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Clinical Trials on Ullrich Congenital Muscular Dystrophy
Total 2178 results
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Sanko UniversityCompletedCerebral Palsy | Muscular Dystrophy | Down Syndrome | Parents | Spina BifidaTurkey
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Tel-Aviv Sourasky Medical CenterUnknownProteinuria | Renal Function | Classic Bladder Exstrophy | GFRIsrael
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Vienna Institute for Research in Ocular SurgeryRecruitingMap Dot Fingerprint DystrophyAustria
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Optos, PLCJohns Hopkins University; University of Southern CaliforniaCompletedAge-Related Macular Degeneration | Diabetic Retinopathy | Macular Edema | Retinal Vein Occlusion | Geographic Atrophy | Epiretinal Membrane | Macular Hole | Pattern Dystrophy of Macula | Central Serous RetinopathyUnited States
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National Institute of Neurological Disorders and...RecruitingMuscular Dystrophy | Peripheral Neuropathy | Normal Physiology | Motor Neuron DisorderUnited States
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Foundation Fighting BlindnessRecruitingRetinitis Pigmentosa | Choroideremia | Usher Syndrome | Batten Disease | Leber Congenital Amaurosis | Goldmann-Favre Syndrome | Kearns-Sayre Syndrome | Retinal Disease | Bardet-Biedl Syndrome | Stargardt Disease | Cone Dystrophy | Retinoschisis | Achromatopsia | Gyrate Atrophy | Eye Diseases Hereditary | Bassen-Kornzweig... and other conditionsUnited States
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Rigshospitalet, DenmarkCompletedNon-Dystrophic Myotonia | Myotonia CongenitaDenmark
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Kahramanmaras Sutcu Imam UniversityCompletedCerebral Palsy | Muscular Dystrophy | Caregiver Burden | Down Syndrome | Spina Bifida | Disabilities MultipleTurkey
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National Eye Institute (NEI)TerminatedInherited Retinal Degeneration | Inherited Ophthalmic DiseasesUnited States
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MeiraGTx UK II LtdSyne Qua Non LimitedCompletedEye Diseases | Retinal Diseases | Eye Diseases, Hereditary | Leber Congenital Amaurosis (LCA)United States, United Kingdom
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The Cleveland ClinicNational Eye Institute (NEI)RecruitingRetinal Diseases | Retinal Detachment | Epiretinal Membrane | Fuchs Endothelial Dystrophy | Macular HoleUnited States
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Assiut UniversityNot yet recruiting
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Johns Hopkins UniversityCompletedBladder ExstrophyUnited States
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Connecticut Children's Medical CenterCompletedBladder ExstrophyUnited States
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khadija liaquatCompletedTorticollis CongenitalPakistan
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Rigshospitalet, DenmarkCompletedMuscular Dystrophy | Mitochondrial Disease | Metabolic MyopathyDenmark
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Lupin Ltd.Recruiting
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Lupin Ltd.Active, not recruitingMyotonic DystrophyFrance, Germany, United Kingdom
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University of NancyCentral Hospital, Nancy, FranceCompleted
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University of VersaillesAssistance Publique - Hôpitaux de Paris; Association Française contre les Myopathies...Completed
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Massachusetts General HospitalBeth Israel Deaconess Medical Center; Brigham and Women's Hospital; University...Recruiting
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Newcastle UniversityRecruiting
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Hospices Civils de LyonWithdrawn
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Assistance Publique - Hôpitaux de ParisNot yet recruitingHemophilia A | Hemophilia B | Cystic Fibrosis | Sickle Cell Disease | Muscular Dystrophy, Duchenne | Fragile X Syndrome | Huntington Disease | Myotonic Dystrophy | Autosomal Recessive Polycystic Kidney Disease | Neurofibromatosis-Noonan Syndrome | Muscular Dystrophy, Becker | Invasive PreNatal Diagnosis in a... and other conditionsFrance
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University Hospital HeidelbergRecruitingCardiomyopathies | Skeletal Muscle DisorderGermany
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Koç UniversityRecruitingMuscular Dystrophies | Telemedicine | Proximal MyopathyTurkey
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Poitiers University HospitalTerminated
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University of AarhusUnknownGlycogen Storage Disease Type 2 | Dystrophia MyotonicaDenmark
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University of ChicagoRecruitingMuscular Dystrophy | Arrhythmia | CardiomyopathyUnited States
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Centre d'Investigation Clinique et Technologique...UnknownHeart, Respiratory, Disease, FunctionalFrance
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Rigshospitalet, DenmarkRecruitingCerebral Palsy | Muscular DystrophiesDenmark
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University of Southern CaliforniaRecruitingRecessive Dystrophic Epidermolysis BullosaUnited States
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Stanford UniversityRecruitingEpidermolysis Bullosa DystrophicaUnited States
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Phoenix Tissue Repair, Inc.CompletedRecessive Dystrophic Epidermolysis BullosaUnited States
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Fondazione Serena Onlus - Centro Clinico NeMO MilanoAzienda Ospedaliera Città della Salute e della Scienza di Torino; Fondazione... and other collaboratorsActive, not recruiting
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Nantes University HospitalCompletedLeber Congenital AmaurosisFrance
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Phoenicis TherapeuticsNot yet recruitingDystrophic Epidermolysis BullosaUnited States
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Thomas Jefferson UniversityOnconova Therapeutics, Inc.RecruitingRecessive Dystrophic Epidermolysis BullosaUnited States
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Castle Creek Biosciences, LLC.Active, not recruitingRecessive Dystrophic Epidermolysis BullosaUnited States
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Phoenix Tissue Repair, Inc.Phoenix Tissue Repair, a BridgeBio companyCompletedRecessive Dystrophic Epidermolysis BullosaUnited States
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RHEACELL GmbH & Co. KGFGK Clinical Research GmbH; Ticeba GmbH; Granzer Regulatory Consulting & ServicesCompletedRecessive Dystrophic Epidermolysis BullosaUnited States, Austria, France, Germany, United Kingdom
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Phoenix Tissue Repair, Inc.CompletedRecessive Dystrophic Epidermolysis BullosaUnited States
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Gangnam Severance HospitalDaewoong Pharmaceutical Co. LTD.CompletedRecessive Dystrophic Epidermolysis BullosaKorea, Republic of
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King's College LondonUniversity College, LondonCompletedRecessive Dystrophic Epidermolysis BullosaUnited Kingdom
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Stanford UniversityCompletedEpidermolysis Bullosa DystrophicaUnited States
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Abeona Therapeutics, IncNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedEpidermolysis Bullosa | Epidermolysis Bullosa DystrophicaUnited States
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Holostem Terapie Avanzate s.r.l.Paracelsus Medical UniversityTerminatedRecessive Dystrophic Epidermolysis BullosaAustria
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Columbia UniversityTerminatedEpidermolysis BullosaUnited States
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University of Southern CaliforniaCompletedRecessive Dystrophic Epidermolysis Bullosa
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University of Southern CaliforniaCompleted