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Search clinical trials for: scAAV2/8-LP1-hFIXco
Total 60 results
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St. Jude Children's Research HospitalChildren's Hospital of Philadelphia; National Heart, Lung, and Blood Institute... and other collaboratorsActive, not recruitingHemophilia BUnited States, United Kingdom
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Peking University Third HospitalRecruitingBietti's Crystalline DystrophyChina
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Beijing Tongren HospitalRecruitingBietti's Crystalline DystrophyChina
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Chigenovo Co., LtdRecruitingBietti's Crystalline DystrophyChina
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University of ArkansasTerminatedBronchopulmonary DysplasiaUnited States
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Fondazione TelethonActive, not recruitingMucopolysaccharidosis Type VIItaly, Turkey
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University College, LondonMedical Research CouncilRecruiting
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City of Hope Medical CenterNational Cancer Institute (NCI)CompletedAcute Myeloid Leukemia Arising From Previous Myelodysplastic Syndrome | Recurrent Acute Myeloid Leukemia | Refractory Acute Myeloid LeukemiaUnited States
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Longbio PharmaActive, not recruitingChronic Spontaneous UrticariaChina
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Longbio PharmaActive, not recruitingMyelodysplastic Syndrome (MDS)China
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Longbio PharmaRecruitingParoxysmal Nocturnal Hemoglobinuria (PNH)China
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City of Hope Medical CenterNational Cancer Institute (NCI)RecruitingAcute Myeloid Leukemia | Recurrent Acute Myeloid Leukemia | Refractory Acute Myeloid LeukemiaUnited States
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Aphaia Pharma US LLCBioClinica, Inc.; ACC GmbH Analytical Clinical Concepts, Germany; Nova-Clin Medical... and other collaboratorsCompletedObesity | Metabolic SyndromeRomania
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI); FDA Office of Orphan Products DevelopmentCompletedLeukemia | Chronic Lymphocytic LeukemiaUnited States
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BiogenCompletedRenal Insufficiency | Congestive Heart FailureIsrael, Italy, United States, Finland, Canada, Australia, France, Netherlands, Poland, Bulgaria, Russian Federation, India, Brazil, Sweden, Romania, Czechia, Argentina, Germany
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St. Jude Children's Research HospitalRecruitingSickle Cell DiseaseUnited States
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Eda Cetin OzdemirCompletedPeriodontal DiseasesTurkey
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Humanity and Health Research CentreBeijing 302 Hospital; Nanfang Hospital of Southern Medical UniversityRecruitingChronic Hepatitis C InfectionChina
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University of Cape TownUppsala University; Liverpool School of Tropical Medicine; University of North...CompletedHIV | TuberculosisSouth Africa, Malawi
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Istituto Auxologico ItalianoUniversità Politecnica delle Marche; University of MilanCompleted
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Kyowa Kirin Co., Ltd.Kyowa Hakko Kirin Pharma, Inc.CompletedParkinson's DiseaseUnited States
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University Hospital, MontpellierClub anesthésie Reanimation ObstetricaleCompletedCaesarian SectionFrance
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Medical University of ViennaPolymun Scientific, Vienna, AustriaCompleted
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SWOG Cancer Research NetworkNational Cancer Institute (NCI)SuspendedStage II Bladder Cancer AJCC v8 | Bladder Carcinoma Infiltrating the Muscle of the Bladder Wall | Infiltrating Renal Pelvis and Ureter Urothelial CarcinomaUnited States
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Assistance Publique - Hôpitaux de ParisWithdrawnPulmonary Arterial Hypertension With Congenital Cardiac Shunt
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); Affini-T Therapeutics, Inc.Active, not recruiting
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Children's Oncology GroupNational Cancer Institute (NCI)Not yet recruitingMetastatic Osteosarcoma | Localized Osteosarcoma | Unresectable Osteosarcoma | Resectable Osteosarcoma
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedMedulloblastoma | Nevoid Basal Cell Carcinoma Syndrome | Desmoplastic/Nodular Medulloblastoma | Medulloblastoma With Extensive NodularityUnited States, Canada, Puerto Rico, Australia
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Children's Oncology GroupNot yet recruitingCentral Nervous System Germinoma | Diabetes Insipidus | Pineal Region Germinoma | Suprasellar Germinoma
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OHSU Knight Cancer InstituteNational Cancer Institute (NCI); Oregon Health and Science UniversityActive, not recruitingCentral Nervous System LymphomaUnited States
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National Cancer Institute (NCI)SuspendedMetastatic Osteosarcoma | Localized Osteosarcoma | High Grade Osteosarcoma | Secondary OsteosarcomaUnited States
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Children's Oncology GroupNational Cancer Institute (NCI); University College, London; Medical Research...CompletedMetastatic Osteosarcoma | Localized OsteosarcomaUnited States, Canada, Australia, New Zealand, Puerto Rico, Switzerland
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Roswell Park Cancer InstituteNational Comprehensive Cancer NetworkCompletedStage III Mantle Cell Lymphoma | Stage IV Mantle Cell Lymphoma | Stage I Mantle Cell Lymphoma | Stage II Contiguous Mantle Cell Lymphoma | Stage II Non-Contiguous Mantle Cell LymphomaUnited States
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National Cancer Institute (NCI)RecruitingRenal Pelvis and Ureter Urothelial CarcinomaUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)CompletedBurkitt Lymphoma | Acute Lymphoblastic Leukemia | Lymphoblastic Lymphoma | CD20 Positive | Adult Acute Lymphoblastic Leukemia in Complete Remission | Childhood Acute Lymphoblastic Leukemia in Complete Remission | Burkitt LeukemiaUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)Active, not recruitingMedulloblastoma | Untreated Childhood Supratentorial Primitive Neuroectodermal Tumor | Anaplastic Medulloblastoma | Supratentorial Embryonal Tumor, Not Otherwise SpecifiedUnited States, Canada, Australia, Puerto Rico
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National Cancer Institute (NCI)RecruitingB Acute Lymphoblastic Leukemia With t(9;22)(q34.1;q11.2); BCR-ABL1United States, Puerto Rico, Israel
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Northwestern UniversityNational Cancer Institute (NCI); Millennium Pharmaceuticals, Inc.Active, not recruitingDiffuse Large B-Cell Lymphoma | Plasmablastic Lymphoma | B-Cell Lymphoma, Unclassifiable, With Features Intermediate Between Diffuse Large B-Cell Lymphoma and Burkitt Lymphoma | Adult Burkitt Lymphoma | MYC Gene MutationUnited States
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National Cancer Institute (NCI)Active, not recruitingDiffuse Large B-Cell Lymphoma | High Grade B-Cell Lymphoma With MYC and BCL2 or BCL6 Rearrangements | Diffuse Large B-Cell Lymphoma, Not Otherwise Specified | Double-Expressor Lymphoma | EBV-Positive Diffuse Large B-Cell Lymphoma, Not Otherwise Specified | High Grade B-Cell Lymphoma, Not Otherwise... and other conditionsUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingMantle Cell LymphomaUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedChildhood Atypical Teratoid/Rhabdoid TumorUnited States, Canada, Australia
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingMantle Cell Lymphoma | Blastoid Variant Mantle Cell Lymphoma | Pleomorphic Variant Mantle Cell LymphomaUnited States
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M.D. Anderson Cancer CenterActive, not recruitingAcute Lymphoblastic Leukemia | Blast Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive | Philadelphia Chromosome Positive | B Acute Lymphoblastic Leukemia With t(9;22)(q34.1;q11.2); BCR-ABL1 | Untreated Adult Acute Lymphoblastic Leukemia | Accelerated Phase Chronic Myelogenous Leukemia,... and other conditionsUnited States
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National Cancer Institute (NCI)CompletedAnaplastic Large Cell Lymphoma, ALK-Positive | Ann Arbor Stage II Noncutaneous Childhood Anaplastic Large Cell Lymphoma | Ann Arbor Stage III Noncutaneous Childhood Anaplastic Large Cell Lymphoma | Ann Arbor Stage IV Noncutaneous Childhood Anaplastic Large Cell LymphomaUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)RecruitingT Acute Lymphoblastic Leukemia | T Lymphoblastic LymphomaUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)RecruitingB Acute Lymphoblastic Leukemia | B Lymphoblastic LymphomaUnited States
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OHSU Knight Cancer InstituteNational Cancer Institute (NCI)CompletedAcute Myeloid Leukemia | Acute Lymphoblastic LeukemiaUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)Active, not recruitingAcute Lymphoblastic Leukemia | Down Syndrome | Philadelphia Chromosome Positive | Childhood B Acute Lymphoblastic Leukemia With t(9;22)(q34.1;q11.2); BCR-ABL1 | Childhood B Acute Lymphoblastic Leukemia | Adult B Lymphoblastic Lymphoma | Ann Arbor Stage I B Lymphoblastic Lymphoma | Ann Arbor Stage... and other conditionsUnited States, Canada, Puerto Rico, Australia, New Zealand, Switzerland, Ireland
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)TerminatedB Acute Lymphoblastic Leukemia | B Acute Lymphoblastic Leukemia, Philadelphia Chromosome Negative | Acute Lymphoblastic Leukemia in RemissionUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedAcute Lymphoblastic Leukemia | Childhood B Acute Lymphoblastic LeukemiaUnited States, Canada, Australia, New Zealand, Switzerland