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Search clinical trials for: Paroxysmal Nocturnal Hemoglobinuria (PNH)
Total 1100 results
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Regeneron PharmaceuticalsAvailableParoxysmal Nocturnal Hemoglobinuria (PNH) | CD55-deficient Protein-losing Enteropathy (PLE) | CD59 Deficiency
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The Canadian College of Naturopathic MedicineOttawa Hospital Research Institute; Vitazan Professional; New Roots HerbalTerminated
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David Rizzieri, MDCompletedSickle Cell Anemia | Pure Red Cell Aplasia | Paroxysmal Nocturnal Hemoglobinuria (PNH) | Severe Aplastic AnemiaUnited States
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Amyndas Pharmaceuticals S.A.CompletedComplement Mediated DiseasesUnited States
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St. Jude Children's Research HospitalCompletedMyelodysplastic Syndrome (MDS) | Leukemia, Acute Lymphocytic (ALL) | Leukemia, Myeloid, Acute(AML) | Leukemia, Myeloid, Chronic(CML) | Hemoglobinuria, Paroxysmal Nocturnal (PNH) | Lymphoma, Non-Hodgkin (NHL) | Juvenile Myelomonocytic Leukemia(JMML)United States
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St. Jude Children's Research HospitalCompletedHodgkin Lymphoma | Myelodysplastic Syndrome (MDS) | Leukemia, Acute Lymphocytic (ALL) | Juvenile Myelomonocytic Leukemia (JMML) | Leukemia, Myeloid, Acute(AML) | Leukemia, Myeloid, Chronic(CML) | Hemoglobinuria, Paroxysmal Nocturnal (PNH) | Lymphoma, Non-Hodgkin (NHL)United States
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St. Jude Children's Research HospitalCompletedLymphoma, Non-Hodgkin | Hodgkin Disease | Chronic Myeloid Leukemia | Acute Myeloid Leukemia (AML) | Acute Lymphoblastic Leukemia (ALL) | Paroxysmal Nocturnal Hemoglobinuria (PNH) | Myelodysplastic Syndrome (MDS) | Secondary AML | Juvenile Myelomonocytic Leukemia (JMML) | Secondary MDSUnited States
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Novartis PharmaceuticalsNot yet recruitingAtypical Hemolytic Uremic Syndrome
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Cedars-Sinai Medical CenterAlexion Pharmaceuticals, Inc.TerminatedPregnancy Related | Preeclampsia | HELLP Syndrome | Severe Preeclampsia | HELLP | Complement Regulatory Factor Defect | PNH | Eculizumab | HELLP Syndrome Second Trimester | AHUS | Complement Abnormality | HELLP Syndrome Third TrimesterUnited States
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Masonic Cancer Center, University of MinnesotaNot yet recruitingAcquired Pure Red Cell Aplasia | Paroxysmal Nocturnal Hemoglobinuria | Severe Aplastic Anemia | Acquired Amegakaryocytic Thrombocytopenia
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Chengdu Suncadia Medicine Co., Ltd.RecruitingParoxysmal Nocturnal HemoglobinuriaChina
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BioCryst PharmaceuticalsRecruitingParoxysmal Nocturnal HemoglobinuriaSouth Africa, Malaysia
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Kira Pharmacenticals (US), LLC.Not yet recruitingParoxysmal Nocturnal HemoglobinuriaChina
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Alexion Pharmaceuticals, Inc.RecruitingParoxysmal Nocturnal HemoglobinuriaItaly
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsRecruitingCongenital Amegakaryocytic Thrombocytopenia | Paroxysmal Nocturnal Hemoglobinuria | Shwachman-Diamond Syndrome | Bone Marrow Failure Syndrome | Congenital Pure Red Cell Aplasia | Hereditary Sideroblastic Anemia | Hematologic Neoplasm With Germline GATA2 Mutation | Hematologic Neoplasm With Germline... and other conditionsUnited States
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Children's Hospital of PhiladelphiaRecruitingParoxysmal Nocturnal Hemoglobinuria | Acquired Aplastic Anemia | Inherited Bone Marrow Failure SyndromesUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingSickle Cell Disease | Severe Congenital Neutropenia | Paroxysmal Nocturnal Hemoglobinuria | Glanzmann Thrombasthenia | Shwachman-Diamond Syndrome | Diamond Blackfan Anemia | Transfusion Dependent Alpha- or Beta- Thalassemia | Non-Malignant Hematologic DisordersUnited States
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Hoffmann-La RocheChugai PharmaceuticalActive, not recruitingParoxysmal Hemoglobinuria, NocturnalFrance, Korea, Republic of, Italy, Japan, Germany, Hungary, Netherlands
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City of Hope Medical CenterNational Cancer Institute (NCI)Active, not recruitingLymphoma | Myelodysplastic Syndromes | Leukemia | Chronic Myeloproliferative Disorders | Multiple Myeloma and Plasma Cell Neoplasm | Myelodysplastic/Myeloproliferative Diseases | Graft Versus Host Disease | Precancerous/Nonmalignant Condition
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Roswell Park Cancer InstituteActive, not recruitingAcute Myeloid Leukemia | Polycythemia Vera | Myelofibrosis | Chronic Myelomonocytic Leukemia | Waldenstrom Macroglobulinemia | Acute Lymphoblastic Leukemia | Chronic Lymphocytic Leukemia | Secondary Acute Myeloid Leukemia | Sickle Cell Disease | Myelodysplastic Syndrome | Plasma Cell Myeloma | Chronic Granulomatous... and other conditionsUnited States
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Samsung Bioepis Co., Ltd.CompletedParoxysmal Nocturnal HemoglobinuriaKorea, Republic of, Taiwan, Malaysia, Thailand, Romania, India, Mexico, Ukraine
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SanofiCompletedParoxysmal Nocturnal HemoglobinuriaUnited States
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Lawson Health Research InstituteAlexion Pharmaceuticals, Inc.Active, not recruitingTransient Ischemic Attack | Paroxysmal Nocturnal Hemoglobinuria | Cerebral Vein Thrombosis | Embolic Stroke of Undetermined SourceCanada
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BioCryst PharmaceuticalsActive, not recruitingParoxysmal Nocturnal HemoglobinuriaUnited Kingdom, Hungary, France, Spain, Malaysia, South Africa, Korea, Republic of
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Chengdu Suncadia Medicine Co., Ltd.Active, not recruitingParoxysmal Nocturnal HemoglobinuriaChina
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Wuhan Createrna Science and Technology Co., LtdCompletedParoxysmal Nocturnal HemoglobinuriaChina
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Wuhan Createrna Science and Technology Co., LtdCompleted
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Assistance Publique - Hôpitaux de ParisLeeds Cancer Centre at St. James's University HospitalCompleted
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Wuhan Createrna Science and Technology Co., LtdCompletedParoxysmal Nocturnal HemoglobinuriaChina
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Kira Pharmacenticals (US), LLC.CompletedParoxysmal Nocturnal HemoglobinuriaAustralia
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Scripps HealthCompletedMelanoma | Sarcoma | Renal Cell Carcinoma | Breast Cancer | Multiple Myeloma | Hodgkin's Lymphoma | Non-Hodgkin's Lymphoma | Ovarian Cancer | Thymoma | Waldenstrom Macroglobulinemia | Mantle Cell Lymphoma | Chronic Lymphocytic Leukemia | Myelodysplastic Syndrome | Acute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Chronic Myelogenous Leukemia and other conditionsUnited States
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Scripps HealthCompletedMyelodysplastic Syndromes | Multiple Myeloma | Hodgkin's Lymphoma | Non-Hodgkin's Lymphoma | Acute Lymphoblastic Leukemia | Chronic Lymphocytic Leukemia | Acute Myelogenous Leukemia | Chronic Myelogenous Leukemia | Small Lymphocytic Lymphoma | Paroxysmal Nocturnal Hemoglobinuria | Severe Aplastic Anemia | Myeloproliferative... and other conditionsUnited States
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Radboud University Medical CenterCompletedParoxysmal Nocturnal Hemoglobinuria | Eculizumab | PK-PDNetherlands
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CARE Pharma Shanghai Ltd.CompletedParoxysmal Nocturnal Hemoglobinuria, Natural History StudyChina
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AKARI TherapeuticsTerminatedParoxysmal Nocturnal HemoglobinuriaPoland
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BiocadCompletedParoxysmal Nocturnal HemoglobinuriaRussian Federation
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...CompletedPrimary Myelofibrosis | Polycythemia Vera | Essential Thrombocythemia | Chronic Myelomonocytic Leukemia | Myeloproliferative Neoplasm | Paroxysmal Nocturnal Hemoglobinuria | de Novo Myelodysplastic Syndrome | Atypical Chronic Myeloid Leukemia, BCR-ABL1 Negative | Refractory Anemia | Refractory Anemia With... and other conditionsUnited States
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Roswell Park Cancer InstituteNational Cancer Institute (NCI)CompletedPrimary Myelofibrosis | Chronic Myelomonocytic Leukemia | Recurrent Adult Acute Myeloid Leukemia | Juvenile Myelomonocytic Leukemia | Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue | Nodal Marginal Zone B-cell Lymphoma | Recurrent Adult Burkitt Lymphoma | Recurrent... and other conditionsUnited States
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Roswell Park Cancer InstituteCompletedPrimary Myelofibrosis | Polycythemia Vera | Chronic Myelomonocytic Leukemia | Recurrent Adult Acute Myeloid Leukemia | Juvenile Myelomonocytic Leukemia | Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue | Nodal Marginal Zone B-cell Lymphoma | Recurrent Adult Burkitt Lymphoma and other conditionsUnited States
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King's College Hospital NHS TrustCompletedParoxysmal Nocturnal HaemoglobinuriaUnited Kingdom
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Sidney Kimmel Comprehensive Cancer Center at Johns...CompletedAplastic Anemia | Paroxysmal Hemoglobinuria, NocturnalUnited States
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Indiana University School of MedicineCompletedMultiple Myeloma | Non-Hodgkin's Lymphoma | Myelofibrosis | Chronic Lymphocytic Leukemia | Anemia, Aplastic | Acute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Chronic Myelogenous Leukemia | Myelodysplasia | Hemoglobinuria, Paroxysmal | Hodgkin's DiseaseUnited States
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Asan Medical CenterCompletedMyelodysplastic Syndromes | Leukemia | Nonmalignant Neoplasm | Paroxysmal Nocturnal HemoglobinuriaKorea, Republic of
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Oregon Health and Science UniversityCompletedMicrovascular and Cardiac Dysfunction in Paroxysmal Nocturnal Hemoglobinuria and Sickle Cell DiseaseSickle Cell Disease | Paroxysmal Nocturnal Hemoglobinuria | Rheologic DiseaseUnited States
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AlexionApproved for marketingHemoglobinuria, ParoxysmalUnited States
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Jonsson Comprehensive Cancer CenterCompleted
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National Cancer Institute (NCI)CompletedThrombocytopenia | Chronic Myelomonocytic Leukemia | Recurrent Adult Acute Myeloid Leukemia | Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities | Adult Acute Myeloid Leukemia With Del(5q) | Adult Acute Myeloid Leukemia With Inv(16)(p13;q22) | Adult Acute Myeloid Leukemia With t(16;16)(p13... and other conditionsUnited States
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkUnknownMyelodysplastic Syndromes | Purpura, Thrombocytopenic | Anemia, Aplastic | Red-Cell Aplasia, Pure | Bone Marrow Failure Syndromes | Hemoglobinuria, Paroxysmal | Leukemia, LymphocyticUnited States
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St. Jude Children's Research HospitalCompletedAcute Myeloid Leukemia | Leukemia | Hodgkin's Lymphoma | Juvenile Myelomonocytic Leukemia | Acute Lymphoblastic Leukemia | Non-Hodgkin Lymphoma | Chronic Myeloid Leukemia | Myelodysplastic Syndrome | Paroxysmal Nocturnal HemoglobinuriaUnited States
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Shandong Qilu Stem Cells Engineering Co., Ltd.Second Affiliated Hospital of Zhengzhou University; The Second Affiliated Hospital... and other collaboratorsRecruitingBone Marrow Failure DisordersChina