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Search clinical trials for: AAV2-hAADC
Total 131 results
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Selecta Biosciences, Inc.National Human Genome Research Institute (NHGRI)SuspendedMethylmalonic Acidemia (MMA)United States
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MeiraGTx UK II LtdSyne Qua Non Limited; EMAS PharmaActive, not recruitingAchromatopsiaUnited Kingdom, United States
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Celladon CorporationCompletedHeart Failure | Cardiomyopathies | Ischemic Cardiomyopathy | Non-ischemic CardiomyopathyUnited States, United Kingdom, Belgium, Germany, Poland, Israel, Netherlands, Hungary, Denmark, Sweden
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uniQure France SASRecruitingMesial Temporal Lobe EpilepsyUnited States
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaBelgium, Canada, United States, Israel, United Kingdom, Spain, Denmark, France, Italy, Netherlands, Switzerland
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CSL BehringEnrolling by invitation
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Terence FlotteMassachusetts General Hospital; University of Massachusetts, WorcesterActive, not recruitingTay-Sachs Disease | Sandhoff DiseaseUnited States
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MeiraGTx UK II LtdCompletedLeber Congenital AmaurosisUnited Kingdom, United States
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MeiraGTx UK II LtdSyne Qua Non Limited; EMAS PharmaCompleted
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REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Sangamo TherapeuticsCompletedIdiopathic Parkinson's DiseaseUnited States
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MeiraGTx UK II LtdSyne Qua Non LimitedCompletedEye Diseases | Retinal Diseases | Eye Diseases, Hereditary | Leber Congenital Amaurosis (LCA)United States, United Kingdom
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Peking University Third HospitalRecruitingBietti's Crystalline DystrophyChina
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Beijing Tongren HospitalRecruitingBietti's Crystalline DystrophyChina
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University of OxfordUniversity College, London; University of Southampton; Moorfields Eye Hospital... and other collaboratorsCompleted
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REGENXBIO Inc.Active, not recruitingNeuronal Ceroid Lipofuscinosis Type 2United Kingdom
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Baxalta now part of ShireTerminatedHemophilia BTurkey, Spain
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Libella Gene TherapeuticsUnknown
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Libella Gene TherapeuticsUnknownEvaluation of Safety and Tolerability of Libella Gene Therapy for Critical Limb Ischemia: AAV- hTERTCritical Limb IschemiaColombia
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VegaVect, Inc.National Eye Institute (NEI)Active, not recruiting
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Libella Gene TherapeuticsUnknownAlzheimer DiseaseColombia
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Mark TuszynskiOhio State UniversityRecruitingMild Cognitive Impairment | Alzheimer's DiseaseUnited States
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Lantu BiopharmaNot yet recruitingSpinal Muscular Atrophy
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King Khaled Eye Specialist HospitalKing Faisal Specialist Hospital & Research CenterCompletedRetinitis Pigmentosa | Retinal DiseaseSaudi Arabia
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PfizerActive, not recruitingHemophilia ASpain, Taiwan, Australia, United States, Japan, France, Turkey, Germany, Korea, Republic of, United Kingdom, Saudi Arabia, Canada, Greece, Sweden, Brazil, Italy
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MeiraGTx, LLCActive, not recruitingParkinson DiseaseUnited States
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University of Massachusetts, WorcesterNational Heart, Lung, and Blood Institute (NHLBI); University of Florida; National... and other collaboratorsCompletedAlpha 1-Antitrypsin DeficiencyUnited States
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CSL BehringRecruiting
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University of OxfordUniversity College, London; Moorfields Eye Hospital NHS Foundation TrustCompleted
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Neuracle Genetics, IncORA, Inc.RecruitingAge-Related Macular DegenerationCanada
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REGENXBIO Inc.National Heart, Lung, and Blood Institute (NHLBI)TerminatedHomozygous Familial Hypercholesterolemia (HoFH)United States, Canada, Italy, Netherlands
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Sardocor Corp.RecruitingHeart Failure, Diastolic | Heart Failure With Preserved Ejection FractionUnited States
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CSL BehringActive, not recruitingHemophilia BUnited States, Belgium, Netherlands, Denmark, Germany, Ireland, Sweden, United Kingdom
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GenethonCompletedLimb Girdle Muscular Dystrophy Type 2C | Gamma-sarcoglycanopathyFrance
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MeiraGTx UK II LtdJanssen Research & Development, LLCCompleted
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Aspa TherapeuticsRecruitingCanavan DiseaseUnited States
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Imperial College LondonBritish Heart Foundation; Leducq Foundation; Celladon CorporationTerminatedChronic Heart Failure | Patients That Have Received a Left Ventricular Assist DeviceUnited Kingdom
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J. Uriach and CompanyCompletedInsulin ResistanceSpain
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Sardocor Corp.Not yet recruitingDMD-Associated Dilated Cardiomyopathy
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W. Michael HootenNational Institute on Drug Abuse (NIDA)Recruiting
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MeiraGTx, LLCEnrolling by invitationParkinson DiseaseUnited States
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National Institute of Allergy and Infectious Diseases...Active, not recruitingHIV-1 Infected Adults With Controlled ViremiaUnited States
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Neurologix, Inc.Weill Medical College of Cornell University; North Shore University HospitalCompletedParkinson's DiseaseUnited States
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ArthrogenUnknown
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ArthrogenCentre for Human Drug Research (CHDR)UnknownArthritis, Rheumatoid | Osteo ArthritisNetherlands
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PfizerRecruitingHemophilia A | Hemophilia BAustralia, United States, Turkey
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Adrenas Therapeutics IncRecruitingCongenital Adrenal HyperplasiaUnited States
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Spark Therapeutics, Inc.Recruiting
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Second Affiliated Hospital, School of Medicine,...Recruiting