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Search clinical trials for: Hereditary Angioedema Type I
Total 493928 results
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TakedaCompletedAngioedemas, HereditaryArgentina
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Prof. Beck Popovic MajaTerminatedEye Cancer, RetinoblastomaSwitzerland
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Genzyme, a Sanofi CompanyActive, not recruitingThyroid CancerUnited States, Australia, Austria, Belgium, Brazil, Canada, Czechia, Denmark, France, Germany, Hungary, India, Italy, Korea, Republic of, Mexico, Netherlands, Poland, Portugal, Romania, Russian Federation, Serbia, Spain, Sweden, Switz...
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Children's Oncology GroupNational Cancer Institute (NCI)Active, not recruitingExtraocular RetinoblastomaUnited States, Canada, Australia, Brazil, Argentina, Egypt
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Imperial College LondonCompletedHereditary Hemorrhagic Telangiectasia | Pulmonary Arteriovenous MalformationsUnited Kingdom
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Virginia Commonwealth UniversityCompletedNeurofibromatosis 1 | Neurocognitive Deficit | Mental Health ImpairmentUnited States
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University of Alabama at BirminghamMemorial Sloan Kettering Cancer CenterActive, not recruitingNeurofibromatosis 2 | Progressive Vestibular Schwannoma (VS)United States
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Intellia TherapeuticsActive, not recruitingTransthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy | Wild-Type Transthyretin Cardiac AmyloidosisFrance, United Kingdom, New Zealand, Sweden
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Dermatology Specialties Limited PartnershipCompletedTuberous Sclerosis | Facial AngiofibromaUnited States, Taiwan, Serbia, Spain, Australia, Czechia, Hungary, New Zealand, Slovakia
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Peking Union Medical College Hospitalthe Second Affiliated Hospital of South China University; The Loudi Central...CompletedArtificial Intelligence | Enteroscope | Intestinal Polyposis, AdenomatousChina
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Memorial Sloan Kettering Cancer CenterEnrolling by invitationSurvivors of Unilateral RetinoblastomaUnited States
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Children's National Research InstituteBristol-Myers SquibbActive, not recruitingMelanoma | Hepatocellular Carcinoma | Osteosarcoma | Ewing Sarcoma | Neuroblastoma | Rhabdomyosarcoma | Wilms Tumor | Hepatoblastoma | Relapsed Pediatric Solid Tumor | Refractory Pediatric Solid TumorUnited States
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Spectrum Health HospitalsCompleted
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AeRang KimTerminatedOsteosarcoma | Ewing Sarcoma | Neuroblastoma | Solid Tumors | Pediatric Cancer | Rhabdomyosarcoma | Wilms Tumor | Soft Tissue Sarcomas | Germ Cell Tumors | Hepatic TumorUnited States
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Joergen SerupSahlgrenska University Hospital, SwedenActive, not recruitingCutaneous NeurofibromaDenmark, Sweden
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University of BirminghamActive, not recruitingWolfram SyndromeFrance, United Kingdom, Poland, Spain
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AstraZenecaWithdrawnNeurofibromatosis Type 1 | Plexiform Neurofibromas | Post-operativeChina
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AeRang KimActive, not recruitingOsteosarcoma | Ewing Sarcoma | Neuroblastoma | Rhabdomyosarcoma | Wilms Tumor | Desmoid Tumor | Germ Cell Tumor | Relapsed Pediatric Solid Tumors | Refractory Pediatric Solid Tumors | Hepatic TumorUnited States
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Assistance Publique - Hôpitaux de ParisNational Research Agency, FranceCompletedRheumatoid Arthritis | Uveitis | Vasculitis | Type 1 Diabetes | Crohn's Disease | Myositis | Healthy Volunteer | Ankylosing Spondylitis | FMF | Systemic Lupus Erythematosus/Antiphospholipid Syndrome | Cryopyrin-Associated Periodic Syndromes /TNF-receptor Associated Periodic Syndrome | Ulcerative Rectocolitis | Unclassified...France
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Geisinger ClinicNational Human Genome Research Institute (NHGRI)Active, not recruitingLynch Syndrome | Familial Hypercholesterolemia | Hereditary Breast and Ovarian Cancer SyndromeUnited States
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Aristotle University Of ThessalonikiTerminatedCarcinosarcoma | Melanoma (Skin) | Basal Cell Carcinoma | Squamous Cell Carcinoma | Seborrheic Keratosis | Dysplastic Nevus Syndrome | Lentigo Maligna | Lichen Planus-Like KeratosisGreece
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Amsterdam UMC, location VUmcUniversity Hospital, Essen; Institut Curie; Ligue contre le cancer, FranceCompletedRetinoblastoma | Secondary Primary Malignancies After RetinoblastomaNetherlands, France, Germany
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ShireTakeda Development Center Americas, Inc.No longer availableAngioedema | Hereditary Angioedema (HAE)United States, Canada, Germany, Hungary, Spain
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Janssen Research & Development, LLCCompletedAdenomatous Polyposis ColiUnited States, Germany, France, Israel, Netherlands, Poland, Puerto Rico, Spain, Sweden
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Abramson Cancer Center at Penn MedicineEnrolling by invitationOvarian Cancer | Genetic Predisposition to Disease | Breast Cancer Female | Hereditary Diseases | Gene Mutation-Related Cancer | Hereditary Breast and Ovarian Cancer | Hereditary Cancer SyndromeUnited States
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CSL BehringCompletedHereditary AngioedemaUnited States, Germany, Japan, Hungary, Canada, Netherlands, Israel
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BioCryst PharmaceuticalsCompletedHereditary Angioedema | HAEUnited States, Austria, Canada, Czechia, France, Germany, Hungary, North Macedonia, Romania, Spain, United Kingdom
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TakedaCompletedHereditary AngioedemaBelgium, Bulgaria, Estonia, Spain, Hungary, Israel, Germany, Czechia, Portugal, Greece, Lithuania, Poland, Latvia, Croatia, Slovakia, Austria, Canada, Ireland, North Macedonia, Romania, Serbia, Slovenia
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TakedaCompletedHereditary AngioedemaJapan
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Istituto Ortopedico RizzoliCompletedExostoses, Multiple HereditaryItaly
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BioCryst PharmaceuticalsCompletedHereditary Angioedema | Prophylaxis | HAEAustria, Denmark, France, Germany, Hungary, Israel, Italy, North Macedonia, Poland, Switzerland, United Kingdom, United States, Australia, Hong Kong, Korea, Republic of, New Zealand, Serbia, Slovakia, South Africa, Spain
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Eastern Cooperative Oncology GroupNational Cancer Institute (NCI)CompletedMelanoma (Skin)United States
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ShireTakeda Development Center Americas, Inc.CompletedAngioedemaUnited States, France, Netherlands, Spain, Hungary, Italy, Canada, Poland, Japan, Germany
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Oslo University HospitalEnrolling by invitation
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Janssen Research & Development, LLCCompletedAdenomatous Polyposis ColiUnited States, Germany, Korea, Republic of, France, Netherlands, Spain, Puerto Rico
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Albert Einstein College of MedicineEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationMucopolysaccharidosis II | Fabry Disease | Niemann-Pick Disease, Type C | Mucopolysaccharidosis VI | Lysosomal Acid Lipase Deficiency | Metachromatic Leukodystrophy | Gaucher Disease | Cerebrotendinous Xanthomatosis | Mucopolysaccharidosis IV A | GM1 Gangliosidosis | Mucopolysaccharidosis VII | Acid Sphingomyelinase... and other conditionsUnited States
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Sol-Gel Technologies, Ltd.TerminatedBasal Cell Nevus SyndromeUnited States, France, Belgium, Denmark, Germany, Italy, Netherlands, Spain, United Kingdom
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University of Alabama at BirminghamCompletedNeurofibromatosis | Plexiform Neurofibromas | NF1United States
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BioCryst PharmaceuticalsActive, not recruitingHereditary Angioedema | HAEFrance, North Macedonia, Poland, Korea, Republic of, Slovakia, South Africa, Czechia
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Jonsson Comprehensive Cancer CenterBeiGene; Driven To CureWithdrawnMetastatic Renal Cell Carcinoma | Stage IV Renal Cell Cancer AJCC v8 | Papillary Renal Cell Carcinoma | Collecting Duct Carcinoma | Unresectable Renal Cell Carcinoma | Hereditary Leiomyomatosis and Renal Cell Carcinoma | Clear Cell Papillary Renal Neoplasm | Hereditary Papillary Renal Cell Carcinoma and other conditionsUnited States
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Vanderbilt UniversityNational Institute of Neurological Disorders and Stroke (NINDS)CompletedNeurofibromatosis Type 1 | Reading DisabilitiesUnited States
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University Hospital, GrenobleCompletedHereditary AngioedemaFrance
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Duke UniversityNational Cancer Institute (NCI)CompletedBurkitt Lymphoma | Retinoblastoma | Diffuse Large B-cell LymphomaTanzania
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Murdoch Childrens Research InstituteCompletedHypertension | Blood Pressure | Neurofibromatosis 1Australia
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Talaris Therapeutics Inc.Duke UniversityTerminatedNiemann-Pick Disease | Alpha-mannosidosis | Tay Sachs Disease | Sandhoff Disease | Metachromatic Leukodystrophy (MLD) | Hurler-Scheie Syndrome | Hurler Syndrome (MPS I) | Hunter Syndrome (MPS II) | Sanfilippo Syndrome (MPS III) | Krabbe Disease (Globoid Leukodystrophy) | Adrenoleukodystrophy (ALD and AMN) | Pelizaeus...United States
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Mario Negri Institute for Pharmacological ResearchCompletedAlport SyndromeItaly
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Ionis Pharmaceuticals, Inc.CompletedHereditary AngioedemaUnited States, Netherlands
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Aucta Pharmaceuticals, IncTerminatedTuberous Sclerosis | Angiofibroma of FaceUnited States, China
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University Hospital, ToursCompletedTuberous Sclerosis Complex | LymphangioleiomyomatosisFrance