron Overload | ThalassemiaIsrael
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University of Milano BicoccaComitato Maria Letizia Verga,ItalyRecruitingLymphoma, Non-Hodgkin | Leukemia, Myeloid, Acute | Leukemia, B-cell | Adrenoleukodystrophy | Lymphoma, Hodgkin | Thalassemia Major | Leukemia, T Cell | DrepanocytosisItaly
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Hangzhou Zede Pharma-Tech Co., Ltd.RecruitingIron Overload | ThalassemiaChina
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Hangzhou Zede Pharma-Tech Co., Ltd.Completed
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Elliott VichinskyCompletedIron Overload | ThalassemiaUnited States
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HaEmek Medical Center, IsraelCompletedSickle Cell Anemia | ThalassemiaIsrael
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National Center for Research Resources (NCRR)University of California, Los AngelesCompletedThrombocytopenia | Inborn Errors of Metabolism | Metachromatic Leukodystrophy | Fanconi's Anemia | Thalassemia Major | Pure Red-Cell AplasiaUnited States
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HaEmek Medical Center, IsraelCompleted
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National Institute of Diabetes and Digestive and...Completed
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Hormozgan University of Medical SciencesCompletedIron Overload | Thalassemia | Transfusion Related ComplicationsIran, Islamic Republic of
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St. Jude Children's Research HospitalCompletedSickle Cell Disease | Thalassemia | Marrow AplasiaUnited States
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Diane GeorgeActive, not recruitingSickle Cell Disease | Hemoglobinopathies | Severe Congenital Neutropenia | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Macrophage Activation Syndrome | Bone Marrow Failure Syndrome | Amegakaryocytic Thrombocytopenia | Schwachman Diamond Syndrome | Primary Immunodeficiency Syndromes | Acquired Immunodeficiency... and other conditionsUnited States
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National Institute of Diabetes and Digestive and...Completed
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Children's Hospital of PhiladelphiaApoPharmaApproved for marketingIron OverloadUnited States
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The University of Hong KongQueen Mary Hospital, Hong KongNot yet recruitingThalassemia | Folic Acid Deficiency Anemia
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Children's Hospital Los AngelesNational Heart, Lung, and Blood Institute (NHLBI); Vanderbilt University Medical... and other collaboratorsCompletedSickle Cell Disease | Thalassemia | Healthy ControlsUnited States
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HaEmek Medical Center, IsraelCompletedSickle Cell Disease | ThalassemiaIsrael
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI)CompletedHypertension, Pulmonary | ThalassemiaUnited States
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Phoenix Children's HospitalCompletedMyelodysplastic Syndromes | Vitamin D Deficiency | Pediatric Cancer | Aplastic Anemia | Stem Cell Transplant Complications | Sickle Cell Anemia in Children | Thalassemia in Children | Blood Disorder | Pediatric Acute Myeloid Leukemia | Pediatric Acute Lymphoid LeukemiaUnited States
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Assistance Publique - Hôpitaux de ParisNovartisCompletedSickle Cell Disease | Thalassemia | MyelodysplasiaFrance
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Novartis PharmaceuticalsCompletedMyelodysplastic Syndrome | ThalassemiaRussian Federation
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Universitas PadjadjaranHasan Sadikin General HospitalCompletedVitamin D Deficiency | Tuberculosis | ThalassemiaIndonesia
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Baqiyatallah Medical Sciences UniversityGuilan University of Medical Sciences; Baqiyatallah Research Center for Gastroenterology... and other collaboratorsCompletedHepatitis C | ThalassemiaIran, Islamic Republic of
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI)CompletedHepatitis C | ThalassemiaUnited States, United Kingdom, Canada
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Ala'a ShararaGilead SciencesCompletedHepatitis C | ThalassemiaLebanon
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UCSF Benioff Children's Hospital OaklandFood and Drug Administration (FDA)CompletedSickle Cell Disease | Pulmonary Hypertension | ThalassemiaUnited States
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Emory UniversityCompletedSickle Cell Disease | Fanconi Anemia | Hurler Syndrome | Chronic Granulomatous Disease | Severe Congenital Neutropenia | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Glanzmann Thrombasthenia | Shwachman-Diamond Syndrome | Thalassemia Major | Leukocyte... and other conditionsUnited States
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Stanford UniversityUniversity of Alabama at Birmingham; University of MinnesotaCompletedSickle Cell Disease | Thalassemia | Diamond-Blackfan AnemiaUnited States
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Medical College of WisconsinNational Heart, Lung, and Blood Institute (NHLBI); University of Wisconsin,... and other collaboratorsRecruitingSudden Infant Death | Congenital Heart Disease | Pregnancy Loss | Gastroschisis | Fetal Death | Brugada Syndrome | High Risk Pregnancy | Stillbirth | Long QT Syndrome | Fetal Demise | Birth Defect | Twin Monochorionic Monoamniotic Placenta | Twin Twin Transfusion Syndrome | Fetal Hydrops | Fetal Arrhythmia | Intrauterine... and other conditionsUnited States
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UCSF Benioff Children's Hospital OaklandNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Medical... and other collaboratorsCompletedSickle Cell Disease | Thalassemia | Diamond-Blackfan AnemiaUnited Kingdom, United States, Germany
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National Heart, Lung, and Blood Institute (NHLBI)CompletedDiabetes Mellitus | Heart Disease | Thalassemia | HemochromatosisUnited States
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Duke UniversityCompletedHemoglobinopathies | Thalassemia | Lysosomal Storage Disease | Immunodeficiencies | Inborn Errors of Metabolism | Sickle Cell | Non Malignant Disorders | Congenital Marrow FailuresUnited States