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Search clinical trials for: Genetic Diseases, Inborn
Total 18709 results
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Medical University of ViennaUniversity of Vienna; Griffith UniversityRecruiting
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Centre Hospitalier Sud FrancilienNot yet recruiting
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Craig EricksonHealx LimitedRecruitingFragile X SyndromeUnited States
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Taumedika s.r.l.Nextrasearch S.r.l.s.Not yet recruitingScar | Laxity; Skin | Wrinkle
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Sofwave Medical LTDRecruiting
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Lundquist Institute for Biomedical Innovation at...Not yet recruitingMucopolysaccharidosis III | Sanfilippo SyndromeUnited States
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Maastricht University Medical CenterRecruitingQuality of Life | Tuberous Sclerosis | Basal Cell Nevus Syndrome | Cutis Laxa | Epidermolysis Bullosa | Ichthyosis | Ectodermal Dysplasia | Albinism | Birt-Hogg-Dube Syndrome | Palmoplantar KeratosesNetherlands
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Hospital do CoracaoUniversity of Sao Paulo; Instituto Dante Pazzanese de Cardiologia; National Institute...Not yet recruiting
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Masaryk Memorial Cancer InstituteMasaryk UniversityRecruitingPancreatic Ductal Adenocarcinoma | Pancreatitis, Chronic | Hereditary DiseasesCzechia
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University Hospital, Strasbourg, FranceNot yet recruiting
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingNoonan Syndrome | Costello Syndrome | RASopathy | Cardio-Facio-Cutaneous SyndromeItaly
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Tampere UniversityProfessor Lauri Lehtimäki; Professor Mika Mäkelä; Professor Sanna Toppila-Salmi; Professor Ilkka JunttilaNot yet recruitingAsthma | Allergy | Rhinitis, Allergic | Asthma in Children | Atopic Dermatitis | Allergen ImmunotherapyFinland
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ENCellRecruitingCharcot-Marie-Tooth Disease Type 1AKorea, Republic of
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Chiesi Farmaceutici S.p.A.ICON plcNot yet recruiting
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Pole Sante Grace de DieuRecruiting
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ENCellNot yet recruitingDuchenne Muscular DystrophyKorea, Republic of
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University Health Network, TorontoNot yet recruitingIrritable Bowel Syndrome | Gastrointestinal Dysfunction | Ehlers-Danlos Syndrome | Hypermobility SyndromeCanada
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Ohio State UniversityRecruiting
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Caroline Michaela KistorpSanofiNot yet recruitingChronic Kidney Diseases | Fabry DiseaseDenmark
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National Institute of Allergy and Infectious Diseases...RecruitingChronic Granulomatous Disease (CGD) | X-Linked Chronic Granulomatous DiseaseUnited States
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Sunshine Guojian Pharmaceutical (Shanghai) Co.,...Not yet recruiting
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University of AarhusAarhus University HospitalRecruitingCardiovascular Diseases | Inflammation | Lymphedema | Turner SyndromeDenmark
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The University of QueenslandNot yet recruitingAtaxia TelangiectasiaAustralia
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University Hospital TuebingenRecruitingRetinitis PigmentosaGermany
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Universidad Politecnica de MadridHospital Infantil Universitario Niño Jesús, Madrid, Spain; Hospital Universitario... and other collaboratorsRecruiting
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Blueskin ASRecruitingPsoriasis | Atopic Dermatitis | Vitiligo | Alopecia AreataDenmark
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University of RochesterNot yet recruitingAge-Related Macular Degeneration | Retinitis Pigmentosa | Retinal Dystrophies | Alcohol Use Disorder | Stargardt DiseaseUnited States
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Kathelijn FischerRadboud University Medical Center; University Medical Center Groningen; Maastricht... and other collaboratorsRecruitingAdolescent | Child | Hemophilia A With Inhibitor | Adult | Hemophilia A Without Inhibitor | Hemophilia A, SevereNetherlands
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New York UniversityNot yet recruiting
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Oman Medical Speciality BoardArmed Forces Hospital, OmanNot yet recruitingSickle-Cell Disease With Crisis
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National Taiwan University HospitalRecruiting
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Qilu Hospital of Shandong UniversityRecruitingChild | Williams Syndrome | Neurodevelopmental DelayChina
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Bioray LaboratoriesXiangya Hospital of Central South University; The 923rd Hospital of Joint Logistics...Recruiting
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Noema Pharma AGNot yet recruiting
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Societa Italiana di Dermatologia Medica, Chirurgica...Recruiting
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Daniel J. WeinerRecruitingCystic FibrosisUnited States
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LEO PharmaRecruiting
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Suzhou Alphamab Co., Ltd.RecruitingHemophilia A With Inhibitor | Hemophilia B With InhibitorChina
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National Heart, Lung, and Blood Institute (NHLBI)Children's National Research InstituteRecruitingSickle Cell Disease | Thalassemia | HemoglobinopathyUnited States
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University of California, Los AngelesRecruitingTuberous SclerosisUnited States
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University of ValenciaAsociación de Fibrosis Quística - Comunidad ValencianaNot yet recruiting
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University Hospital, ToulouseNot yet recruitingFamilial Adenomatous PolyposisFrance
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Lantu BiopharmaNot yet recruitingBeta-Thalassemia
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argenxRecruitingThyroid Eye DiseaseUnited States
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BioMarin PharmaceuticalRecruitingIdiopathic Short StatureUnited States
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Hangzhou Yirui Pharmaceutical Technology Co., LtdNot yet recruitingAtopic DermatitisUnited States
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argenxRecruitingThyroid Eye DiseaseUnited States
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Forge Biologics, IncNot yet recruitingKrabbe DiseaseUnited States
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BioMarin PharmaceuticalRecruitingPhenylketonuria (PKU)United States