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Clinical Trials on X-linked Lymphoproliferative Syndrome in Japan
Total 110 results
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Kyowa Kirin Co., Ltd.Active, not recruiting
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TakedaRecruitingSpinal and Bulbar Muscular AtrophyJapan
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Janssen Pharmaceutical K.K.RecruitingX-Linked Retinitis PigmentosaJapan
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GlaxoSmithKlineCompletedMucopolysaccharidosis IIJapan
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Janssen Pharmaceutical K.K.RecruitingX-Linked Retinitis PigmentosaJapan
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Mitsubishi Tanabe Pharma America Inc.RecruitingErythropoietic Protoporphyria (EPP) | X-Linked Protoporphyria (XLP)United States, Spain, France, United Kingdom, Japan, Italy, Australia, Bulgaria, Czechia, Netherlands, Poland
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JCR Pharmaceuticals Co., Ltd.Completed
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Taiho Pharmaceutical Co., Ltd.Completed
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National Center of Neurology and Psychiatry, JapanNippon Shinyaku Co., Ltd.Completed
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National Center of Neurology and Psychiatry, JapanNippon Shinyaku Co., Ltd.Completed
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Kyowa Kirin Co., Ltd.CompletedX-linked Hypophosphatemic Rickets/OsteomalaciaJapan, Korea, Republic of
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Kyowa Kirin Co., Ltd.CompletedX-linked Hypophosphatemic Rickets/OsteomalaciaJapan
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JCR Pharmaceuticals Co., Ltd.Completed
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JCR Pharmaceuticals Co., Ltd.Active, not recruitingMucopolysaccharidosis IIJapan
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Novo Nordisk A/SEnrolling by invitationHaemophilia A | Haemophilia BJapan
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Nippon Shinyaku Co., Ltd.Active, not recruiting
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Nagoya UniversityUnknownHypertension | Healthy | Diabetes Mellitus | Hyperlipidemia | Metabolic Syndrome XJapan
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Taiho Pharmaceutical Co., Ltd.RecruitingDuchenne Muscular DystrophyJapan
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Daiichi Sankyo Co., Ltd.Orphan Disease Treatment Institute Co., Ltd.Completed
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Daiichi Sankyo Co., Ltd.Active, not recruitingDuchenne Muscular DystrophyJapan
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Suzuka HospitalNagoya UniversityUnknownCardiomyopathies | Duchenne Muscular DystrophyJapan
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Kobe UniversityNobelpharma; Japan Medical AssociationUnknownMuscular Dystrophy, DuchenneJapan
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Taiho Pharmaceutical Co., Ltd.Completed
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With InhibitorsJapan
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With InhibitorsJapan
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With InhibitorsJapan
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Novartis PharmaceuticalsRecruitingNLRC4-GOF, AIFEC (Autoinflammation With Infantile Enterocolitis), XIAP Deficiency, CDC42 MutationsSpain, France, United States, Canada, Japan, United Kingdom, Turkey, Czechia, Italy
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BayerCompletedHemophilia A | Hemophilia BUkraine, United Kingdom, Bulgaria, Germany, Japan
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Baxalta now part of ShireTakedaCompleted
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Genzyme, a Sanofi CompanyCompleted
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A | Haemophilia BSpain, Germany, Japan
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-Linked HypophosphatemiaKorea, Republic of, Canada, United States, Australia, Japan, United Kingdom, Sweden
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CelgeneCompletedMyelodysplastic Syndromes | Multiple MyelomaJapan
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Weill Medical College of Cornell UniversityBayer; University Hospital, BonnCompletedHemophilia A | Hemophilia BUnited States, Israel, Australia, Italy, Sweden, Germany, Japan, Netherlands, Taiwan
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Genzyme, a Sanofi CompanyCompleted
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Novo Nordisk A/SEnrolling by invitation
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GlaxoSmithKlineActive, not recruiting
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Baxalta now part of ShireCompletedRecombinant Factor VIIa BI (rFVIIa BI) Treatment of Acute Bleeding Episodes Per an On-demand RegimenHemophilia A | Hemophilia BJapan, Russian Federation, Spain, United States, Poland, Romania, Serbia, Taiwan, Ukraine
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Keio UniversityCompletedAcute Lymphoblastic Leukemia | Myelodysplastic Syndrome | Acute Myelogenous Leukemia | Chronic Myelogenous LeukemiaJapan
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Cooperative International Neuromuscular Research...United States Department of DefenseCompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | Limb Girdle Muscular DystrophyUnited States, Japan, Canada
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Baxalta now part of ShireCompletedHemophilia BPoland, United Kingdom, Spain, Bulgaria, Romania, Japan, Russian Federation, Brazil, Chile, Sweden, Colombia, Ukraine, Argentina, Czechia
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CSL BehringCompletedHemophilia BUnited States, Japan, Israel, Austria, Bulgaria, France, Germany, Italy, Russian Federation, Spain
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.Active, not recruitingDuchenne Muscular DystrophyKorea, Republic of, Chile, Japan, China, United Kingdom, Netherlands, Spain, Norway, Russian Federation, Australia, Greece, Italy, New Zealand, Turkey, Mexico, Czechia, Canada
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Baxalta now part of ShireCompletedHemophilia A | Hemophilia B | Hemophilia A or B With InhibitorsPoland, United States, Bulgaria, Romania, Japan, Russian Federation, New Zealand, Croatia, Ukraine, Brazil
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Sarepta Therapeutics, Inc.Hoffmann-La RocheRecruitingDuchenne Muscular DystrophyBelgium, United States, Japan, Spain, Italy, United Kingdom
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PfizerTerminatedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Japan, Italy
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PfizerTerminatedDuchenne Muscular DystrophyUnited States, Australia, Canada, United Kingdom, Japan, Bulgaria, Italy, Poland
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BioMarin PharmaceuticalNo longer availableDuchenne Muscular DystrophyUnited States, Germany, United Kingdom, Japan, Netherlands, France, Spain, Korea, Republic of, Italy, Belgium, Taiwan, Argentina, Australia, Bulgaria, Czechia, Israel, Norway, Poland, Russian Federation, Turkey
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Baxalta now part of ShireCompletedHemophilia BTaiwan, Colombia, Argentina, Brazil, Bulgaria, Chile, Czechia, India, Ireland, Italy, Japan, Poland, Romania, Russian Federation, Sweden, Ukraine, United Kingdom