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Clinical Trials Sponsored by Orphan Medical
Total 56065 results
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Daiichi Sankyo Co., Ltd.Orphan Disease Treatment Institute Co., Ltd.Completed
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FDA Office of Orphan Products DevelopmentNational Institute of Mental Health (NIMH)Completed
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Organ Recovery Systems, Inc.Recruiting
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University of ArizonaHorphag ResearchTerminatedDiastolic Dysfunction | Cardiac FibrosisUnited States
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MetroHealth Medical CenterVA Office of Research and Development; Case Western Reserve University; FDA Office...Active, not recruitingSpinal Cord Injury | TetraplegiaUnited States
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Weill Medical College of Cornell UniversityFDA Office of Orphan Products Development; The Leukemia and Lymphoma Society; Karyopharm Therapeutics IncCompletedDiffuse Large B-Cell LymphomaUnited States
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Icahn School of Medicine at Mount SinaiCompleted
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Thibaut GuiraudRecruitingChronic Low-back PainFrance
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Rohan DharmakumarCompleted
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ORHUN EKRENCompletedDental Implant | Short Dental Implant
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Meliha OrhonCompleted
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University Medical Center GroningenMaastricht University Medical Center; Center of Expertise for Chronic Organ...Completed
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Charles Drew University of Medicine and ScienceCompletedHIV Infections | CachexiaUnited States
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Icahn School of Medicine at Mount SinaiCompleted
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Icahn School of Medicine at Mount SinaiCompleted
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Icahn School of Medicine at Mount SinaiCompletedCommon Variable Immunodeficiency
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Organ Recovery Systems, Inc.Completed
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Organ Transplant Institute, ChinaUnknown
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Skane University HospitalIndiana Hemophilia &Thrombosis Center, Inc.; Bioverativ Therapeutics Inc.; Swedish...Active, not recruitingFactor IX DeficiencyUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI); FDA Office of Orphan Products DevelopmentCompletedLeukemia | Chronic Lymphocytic LeukemiaUnited States
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RedHill Biopharma LimitedMedical University of South Carolina; National Cancer Institute (NCI); FDA Office... and other collaboratorsCompletedPancreatic Cancer | Unspecified Adult Solid Tumor, Protocol SpecificUnited States
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Kevin KilgoreNational Institute of Neurological Disorders and Stroke (NINDS); Case Western... and other collaboratorsRecruitingSpinal Cord Injuries | Spinal Cord Injury at C5-C7 Level | Spinal Cord Injury Cervical | Spinal Cord Injury at C5-C7 Level With Complete Lesion | Spinal Cord Injury at C5-C7 Level With Incomplete LesionUnited States
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Stony Brook UniversityFDA Office of Orphan Products Development; State University of New YorkCompletedSepsis | Respiratory Distress Syndrome | Respiratory Distress Syndrome, AdultUnited States
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Orphan...CompletedHyperoxaluriaUnited States
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Aliaa Rehan YoussefCompletedMechanical Low Back PainEgypt
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Aliaa Rehan YoussefCompletedNeck Pain | Cervical PainEgypt
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Steven Hays, MDOrphAI TherapeuticsRecruitingLung Transplantation | Chronic Lung Allograft Dysfunction | Bronchiolitis Obliterans SyndromeUnited States
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University of FloridaFood and Drug Administration (FDA); FDA Office of Orphan Products DevelopmentCompletedMitochondrial DiseasesUnited States, Canada
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Aliaa Rehan YoussefCompletedBone Deformity | Limb Length DiscrepancyEgypt
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University Hospital, ToursSwedish Orphan Biovitrum; INSERM CIC-P 1415, University Hospital Center of...TerminatedCOVID-19 Infection | ANAKINRA Treatment | Optimized Standard of Care (oSOC)France
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Aliaa Rehan YoussefCompleted
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Aliaa Rehan YoussefCompleted
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Januario Castro, M.D.FDA Office of Orphan Products Development; Memgen, LLCTerminatedChronic Lymphocytic Leukemia | Small Lymphocytic LymphomaUnited States
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Jena University HospitalNovartis; Amgen; Grifols Biologicals, LLC; argenx; Swedish Orphan Biovitrum; University...Recruiting
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FDA Office of Orphan Products DevelopmentHugo W. Moser Research Institute at Kennedy Krieger, Inc.Completed
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Weill Medical College of Cornell UniversityChildren's Hospital Colorado; SLC6A1 Connect; STXBP1 Foundation; Clara Inspired; University... and other collaboratorsEnrolling by invitationDevelopmental and Epileptic Encephalopathy | STXBP1 Encephalopathy With Epilepsy, SLC6A1 Neurodevelopmental DisorderUnited States
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Maastricht University Medical CenterAstraZeneca; Center for Integrated Rehabilitation and Organ Failure HornUnknownChronic Obstructive Airway DiseaseNetherlands
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Boston CollegeChristian Alliance for Orphans; Helping Children Worldwide; Child Reintegration...Active, not recruitingEvaluation of a Family Strengthening Program Evaluation in Sierra Leone to Prevent Family SeparationParent-Child Relations | Parenting | Emotion Regulation | Economic ProblemsSierra Leone
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Organ, Tissue, Regeneration, Repair and ReplacementRecruiting
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Organ, Tissue, Regeneration, Repair and ReplacementCompletedOral Mucositis | Carcinoma in Situ of Upper Respiratory TractFrance
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Organ, Tissue, Regeneration, Repair and ReplacementRecruitingDiabetic Foot Ulcer | Arterial Ulcer | Chronic Ulcer of Leg or Foot | Venous Ulcer of LegFrance
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Hamid Al-Essa Organ Transplant CenterCompletedCOVID-19 Positive Patients With Acute Kidney InjuryKuwait
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Hamid Al-Essa Organ Transplant CenterCompletedKideny Transplant Recipients With High Cardiovascular Risk ScoreKuwait
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UCSF Benioff Children's Hospital OaklandDepartment of Health and Human Services; FDA Office of Orphan Products DevelopmentCompleted
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Swedish Orphan BiovitrumPRA Health Sciences; Cromsource; BioMérieux; Q2 Solutions; Cytel Inc.; ABF Pharmaceutical...Terminated
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National Institute of Arthritis and Musculoskeletal...FDA Office of Orphan Products DevelopmentCompleted
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Hamid Al-Essa Organ Transplant CenterCompleted
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NSW Organ and Tissue Donation ServiceCompletedTissue and Organ ProcurementAustralia
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Organ, Tissue, Regeneration, Repair and ReplacementCompletedDiabetes Mellitus | Foot Ulcer | Diabetic NeuropathyFrance