- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on X-ALD in United States
Total 169552 results
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VegaVect, Inc.National Eye Institute (NEI)Active, not recruiting
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University of California, DavisNational Institute of Mental Health (NIMH)CompletedFragile X PremutationUnited States
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National Eye Institute (NEI)CompletedRetinoschisis | X-LinkedUnited States
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GE HealthcareCompleted
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University of MiamiJackson Health SystemNo longer available
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The University of Texas Health Science Center,...Samsung ElectronicsCompletedChest X-ray for Clinical EvaluationUnited States
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Retina Foundation of the SouthwestDSM Nutritional Products, Inc.; Foundation Fighting BlindnessCompletedRetinitis Pigmentosa | X-linked Genetic DiseasesUnited States
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Guido A. Davidzon, MD, SMWithdrawn
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Tetra Discovery PartnersCompletedFragile X Syndrome | Fra(X) Syndrome | FXSUnited States
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University of California, DavisUniversity of Alberta; St. Justine's HospitalRecruitingNeurobehavioral Manifestations | Genetic Diseases, X-Linked | Intellectual Disability | Fragile X Syndrome | Sex Chromosome Disorders | Fragile X Mental Retardation Syndrome | Trinucleotide Repeat Expansion | Fra(X) Syndrome | FXS | Mental Retardation, X LinkedUnited States, Canada
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University of FloridaAudentes TherapeuticsCompletedX-linked Myotubular MyopathyUnited States
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National Institute of Allergy and Infectious Diseases...RecruitingX-linked Severe Combined Immunodeficiency (XSCID)United States
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Marinus PharmaceuticalsUniversity of California, Davis; U.S. Army Medical Research and Development...Completed
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedFragile X Syndrome (FXS)United States
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.National Institutes of Health (NIH)CompletedFragile X SyndromeUnited States
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National Institute of Allergy and Infectious Diseases...TerminatedGrowth Failure | X-linked Severe Combined Immunodeficiency (XSCID) | Growth Hormone ResistenceUnited States
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National Eye Institute (NEI)CompletedRetinoschisis | X-LinkedUnited States
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James DowlingCanadian Institutes of Health Research (CIHR); Cures Within Reach; The Joshua... and other collaboratorsRecruitingX Linked Myotubular MyopathyUnited Kingdom, Canada, United States
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Cure CMDUniversity of Michigan; Congenital Muscle Disease International RegistrCompleted
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Children's Hospital Medical Center, CincinnatiRecruitingFragile X SyndromeUnited States
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Esoterix Genetic Laboratories, LLCUnknownFragile X SyndromeUnited States
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Nova Mentis Life Science CorpFourthWall TestingRecruitingAutism Spectrum Disorder | Fra(X) SyndromeUnited States
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St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI); Assisi Foundation; California...SuspendedSevere Combined Immunodeficiency Disease, X-linkedUnited States
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingFragile X SyndromeUnited States
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National Institute of Mental Health (NIMH)CompletedHealthy Volunteers | Fragile X SyndromeUnited States
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Stanford UniversityCompletedFragile X SyndromeUnited States
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University of California, DavisCompletedFragile X Syndrome | Genetic DiseasesUnited States
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University of California, DavisCompleted
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University of California, DavisThe National Fragile X FoundationCompleted
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Edimer PharmaceuticalsCompletedX Linked Hypohidrotic Ectodermal DysplasiaUnited States
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Stanford UniversityCompleted
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National Institute of Allergy and Infectious Diseases...CompletedGenetic Diseases, X-Linked | Lymphoproliferative Disease | X-Linked Lymphoproliferative DiseaseUnited States
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Massachusetts General HospitalNational Institutes of Health (NIH)UnknownHealthy | Fragile X SyndromeUnited States
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Craig EricksonHealx LimitedRecruitingFragile X SyndromeUnited States
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Elizabeth Berry-KravisCompletedFragile X SyndromeUnited States
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National Institute of Allergy and Infectious Diseases...UnknownX-Linked Combined Immunodeficiency DiseasesUnited States
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National Institute of Allergy and Infectious Diseases...CompletedSevere Combined ImmunodeficiencyUnited States
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Ovid Therapeutics Inc.CompletedFragile X Syndrome (FXS)United States
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Stanford UniversityTerminatedFragile X Syndrome (FXS) | Idiopathic Intellectual Developmental Disorder (IDD)United States
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Children's Hospital Medical Center, CincinnatiCompleted
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Randi J. Hagerman, MDCompleted
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Indiana UniversityIndiana Clinical and Translational Sciences InstituteCompleted
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Indiana University School of MedicineCompletedFragile X SyndromeUnited States
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Stanford UniversityNational Institute of Mental Health (NIMH); Autism SpeaksCompleted
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Edimer PharmaceuticalsCompletedX-linked Hypohidrotic Ectodermal DysplasiaUnited States
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Rowan UniversityUniversity of Pennsylvania; FRAXA Research FoundationUnknown
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Children's Hospital Medical Center, CincinnatiRush University Medical CenterCompleted
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Midwest Biomedical Research FoundationSuspended
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University of California, DavisNational Institute on Aging (NIA); Forest LaboratoriesCompletedFragile X-Associated Tremor/Ataxia Syndrome | Fragile X Premutation CarriersUnited States