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Search clinical trials for: Infantile Spinal Muscular Atrophy
Total 30572 results
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University Hospital, Basel, SwitzerlandEnrolling by invitationSpinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type IIISwitzerland
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Biohaven Pharmaceuticals, Inc.Active, not recruitingNeuromuscular Diseases | Spinal Muscular Atrophy | SMAUnited States, Netherlands, United Kingdom, Spain, Czechia, Belgium, Germany, Italy, Poland
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Centre Hospitalier Régional de la CitadelleCompletedSafety and Efficacy Study of Pyridostigmine on Patients With Spinal Muscular Atrophy Type 3 (EMOTAS)Spinal Muscular Atrophy Type 3Belgium
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Cystinose StiftungLabor Becker & Kollegen, Munich, Germany; Screening Labor Hannover; Genetikum... and other collaboratorsCompletedSpinal Muscular Atrophy | Cystinosis | Cystinosis, NephropathicGermany
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Assistance Publique - Hôpitaux de ParisCompletedDuchenne Muscular Dystrophy | Spinal Muscular AtrophyFrance
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Eisai Co., Ltd.CompletedAmyotrophic Lateral Sclerosis (ALS)Japan
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Eisai Co., Ltd.CompletedAmyotrophic Lateral Sclerosis (ALS)Japan
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University of UtahAbbott; Leadiant Biosciences, Inc.; Families of Spinal Muscular AtrophyCompletedSpinal Muscular AtrophyUnited States
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Novartis PharmaceuticalsCompletedSpinal Muscular AtrophyBelgium, Germany, Italy, Russian Federation, Poland, Bulgaria, Denmark
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Novartis Gene TherapiesTerminatedSpinal Muscular AtrophyUnited States
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Ohio State UniversityCompletedSpinal Cord Injuries | Metabolic Disease | Skeletal Muscle AtrophyUnited States
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Columbia UniversityThe Spinal Muscular Atrophy FoundationCompleted
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Synchron Medical, Inc.WithdrawnParalysis | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Neurologic Disorder | Spinal Muscular Atrophy | Spinal Cord Injury | Stroke, Lacunar | Upper Limb Injury | Paralysis; Stroke | Stroke, BrainstemAustralia
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Northwell HealthCompletedAdult Spinal Muscular AtrophyUnited States
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Hoffmann-La RocheCompletedMuscular Atrophy, SpinalUnited States
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Fondazione Policlinico Universitario Agostino Gemelli...CompletedUltrasonography | Spinal Muscular Atrophy | Anesthesia, Spinal | Spinal Puncture ComplicationsItaly
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The Children's Hospital of Zhejiang University...Withdrawn
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Nationwide Children's HospitalNovartisActive, not recruitingSpinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type IUnited States
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Duke UniversityCenters for Disease Control and Prevention; National ALS Registry; Agency for...CompletedMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Progressive Muscular AtrophyUnited States
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Asan Medical CenterActive, not recruitingSarcopenia | Lumbar Spinal Stenosis | Neurogenic ClaudicationKorea, Republic of
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Universidad Autonoma de MadridKing's College London; Centro Superior de Estudios Universitarios LasalleCompletedMuscle Atrophy | Intervertebral Disc Compression | Spine InjurySpain, United Kingdom
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UMC UtrechtPrincess Beatrix Muscle FoundationActive, not recruitingSpinal Muscular AtrophyNetherlands
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Novartis Gene TherapiesPRA Health SciencesCompletedSpinal Muscular Atrophy Type IKorea, Republic of, Taiwan, Japan
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University Medical Centre LjubljanaCompleted
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Istanbul Medipol University HospitalEnrolling by invitationSpinal Muscular Atrophy | Muscle Tone PoorTurkey
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Washington University School of MedicineActive, not recruitingSpinal Muscular Atrophy | Spinal Muscular Atrophy Type 3 | Spinal Muscular Atrophy Type IIUnited States, Canada
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Istanbul Medipol University HospitalEnrolling by invitationQuality of Life | Neuromuscular Diseases | Spinal Muscular Atrophy | Pediatric DisorderTurkey
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Novartis Gene TherapiesCompletedSpinal Muscular Atrophy 1United States
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Novartis Gene TherapiesPRA Health SciencesCompletedSpinal Muscular AtrophyUnited States, United Kingdom, Australia, Belgium, Canada, Japan
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LMU KlinikumCompletedHealthy | Myotonic Dystrophy Type 2 | Pompe Disease (Late-onset) | Spinal Muscular Atrophy Type 3 | Myotonic Dystrophy Type 1 (DM1) | Facioscapulohumeral Muscular Dystrophy 1 | Inclusion Body Myositis, SporadicGermany
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Columbia UniversityBiogen; ALS AssociationCompleted
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National Institute of Neurological Disorders and...CompletedMotor Neuron Disease | Spinal and Bulbar Muscular Atrophy (SBMA)United States
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Novartis Gene TherapiesCompletedGene Therapy | SMA - Spinal Muscular AtrophyUnited States
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Novartis Gene TherapiesCompletedSMAFrance, United Kingdom, Italy, Belgium
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MarsiBionicsFundacion para la Investigacion Biomedica del Hospital Universitario Ramon...CompletedSpinal Muscular Atrophy Type IISpain
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Hasselt UniversityJessa Hospital; Sint-Trudo Hospital; Sint-Franciscus ZiekenhuisSuspendedExtreme Lateral Interbody FusionFUSION (XLIF) Versus Posterior Lumbar Interbody Fusion (PLIF) (XLIF)Atrophy | Muscle Damage | Degenerative Diseases, Spinal CordBelgium
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CENTOGENE GmbH RostockCompletedScoliosis | Muscular Atrophy | Duchenne Muscular Dystrophy | Lordosis | Muscular Weakness | Increased Lordosis/Scoliosis | Hyporeflexia | Red-Green Color BlindnessEgypt, India, Albania, Pakistan, Georgia, Lebanon, Romania, Sri Lanka
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Ankara City Hospital BilkentCompletedAnesthesia | Child, Only | Muscular Atrophy, SpinalTurkey
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Columbia UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedSpinal Muscular Atrophy Type 3 | Mitochondrial MyopathyUnited States
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Great Ormond Street Hospital for Children NHS Foundation...CompletedSpinal Muscular AtrophyUnited Kingdom
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Ohio State UniversityBiogen; Cure SMACompleted
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NYU Langone HealthWinthrop University HospitalWithdrawnSpinal Muscular AtrophyUnited States
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University Hospital, Basel, SwitzerlandCompletedLumbar Spinal Stenosis (LSS)Switzerland
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Catalyst Pharmaceuticals, Inc.CompletedMuscular Atrophy, SpinalItaly
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Hospital Israelita Albert EinsteinMinistry of Health, BrazilCompletedSpinal Muscular AtrophyBrazil
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BiogenCompleted
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Centre Hospitalier Régional de la CitadelleRoche Pharma AG; Biogen; AveXis, Inc.; Association Belge contre les Maladies neuro...CompletedSpinal Muscular AtrophyBelgium
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Hoffmann-La RocheCompleted
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Gillette Children's Specialty HealthcareCompletedCerebral Palsy | Muscular Dystrophy | Osteopenia | Rett Syndrome | Spinal Muscular Atrophy | Spina BifidaUnited States
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BiogenCompletedSpinal Muscular AtrophyUnited States