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Clinical Trials on Ullrich Congenital Muscular Dystrophy
Total 2142 results
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Hôpital CochinAssociation Monégasque contre les MyopathiesUnknownDuchenne Muscular Dystrophy | Duchenne Muscular Dystrophy-Associated Dilated CardiomyopathyFrance
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingDuchenne Muscular Dystrophy | Natural History | Motor Function; RetardationItaly
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Avidity Biosciences, Inc.Enrolling by invitationDuchenne Muscular Dystrophy | DMD | Exon 44 | DuchenneUnited States
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Hacettepe UniversityCompletedDuchenne Muscular Dystrophy | Gait Disorders in ChildrenTurkey
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Bioblast Pharma Ltd.WithdrawnOculopharyngeal Muscular DystrophyCanada
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National Human Genome Research Institute (NHGRI)TerminatedCommunication | Genetic DiseaseUnited States
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Craig McDonald, MDCardero Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Benha UniversityCompletedDuchenne Muscular Dystrophy | Inflammatory MyopathyEgypt
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyUnited States, Netherlands, Belgium, Germany, Argentina, Brazil, France, Italy, Sweden, Turkey
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Shriners Hospitals for ChildrenCompletedDuchenne Muscular DystrophyUnited States
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Wake Forest University Health SciencesMuscular Dystrophy AssociationCompletedMuscular Dystrophies, Limb-Girdle (GENETICALLY CONFIRMED)United States
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Hacettepe UniversityCompletedDuchenne Muscular Dystrophy | Upper Limb Function | Respiratory Function Test
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Children's Hospital of Eastern OntarioJesse's Journey-The Foundation for Gene and Cell TherapyCompletedDuchenne Muscular DystrophyCanada
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Monica Levy AndersenCompletedOther Diseases or ConditionsBrazil
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PTC TherapeuticsMuscular Dystrophy AssociationCompletedDuchenne Muscular DystrophyUnited States
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Sahra ŞirvanEnrolling by invitationDuchenne Muscular DystrophyTurkey
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular DystrophyUnited States
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University Hospital, ToulouseUnknownDuchenne Muscular DystrophyFrance
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Hacettepe UniversityCompletedDuchenne Muscular DystrophyTurkey
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Oslo University HospitalUniversity Hospital of North Norway; The Research Council of NorwayCompletedDuchenne Muscular DystrophyNorway
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University of CalgaryMuscular Dystrophy CanadaEnrolling by invitationMuscular Dystrophies | Oculopharyngeal Muscular Dystrophy | Myopathy; HereditaryCanada
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AbiliTech Medical Inc.Richard M. Schulze Family FoundationRecruitingCerebral Palsy | Muscular Dystrophies | Duchenne Muscular Dystrophy | Becker Muscular Dystrophy | Spinal Muscular Atrophy | Limb Girdle Muscular Dystrophy | FSHDUnited States
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Mayo ClinicNational Eye Institute (NEI)CompletedRetinal Disease | Best Vitelliform Macular Dystrophy | Bestrophinopathy | Adult Onset Vitelliform Macular Dystrophy | Autosomal Dominant VitreoretinalchoroidopathyUnited States
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Hacettepe UniversityCompletedDuchenne Muscular Dystrophy | Muscle Strength | Hamstring Contractures | Lower ExtremityTurkey
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PTC TherapeuticsEnrolling by invitationDuchenne Muscular DystrophyUnited States, Canada
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Hacettepe UniversityCompletedGait Disorders, Neurologic | Body Posture | Balance | Foot PostureTurkey
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L.V. Prasad Eye InstituteAllerganRecruitingCongenital Hereditary Endothelial Dystrophy of CorneaIndia
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Suzuka HospitalNagoya UniversityUnknownCardiomyopathies | Duchenne Muscular DystrophyJapan
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Asklepios Biopharmaceutical, Inc.RecruitingMuscular Dystrophy | Limb Girdle Muscular Dystrophy | LGMD2I | LGMD | Limb-Girdle Muscular Dystrophy Type 2 | LGMD2 | FKRP | FKRP Mutation | Fukutin Related ProteinUnited States
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Capricor Inc.CompletedDuchenne Muscular DystrophyUnited States
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Nationwide Children's HospitalParent Project Muscular DystrophyCompletedBecker Muscular Dystrophy | Sporadic Inclusion Body MyositisUnited States
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Capricor Inc.CompletedDuchenne Muscular Dystrophy | CardiomyopathyUnited States
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Subha RamanBallou SkiesCompletedDuchenne Muscular DystrophyUnited States
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Holland Bloorview Kids Rehabilitation HospitalChildren's Hospital of Eastern OntarioCompletedMuscular Dystrophies | Congenital MyopathyCanada
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Laval UniversityCompleted
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Vanderbilt University Medical CenterRecruitingDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, Duchenne | Musculoskeletal DiseaseUnited States, Taiwan, India, Korea, Republic of, Thailand, Australia, Brazil, Bulgaria, Canada, China, Hong Kong, Malaysia, Mexico, Poland, Puerto Rico, Russian Federation, Turkey, Japan
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Istituto Auxologico ItalianoCompletedOsteoporosis | Duchenne Muscular Dystrophy
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Assistance Publique - Hôpitaux de ParisAssociation Française contre les Myopathies (AFM), ParisCompletedHeart Failure | Duchenne Muscular Dystrophy | CardiomyopathyFrance
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Nationwide Children's HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedMuscular DystrophiesUnited States
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GenethonCompletedLimb Girdle Muscular Dystrophy Type 2C | Gamma-sarcoglycanopathyFrance
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Radboud University Medical CenterSolve FSHDRecruitingMuscular Dystrophy, FacioscapulohumeralNetherlands
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Centre Hospitalier Universitaire de NiceCompletedMuscular Dystrophy, FacioscapulohumeralFrance
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Centre Hospitalier Universitaire de NiceCompletedMuscular Dystrophy, FacioscapulohumeralFrance
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National Eye Institute (NEI)National Cancer Institute (NCI)RecruitingStargardt-Like Macular DystrophyUnited States
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Vanderbilt University Medical CenterRecruitingDuchenne Muscular DystrophyUnited States
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Peking Union Medical College HospitalNational Natural Science Foundation of China; Cancer Institute and Hospital...Recruiting
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Hacettepe UniversityCompletedDuchenne Muscular Dystrophy | Ambulation Difficulty | Ambulation Disorder, NeurologicTurkey
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Hacettepe UniversityCompletedDuchenne Muscular Dystrophy | Gait Disorders, Neurologic | Gait Disorders in ChildrenTurkey
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Newcastle-upon-Tyne Hospitals NHS TrustCompletedDuchenne Muscular DystrophyUnited Kingdom