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Search clinical trials for: genetic disorders
Total 155546 results
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Innovation Research & TrainingRecruiting
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Amany Keruakous, MD, MS.Not yet recruiting
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Bio Sidus SARecruiting
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University of LorraineLigue contre le cancer, FranceRecruitingQuality of Life | Cancer, Breast | Resilience, Psychological | Adverse Childhood Experiences | Attachment Styles | Epigenesis, GeneticFrance
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University of MinnesotaRecruitingGaucher DiseaseUnited States
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Institut de Myologie, FranceRoche Pharma AGNot yet recruitingMuscular Atrophy, Spinal, Type II | Muscular Atrophy, Spinal, Type IIIFrance
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UMC UtrechtRecruitingPseudoxanthoma ElasticumNetherlands
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingStudy of Genotype and Phenotype Characterization in Duchenne Muscular Dystrophy With Small MutationsMuscular Dystrophy, DuchenneItaly
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Alexandria UniversityRecruitingSubstance Use Disorders | Substance DependenceEgypt
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Hugo W. Moser Research Institute at Kennedy Krieger...RecruitingCornelia de Lange SyndromeUnited States
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Queen Mary University of LondonRecruitingGrowth Disorders | Short StatureUnited Kingdom
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National University of SingaporeUniversity Health Network, Toronto; National University Hospital, Singapore; Singapore... and other collaboratorsRecruitingCardiovascular DiseasesSingapore
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University of SouthamptonUniversity Hospital Southampton NHS Foundation Trust; National Institute for... and other collaboratorsRecruitingHuntington DiseaseUnited Kingdom
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingSteroid-refractory Diamond-Blackfan Anemia (DBA)United States
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Hellenic Atherosclerosis SocietyNot yet recruitingFamilial Hypercholesterolemia
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Vico Therapeutics B. V.RecruitingHuntington Disease | Spinocerebellar Ataxia Type 3 | Spinocerebellar Ataxia Type 1Israel, Germany, United Kingdom, Poland, Denmark, Netherlands, France
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Xiangya Hospital of Central South UniversityNot yet recruitingParkinson's DiseaseChina
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Neurophth Therapeutics IncRecruitingLeber Hereditary Optic Neuropathy (LHON)China, United States
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Minoryx Therapeutics, S.L.RecruitingCerebral Adrenoleukodystrophy (cALD)United States, Brazil, Argentina
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GRIN Therapeutics, Inc.RecruitingGRIN-related DisordersAustralia, United Kingdom, Spain, Netherlands, Germany, Italy, Canada
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Assiut UniversityNot yet recruiting
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Katarzyna HolcmanRecruitingTransthyretin AmyloidosisPoland
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Centre Hospitalier Universitaire de NiceRecruitingType 1 Facioscapulohumeral Muscular DystrophyFrance
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IRCCS Burlo GarofoloRecruitingAcute Lymphocytic LeukemiaItaly
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Assistance Publique - Hôpitaux de ParisRecruitingHuntington DiseaseFrance
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Masonic Cancer Center, University of MinnesotaRecruitingFollicular Lymphoma | Myelodysplastic Syndromes | Leukemia, Myeloid | Myelofibrosis | Burkitt Lymphoma | Marginal Zone Lymphoma | Acute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Chronic Myelogenous Leukemia | Prolymphocytic Leukemia | Plasma Cell Leukemia | Myeloproliferative Neoplasm | Small Lymphocytic... and other conditionsUnited States
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EarliTec Diagnostics, IncMarcus Autism CenterRecruitingAutism Spectrum Disorder | AutismUnited States
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Qianfoshan HospitalRecruitingIron Deficiency Anemia of Pregnancy | Iron Storage DiseaseChina
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Christoph KönigsRoche Pharma AG; Chugai Pharma Germany GmbHRecruitingSevere Hemophilia A | Severe Hemophilia A With Inhibitor | Severe Hemophilia A Without InhibitorGermany
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St. Mary's University, TwickenhamRecruiting
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City of Hope Medical CenterNational Cancer Institute (NCI)RecruitingRefractory B-Cell Non-Hodgkin Lymphoma | Recurrent B-Cell Non-Hodgkin Lymphoma | High Grade B-Cell Non-Hodgkin's Lymphoma | Intermediate Grade B-Cell Non-Hodgkin's LymphomaUnited States
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IRCCS San RaffaeleFondazione IRCCS Ca' Granda, Ospedale Maggiore PoliclinicoRecruiting
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National Cancer Institute (NCI)RecruitingLymphoma, B-Cell | Chronic Lymphocytic Leukemia | B-Cell Chronic Lymphocytic LeukemiaUnited States
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Johns Hopkins UniversityNational Institute on Aging (NIA)RecruitingAlzheimer Disease | Mild Cognitive ImpairmentUnited States
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Central Hospital, Nancy, FranceNot yet recruitingAlzheimer Disease | Homocystinemia
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Assistance Publique - Hôpitaux de ParisNot yet recruitingCerebral Small Vessel Diseases | CADASIL (Diagnosis)
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Assiut UniversityNot yet recruitingClinical Outcome in WILSON Disease
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Assiut UniversityNot yet recruiting
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Children's Hospital of Fudan UniversityRecruitingPrader-Willi SyndromeChina
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ApcinteX LtdCentessa Pharmaceuticals plcRecruitingHemophilia A | Hemophilia BUnited States, Italy, Spain, Taiwan, Australia, Belgium, United Kingdom, France, Germany, India, South Africa, Poland, Canada, Armenia, Turkey
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ApcinteX LtdCentessa Pharmaceuticals plcRecruitingHemophilia B | Hemophilia B With InhibitorUnited States, Spain, Australia, Taiwan, France, United Kingdom, Italy, Turkey, Armenia, India, Germany
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Regeneron PharmaceuticalsRecruitingCongenital Hearing Loss Secondary to Biallelic Mutations of the Otoferlin Gene (OTOF)Spain, United Kingdom, United States
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University of PennsylvaniaRecruiting
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Assiut UniversityRecruiting
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Centre Hospitalier Universitaire de Pointe-a-PitreDirection Générale de l'Offre de SoinsRecruitingDyslipidemia | Sickle Cell Disease | ComplicationFrance
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Western UniversityRecruitingFrontotemporal Dementia | Family MembersCanada
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Cardiff UniversityUniversity of CanterburyRecruitingCleft Lip and Palate | Parenting | Neurofibromatoses | Skin Condition | Alopecia | Craniofacial | Limb DifferenceUnited Kingdom
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University Hospital HeidelbergRecruitingCardiomyopathies | Skeletal Muscle DisorderGermany
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The Third Xiangya Hospital of Central South UniversityNot yet recruitingCharcot-Marie-Tooth Disease (CMT)
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Assiut UniversityNot yet recruitingThalassemia Major