- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: Thalassemia intermedia
Total 1538 results
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PfizerActive, not recruitingSickle Cell DiseaseUnited States, Oman, United Kingdom, France, Egypt, Ghana, Italy, Kenya, Nigeria, Saudi Arabia
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Association for Innovation and Biomedical Research...European Vision Institute Clinical Research NetworkActive, not recruitingAtrophy | Age Related Macular Degeneration | Prediction | Intermediate AMDPortugal, France, Germany, Ireland, Italy, Netherlands, Spain, Switzerland, United Kingdom
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Chiesi Farmaceutici S.p.A.Active, not recruitingIdiopathic Pulmonary FibrosisNorth Macedonia, Ukraine, United Kingdom
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St. Jude Children's Research HospitalNational Cancer Institute (NCI); University of Florida; The Pew Charitable TrustsActive, not recruitingBrain and Central Nervous System TumorsUnited States, Australia
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Bangabandhu Sheikh Mujib Medical University, Dhaka...CompletedTransfusion-dependent ThalassemiaBangladesh
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Alumis IncActive, not recruitingUveitis, Intermediate | Noninfectious Panuveitis | Uveitis Posterior Non-InfectiousUnited States
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National Cancer Institute, EgyptCompletedPain, Postoperative | Cancer of LarynxEgypt
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Roswell Park Cancer InstituteActive, not recruitingAcute Myeloid Leukemia | Polycythemia Vera | Myelofibrosis | Chronic Myelomonocytic Leukemia | Waldenstrom Macroglobulinemia | Acute Lymphoblastic Leukemia | Chronic Lymphocytic Leukemia | Secondary Acute Myeloid Leukemia | Sickle Cell Disease | Myelodysplastic Syndrome | Plasma Cell Myeloma | Chronic Granulomatous... and other conditionsUnited States
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PfizerActive, not recruitingSickle Cell DiseaseUnited States, Lebanon, United Kingdom, Oman, Turkey, Canada, Egypt, Kenya, France, Italy, Netherlands
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NYU Langone HealthPerlmutter Cancer CenterCompletedMyelodysplastic SyndromesUnited States
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedB-cell Childhood Acute Lymphoblastic Leukemia | L1 Childhood Acute Lymphoblastic Leukemia | L2 Childhood Acute Lymphoblastic Leukemia | Intermediate Risk Recurrent Childhood Acute Lymphoblastic LeukemiaUnited States, Canada, Australia, Switzerland
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bluebird bioActive, not recruitingTransfusion-dependent Beta-ThalassemiaUnited States, France, United Kingdom, Australia, Thailand, Italy, Germany, Greece
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Bellicum PharmaceuticalsTerminatedHemoglobinopathies | Hemophagocytic Lymphohistiocytosis | Metabolic Disorders | Primary Immune Deficiency Disorders | Inherited Bone Marrow Failure SyndromeUnited States
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UNC Lineberger Comprehensive Cancer CenterWithdrawn
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingProstate Adenocarcinoma | Stage I Prostate Cancer AJCC v8 | Stage II Prostate Cancer AJCC v8 | Stage IIIA Prostate Cancer AJCC v8 | Stage IIC Prostate Cancer AJCC v8 | Stage IIA Prostate Cancer AJCC v8 | Stage IIB Prostate Cancer AJCC v8United States
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M.D. Anderson Cancer CenterActive, not recruiting
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Chiesi Canada CorpCompletedIron Overload | Beta Thalassemia Major AnemiaEgypt, Indonesia
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National Eye Institute (NEI)CompletedUveitis | Vasculitis | Ocular Inflammatory DiseaseUnited States
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Region SkaneCompletedSeptic Shock | Hypotension and Shock | Norepinephrine Adverse ReactionSweden
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National Institute of Blood and Marrow Transplant...Completed
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bluebird bioCompletedBeta-ThalassemiaUnited States, Germany, United Kingdom, France, Greece, Italy
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City of Hope Medical CenterCalifornia Institute for Regenerative Medicine (CIRM)Active, not recruitingSickle Cell Disease | Anemia, Sickle Cell | Hemoglobinopathies | Thalassemia | Sickle Cell DisorderUnited States
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Edwards LifesciencesCompletedSymptomatic Severe Aortic StenosisUnited States, Canada
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsEnrolling by invitationHematologic Diseases | Genetic Diseases, Inborn | Sickle Cell Disease | Hemoglobinopathies | Sickle Cell Anemia | Thalassemia | Beta-ThalassemiaUnited States, Canada, Italy, United Kingdom, Germany
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Sidney Kimmel Comprehensive Cancer Center at Johns...MacroGenicsActive, not recruitingProstate CancerUnited States
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Bioray LaboratoriesXiangya Hospital of Central South University; First Affiliated Hospital of... and other collaboratorsEnrolling by invitation
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University Hospital, Basel, SwitzerlandCompleted
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Memorial Sloan Kettering Cancer CenterCompletedProstate CancerUnited States
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FibroGenAstraZeneca; Astellas Pharma IncTerminatedPrimary MDS (Very Low, Low or Intermediate IPSS-R With <5% Blasts)United States, Australia, Belgium, Germany, Israel, Italy, Korea, Republic of, Russian Federation, Spain, United Kingdom, France, Turkey, Canada, Denmark, India, Poland
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MorphoSys AGActive, not recruitingDiffuse Large B-cell LymphomaGermany, France, Hungary, Italy, Spain, United States, Austria, Czechia, Australia, Israel, Korea, Republic of, Turkey, Taiwan, Argentina, Canada, Colombia, Ireland, Japan, Malaysia, New Zealand, Philippines, Poland, Romania, Russian... and more
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Memorial Sloan Kettering Cancer CenterFerring PharmaceuticalsActive, not recruitingProstate Cancer | Prostatic AdenocarcinomaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingSickle Cell Disease | Congenital Hemolytic AnemiaUnited States
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Longboard PharmaceuticalsAvailableDravet Syndrome | Lennox Gastaut Syndrome | Developmental and Epileptic EncephalopathiesUnited States
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...Active, not recruitingChronic Lymphocytic Leukemia | Non-Hodgkin LymphomaUnited States
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Bioray LaboratoriesFirst Affiliated Hospital of Guangxi Medical UniversitySuspendedThalassemia MajorChina
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CelgeneCompletedMyelodysplastic SyndromesUnited States, United Kingdom, Australia, Poland, Spain, Belgium, Italy, Germany, France, Canada
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Sun Yat-sen UniversityCompletedHepatocellular Carcinoma | Sorafenib | Transarterial ChemoembolizationChina
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Hospices Civils de LyonActive, not recruiting
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Children's Hospital of PhiladelphiaActive, not recruitingHemoglobinopathies | Immunodeficiencies | Non Malignant DiseasesUnited States
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Gesellschaft fur Medizinische Innovation - Hamatologie...ClinAssess GmbHCompleted
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CSSS de GatineauActive, not recruitingProstate CancerCanada
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City of Hope Medical CenterNational Cancer Institute (NCI)Active, not recruitingRecurrent Grade 1 Follicular Lymphoma | Recurrent Grade 2 Follicular Lymphoma | Recurrent Grade 3 Follicular Lymphoma | Recurrent Mantle Cell Lymphoma | Recurrent Non-Hodgkin LymphomaUnited States
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Fundación EPICActive, not recruitingCoronary Artery Disease | Left Main Coronary Artery Disease | Left Main Coronary Artery Stenosis | Restenosis, CoronarySpain
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Ashok MuthukrishnanProgenics Pharmaceuticals, Inc.TerminatedProstate CancerUnited States
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Terumo BCTbioUnited States Department of Defense; U.S. Army Medical Research and Development... and other collaboratorsTerminatedTransfusion Dependent ThalassemiaUnited States, Israel, Italy, Turkey
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Masonic Cancer Center, University of MinnesotaTerminatedSickle Cell Disease | Thalassemia | Cerebral Adrenoleukodystrophy | Inherited Metabolic Disorders | High Risk Hematologic DisordersUnited States
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Imperial College LondonCompleted
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Boston Children's HospitalNovartisCompletedSickle Cell Disease | Thalassemia Major | Transfusion-dependent HemachromatosisUnited States
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Azienda U.S.L. 1 di Massa e CarraraWithdrawn