- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: severe primary immune deficieny
Total 78791 results
-
Medical University of GrazActive, not recruitingPrimary Immunodeficiency | Immune Thrombocytopenia | Autoimmune Hemolytic Anemia | Evans SyndromeAustria
-
NovavaxDepartment of Health and Human ServicesCompletedCovid19 | SARS-CoV InfectionUnited States, Mexico, Puerto Rico
-
Paul SzabolcsEnrolling by invitationChronic Granulomatous Disease (CGD) | Wiskott-Aldrich Syndrome | Severe Chronic Neutropenia | Severe Combined Immunodeficiency (SCID) | Immunodeficiency With Predominant T-cell Defect, Unspecified | Hyper IgE Syndromes | Hyper IgM Deficiencies | Mendelian Susceptibility to Mycobacterial Disease | Common...United States
-
Pharmacyclics LLC.Janssen Research & Development, LLCActive, not recruitingChronic Graft Versus Host DiseaseUnited States, Spain, Korea, Republic of, Australia, Austria, Canada, France, Germany, Israel, Italy, Netherlands, Russian Federation, United Kingdom
-
Fondazione TelethonCompletedSevere Combined Immunodeficiency Due to ADA DeficiencyItaly
-
David WilliamsUniversity of California, Los Angeles; Boston Children's Hospital; Children's...CompletedSevere Combined ImmunodeficiencyUnited States
-
University of FloridaLive Like Bella Pediatric Cancer ResearchCompletedCommon Variable Immunodeficiency | Severe Combined Immunodeficiency | Sickle Cell Disease | Hurler Syndrome | Chronic Granulomatous Disease | Thalassemia | Wiskott-Aldrich Syndrome | Adrenoleukodystrophy | X-linked Lymphoproliferative Disease | Diamond Blackfan Anemia | Bone Marrow Failure Syndrome | Hemophagocytic... and other conditionsUnited States
-
Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...Active, not recruitingNon-Hodgkin's Lymphoma | Acute Lymphoblastic Leukemia | Chronic Myeloid Leukemia | Myelodysplastic SyndromeUnited States
-
University of California, Los AngelesGreat Ormond Street Hospital for Children NHS Foundation TrustEnrolling by invitationAdenosine Deaminase Deficiency | Severe Combined Immunodeficiency (SCID)United States, United Kingdom
-
Chiesi Farmaceutici S.p.A.CompletedSevere Combined Immunodeficiency | Adenosine Deaminase DeficiencyUnited States
-
Zimmer, GmbHActive, not recruitingOsteoarthritis | Rheumatoid Arthritis | Traumatic Arthritis | Polyarthritis | Severe Knee Pain | Severe Knee DisabilityFrance, Spain, United Kingdom, Austria, Germany, Netherlands
-
Great Ormond Street Hospital for Children NHS Foundation...Orchard TherapeuticsCompletedSevere Combined Immunodeficiency Due to ADA DeficiencyUnited Kingdom
-
University of Alabama at BirminghamCompletedLymphoma | Leukemia | Myelofibrosis | Myelodysplastic Syndrome | Severe Aplastic Anemia | Allogeneic TransplantUnited States
-
University of California, Los AngelesOrchard Therapeutics; California Institute for Regenerative Medicine (CIRM)CompletedSevere Combined Immunodeficiency Due to ADA DeficiencyUnited States
-
University of California, Los AngelesWithdrawnSevere Combined Immunodeficiency Due to ADA DeficiencyUnited States
-
Eli Lilly and CompanyCompletedRheumatoid ArthritisUnited States, Canada, Puerto Rico, China, Spain, Australia, Japan, India, Portugal, Germany, Turkey, Switzerland, Mexico, Poland, Belgium, France, Hungary, Korea, Republic of, Russian Federation, Taiwan, Israel, Austria, Italy, Argen... and more
-
Centre Leon BerardWithdrawnMyelodysplastic Syndromes | Severe Combined Immunodeficiency | Acute Leukemia | Haematological Malignancy | Hemoglobinopathy in Children | Bone Marrow AplasiaFrance
-
Children's Hospital of Fudan UniversityCompletedSevere Combined Immunodeficiency | Neonatal ScreeningChina
-
Assistance Publique - Hôpitaux de ParisCompletedX-linked Severe Combined ImmunodeficiencyFrance
-
Great Ormond Street Hospital for Children NHS Foundation...Orchard TherapeuticsCompletedAdenosine Deaminase Deficiency | Severe Combined Immunodeficiencies (SCID)United Kingdom
-
Association Pour l'Aide a la Recherche en Immunologie...CompletedSevere Combined ImmunodeficiencyFrance
-
Children's Oncology GroupNational Cancer Institute (NCI)CompletedAcute Lymphoblastic Leukemia | Childhood B Acute Lymphoblastic LeukemiaUnited States, Canada, Australia, New Zealand, Switzerland
-
Donald B. Kohn, M.D.National Institutes of Health (NIH); FDA Office of Orphan Products DevelopmentCompletedSevere Combined ImmunodeficiencyUnited States
-
AstraZenecaCompletedSevere AsthmaHungary, Germany, Bulgaria, Czechia, France, Greece, Italy, Netherlands, Poland, Romania, Slovenia, Spain
-
Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...TerminatedGenetic Disorder | Severe Aplastic Anemia | Immunodeficiency SyndromeUnited States
-
National Institute of Allergy and Infectious Diseases...National Center for Advancing Translational Sciences (NCATS); Primary Immune...Enrolling by invitationADA-SCID | Omenn Syndrome | SCID | Reticular Dysgenesis | XSCID | Leaky SCIDUnited States, Canada
-
National Institute of Allergy and Infectious Diseases...National Center for Advancing Translational Sciences (NCATS); Office of Rare... and other collaboratorsEnrolling by invitationOmenn Syndrome | Reticular Dysgenesis | Severe Combined Immunodeficiency (SCID) | XSCID | Leaky SCID | ADA SCIDUnited States, Canada
-
Case Comprehensive Cancer CenterCompletedLymphoma | Myelodysplastic Syndromes | Leukemia | Chronic Myeloproliferative Disorders | Multiple Myeloma and Plasma Cell Neoplasm | Myelodysplastic/Myeloproliferative DiseasesUnited States
-
Leadiant Biosciences, Inc.CompletedSevere Combined Immunodeficiency | ADA-SCID | Adenosine Deaminase DeficiencyUnited States
-
University Hospital, Strasbourg, FranceCompletedPrimary Immune-Deficiency (PID) Common Variable Immune Deficiency (CVID)France
-
Children's Hospital of Fudan UniversityThe First Affiliated Hospital of Zhengzhou University; Shanghai Children's... and other collaboratorsActive, not recruitingSevere Combined Immunodeficiency DiseaseChina
-
Emory UniversityCompletedSickle Cell Disease | Fanconi Anemia | Hurler Syndrome | Chronic Granulomatous Disease | Severe Congenital Neutropenia | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Glanzmann Thrombasthenia | Shwachman-Diamond Syndrome | Thalassemia Major | Leukocyte... and other conditionsUnited States
-
National Human Genome Research Institute (NHGRI)Withdrawn
-
National Human Genome Research Institute (NHGRI)CompletedSevere Combined Immunodeficiency SyndromeUnited States
-
National Institute of Allergy and Infectious Diseases...UnknownX-Linked Combined Immunodeficiency DiseasesUnited States
-
Roswell Park Cancer InstituteCompletedPrimary Myelofibrosis | Polycythemia Vera | Chronic Myelomonocytic Leukemia | Recurrent Adult Acute Myeloid Leukemia | Juvenile Myelomonocytic Leukemia | Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue | Nodal Marginal Zone B-cell Lymphoma | Recurrent Adult Burkitt Lymphoma and other conditionsUnited States
-
Shenzhen Geno-Immune Medical InstituteUnknownAdenosine DeAminase Severe Combined ImmunoDeficiency (ADA-SCID)China
-
Shenzhen Geno-Immune Medical InstituteUnknownSCID, X LinkedChina
-
Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...CompletedSevere Combined Immunodeficiency | Adenosine Deaminase Deficiency | Immune System Disorder | Autosomal Recessive Disorder | Purine-Nucleoside Phosphorylase Deficiency | Severe Combined Immunodeficiency With Absence of T and B Cells | X-Linked Severe Combined ImmunodeficiencyUnited States
-
University of Illinois at ChicagoCompletedAcute Myeloid Leukemia | Polycythemia Vera | Multiple Myeloma | Myelofibrosis | Acute Leukemia | Chronic Myelogenous Leukemia | Aplastic Anemia | Myeloproliferative Disorder | Hodgkin's Disease | Malignant Lymphoma | Lymphocytic LeukemiaUnited States
-
University of California, San FranciscoTerminatedSevere Combined ImmunodeficiencyUnited States
-
Nantes University HospitalCompletedSevere Combined Immunodeficiency, AtypicalFrance
-
Neena Kapoor, M.D.Terminated
-
University of MiamiJackson Health SystemNo longer available
-
Great Ormond Street Hospital for Children NHS Foundation...UnknownX-linked Severe Combined ImmunodeficiencyUnited Kingdom
-
Emory UniversityChildren's Healthcare of AtlantaTerminatedSickle Cell Disease | Fanconi Anemia | Thalassemia | Severe Congenital Neutropenia | Wiskott-Aldrich Syndrome | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Glanzmann Thrombasthenia | Leukocyte Adhesion Deficiency | Dyskeratosis-congenita | Chediak-Higashi Syndrome | Chronic-granulomatous Disease | Schwachman-Diamond...United States
-
National Human Genome Research Institute (NHGRI)CompletedSevere Combined ImmunodeficiencyUnited States
-
National Institute of Allergy and Infectious Diseases...CompletedSevere Combined ImmunodeficiencyUnited States
-
National Human Genome Research Institute (NHGRI)CompletedImmune System DiseasesUnited States