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Search clinical trials for: Glucocerebrosidase Deficiency Disease
Total 384098 results
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Genzyme, a Sanofi CompanyRecruitingGaucher Disease | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency DiseaseHungary, Croatia, United States, Australia, Belgium, Brazil, Bulgaria, Canada, Denmark, Germany, Greece, Hong Kong, India, Indonesia, Italy, Jordan, Korea, Republic of, Kuwait, Lebanon, Malaysia, Pakistan, Philippines, Poland, Saudi Arabia and more
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1 | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency Disease | Gaucher Disease, Non-Neuronopathic FormUnited States, Israel, Mexico, Russian Federation, Argentina, Italy
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1 | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency Disease | Gaucher Disease, Non-Neuronopathic FormUnited States, United Kingdom, Spain, Italy, Brazil, Canada, Poland
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Genzyme, a Sanofi CompanyCompletedCerebroside Lipidosis Syndrome | Glucosylceramide Beta-Glucosidase Deficiency Disease | Gaucher Disease Type I | Clucocerebrosidase Deficiency Disease | Gaucher Disease, Non-Neuronopathic FormUnited States
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University of ReadingKing's College London; University of LeedsNot yet recruitingAnemia, Iron Deficiency | Low Iron Stores | Cardiometabolic DiseaseUnited Kingdom
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KalVista Pharmaceuticals, Ltd.Not yet recruiting
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Inozyme PharmaNot yet recruitingPseudoxanthoma Elasticum | Arterial Calcification | Gene Mutations | Ectonucleotide Pyrophosphatase/phosphodiesterase1 Deficiency | Autosomal Recessive Hypophosphatemic Rickets Type 2
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University of PennsylvaniaRecruitingHIV/AIDSUnited States
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Elizabeth Austen LawsonNot yet recruitingOxytocin Deficiency | Arginine Vasopressin Deficiency
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Duke Street Bio LtdNot yet recruitingAdvanced Malignancies With Homologous Recombination Deficiency (HRD) (Breast, Ovarian, mCRPC, Brain Metastases)
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German University in CairoProf. Mohamed Hassan Solayman, Clinical pharmacy Department, German University... and other collaboratorsNot yet recruiting
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University of ParmaIRCCS Azienda Ospedaliero-Universitaria di Bologna; Federico II University; University... and other collaboratorsRecruiting
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Guiding Right, Inc.University of California, San DiegoRecruitingHIV/AIDS | Mental Health IssueUnited States
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South Tees Hospitals NHS Foundation TrustRecruitingAcute Myocardial InfarctionUnited Kingdom
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Juan Pablo Romero. MD, PhDFundación de Investigación Biomédica - Hospital Universitario de La PrincesaNot yet recruitingParkinson DiseaseSpain
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Claris Biotherapeutics, Inc.RecruitingLimbal Stem Cell DeficiencyUnited States
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Poznan University of Physical EducationNot yet recruitingMood Disorders | Endothelial Dysfunction | Malnutrition, CaloriePoland
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Children's Hospital Medical Center, CincinnatiNot yet recruitingVitamin D Deficiency | Vitamin A Deficiency | Graft Vs Host DiseaseUnited States
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Assiut UniversityNot yet recruiting
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London North West Healthcare NHS TrustRecruitingLynch Syndrome | Polyposis Syndrome, Hereditary Mixed, 1 | Polyposis Syndrome, Hereditary Mixed, 2United Kingdom
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University of MilanKolfarma s.r.l. - Italy; Fondazione TelethonRecruiting
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Assistance Publique - Hôpitaux de ParisNot yet recruitingInfectious Complications (Epidural Abscess or Meningitis) | Obstetrical Neuraxial AnaesthesiaFrance
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Xuanwu Hospital, BeijingNot yet recruitingCDKL5 Deficiency DisorderChina
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Assiut UniversityNot yet recruitingAnemia, Iron Deficiency
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Seoul St. Mary's HospitalNot yet recruiting
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Assiut UniversityNot yet recruitingVitamin B 12 Deficiency | End Stage Renal Disease on Dialysis
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University Hospital, MontpellierUniversité Montpellier; Centre National de la Recherche Scientifique, FranceNot yet recruiting
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Atlantic Health SystemRegeneron PharmaceuticalsNot yet recruitingFamilial Hypercholesterolemia | High Density Lipoprotein Deficiency | Lipoprotein Types--Lp System Lp(A) Hyperlipoproteinemia | Apolipoprotein B 100, Familial Defective | Low-Density-Lipoid-Type HyperlipoproteinemiaUnited States
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Hospital de Clinicas de Porto AlegreVifor PharmaNot yet recruitingHeart Failure, Systolic | Iron DeficienciesBrazil
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University of TennesseeNot yet recruitingNutritional Deficiency | Very Low Birth Weight Infant
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EMD Serono Research & Development Institute, Inc.Merck KGaA, Darmstadt, GermanyNot yet recruitingOvarian CancerUnited States, Germany
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Shanghai Vitalgen BioPharma Co., Ltd.Not yet recruitingAromatic L-amino Acid Decarboxylase Deficiency
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Mansoura UniversityRecruitingGastrointestinal DiseasesEgypt
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Hookipa Biotech GmbHNot yet recruitingHuman Immunodeficiency Virus (HIV) InfectionUnited States
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China-Japan Friendship HospitalRecruiting
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Cairo UniversityNot yet recruitingHeart Failure With Reduced Ejection Fraction
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University of North Carolina, Chapel HillNorth Carolina Translational and Clinical Sciences InstituteNot yet recruitingColorectal Cancer | Rectal Cancer | Rectal Neoplasms | Colon Cancer | Colon Adenocarcinoma | Colon Rectal Cancer | Hereditary Nonpolyposis Colon CancerUnited States
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University of UlsterNorthern Health & Social Care Trust (NHSCT); Solvotrin Therapeutics - Active...Not yet recruitingIron Deficiency Anemia of PregnancyUnited Kingdom
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Uppsala UniversityUniversity of Turku; Bielefeld University; Vivo international e.V.; The Swedish... and other collaboratorsNot yet recruitingMalnutrition | Psychological Distress | Mental Health | Malnutrition, Child | Dietary Deficiency
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Belgian Research on AIDS and HIV ConsortiumNot yet recruitingHuman Immunodeficiency Virus
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Hospital Universitario 12 de OctubreNot yet recruitingShock | Vasopressor Adverse Reaction | Vasopressin Causing Adverse Effects in Therapeutic Use | Vasopressin DeficiencySpain
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Rocket Pharmaceuticals Inc.Not yet recruitingPyruvate Kinase DeficiencySpain, United States
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King's College Hospital NHS TrustChiesi LimitedNot yet recruitingRespiratory Distress Syndrome | Surfactant Deficiency Syndrome Neonatal | Preterm Pregnancy
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ANRS, Emerging Infectious DiseasesNot yet recruiting
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Fundacja NutriciaInstitute of Mother and Child, Warsaw, PolandNot yet recruitingChild | Nutritional Status | Children | Dietary Habits | Consumption | Diet, Healthy | Diet Habit | Nutritional Deficiency | Cross-sectional Study | Dietary Assessment | Macronutrients
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IRCCS Ospedale San RaffaeleNot yet recruitingRare Diseases | Corneal Neovascularization | Limbal Stem Cell Deficiency | Aniridia | Neurotrophic Keratopathy | Ocular Cicatricial Pemphigoid | Ocular Graft-versus-host Disease | EEC Syndrome
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Raydiant Oximetry, Inc.Eunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingOxygen Deficiency | Fetal Complications | Fetal Hypoxia | Fetal Conditions | Fetal Distress | Labor (Obstetrics)--Complications | Labor Fetal AnoxiaUnited States
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Johns Hopkins UniversityNational Institutes of Health (NIH); Desmond Tutu HIV FoundationNot yet recruitingHuman Immunodeficiency Virus | Emergency Department | Pre-Exposure Prophylaxis | South Africa
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Wave Life Sciences Ltd.RecruitingAlpha-1 Antitrypsin DeficiencyCanada
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University of ZurichSwiss HIV Cohort StudyRecruiting