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Search clinical trials for: rAAV2/5-PBGD vector dosage 2
Total 201 results
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Digna Biotech S.L.University of Navarra; Porphyria Centre Sweden; UniQure N.V.; Nationales Centrum...CompletedAcute Intermittent PorphyriaSpain
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Affiliated Hospital of Guangdong Medical UniversityNot yet recruitingHemophilia B Without Inhibitor
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Zhejiang UniversityNot yet recruitingHemophilia B Without Inhibitor
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Affiliated Hospital of Guangdong Medical UniversityNot yet recruiting
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Innovent Biologics (Suzhou) Co. Ltd.Completed
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Pennington Biomedical Research CenterNational Center for Complementary and Integrative Health (NCCIH); Office of...CompletedDiabetes PreventionUnited States
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Novo Nordisk A/SCompletedType 2 Diabetes | Healthy VolunteersUnited States, Canada
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Taiho Pharmaceutical Co., Ltd.RecruitingChronic Spontaneous UrticariaJapan
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The University of Texas Health Science Center,...The Methodist Hospital Research Institute; MedStar National Rehabilitation...RecruitingSpinal Cord InjuriesUnited States
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Edgewise Therapeutics, Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Pulmongene Ltd.CompletedIdiopathic Pulmonary FibrosisAustralia
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AIM Vaccine Co., Ltd.First Affiliated Hospital Bengbu Medical College; Ningbo Rongan Biological...Not yet recruiting
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AIM Vaccine Co., Ltd.First Affiliated Hospital Bengbu Medical College; Ningbo Rongan Biological...Active, not recruiting
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CohBar, Inc.CompletedNonalcoholic Fatty Liver DiseaseUnited States
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National Cancer Institute (NCI)Terminated
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Sun Pharma Advanced Research Company LimitedCompleted
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PfizerCompleted
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PfizerCompleted
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Novo Nordisk A/SCompleted
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QurAlis CorporationRecruitingAmyotrophic Lateral SclerosisCanada, Germany, Netherlands, Ireland, United Kingdom, Belgium
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BiocadCompleted
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Janssen Research & Development, LLCCompleted
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GlaxoSmithKlineWithdrawnVenous ThromboembolismUnited States
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Janssen Research & Development, LLCActive, not recruitingCrohn's DiseaseUnited States, Israel, Japan, Belgium, Lebanon, Taiwan, Netherlands, Russian Federation, Korea, Republic of, Jordan, France, Portugal, Turkey, Greece, Canada, Germany, Malaysia, Belarus, Latvia, Poland, Australia, Italy, Croatia, China, United Kingdom and more
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BioMarin PharmaceuticalRecruitingHereditary Angioedema | HAEUnited States, Spain, Australia
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Memorial Sloan Kettering Cancer CenterCompletedMyelodysplastic Syndromes (MDS) | Acute Myelogenous Leukemia (AML)United States
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Boehringer IngelheimCompletedPulmonary Disease, Chronic ObstructiveNetherlands
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University Hospital, GhentCompleted
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AstraZenecaCompletedAsthma | Chronic Obstructive Pulmonary Disease (COPD)United Kingdom
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Lidian ChenPeking University Third HospitalNot yet recruiting
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Janssen Research & Development, LLCCompletedColitis, UlcerativeUnited States, Russian Federation, Australia, Poland, Germany, Brazil, Ukraine, Argentina, Mexico
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Longbio PharmaActive, not recruitingChronic Spontaneous UrticariaChina
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Longbio PharmaActive, not recruitingMyelodysplastic Syndrome (MDS)China
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Harry T Whelan, MDCompletedNeurofibromatosesUnited States
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BioNTech SEPfizerRecruitingCOVID-19 | Severe Acute Respiratory Syndrome Coronavirus 2 | SARS-CoV-2 VirusUnited States, Brazil, Puerto Rico
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PfizerCompleted
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Janssen Research & Development, LLCCompleted
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Helixmith Co., Ltd.UnknownIschemic Heart Disease | Acute Myocardial InfarctionKorea, Republic of
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Longbio PharmaRecruitingParoxysmal Nocturnal Hemoglobinuria (PNH)China
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Ikena OncologyGilead SciencesTerminatedBreast Cancer | Head and Neck Cancer | Gynecologic Cancer | Colorectal Cancer | Pancreatic Cancer | Gastric Adenocarcinoma | Lung Adenocarcinoma | Advanced Solid TumorUnited States
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LTN PHARMACEUTICALS, INC.CompletedProstate CancerUnited States
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Centre Hospitalier Universitaire de NīmesCompletedAmyotrophic Lateral SclerosisFrance, United Kingdom
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Rutgers, The State University of New JerseyNational Cancer Institute (NCI)CompletedAcute Myeloid Leukemia | Chronic Myelomonocytic Leukemia | Secondary Acute Myeloid Leukemia | Myelodysplastic Syndrome | Recurrent Acute Myeloid Leukemia | Refractory Acute Myeloid Leukemia | Myeloproliferative Neoplasm | Myeloblasts 10 Percent or More of Bone Marrow Nucleated CellsUnited States
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University of PennsylvaniaWalter Reed National Military Medical CenterRecruiting
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Shanghai Municipal Center for Disease Control and...Shanghai Institute Of Biological ProductsUnknown
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Radicle ScienceActive, not recruitingCognitive FunctionUnited States
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AstraZenecaCompletedAsthma (Part 1) | COPD (Part 2)United Kingdom
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NovartisTerminatedHypertensionUnited States, Denmark, Finland, Norway, Sweden