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Search clinical trials for: Long Chain 3-hydroxy-acyl-CoA Dehydrogenase Deficiency
Total 80018 results
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University College, LondonLondon School of Hygiene and Tropical Medicine; MRC/UVRI and LSHTM Uganda Research... and other collaboratorsActive, not recruitingHIV Infections | Hiv | HIV-1-infection | Paediatric Human Immunodeficiency Virus InfectionUganda, Zimbabwe, Kenya, South Africa
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Astria Therapeutics, Inc.Enrolling by invitationHereditary AngioedemaUnited States, Canada
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Ultragenyx Pharmaceutical IncActive, not recruitingOrnithine Transcarbamylase (OTC) DeficiencyCanada, United States, France, Spain, United Kingdom
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Avni JoshiEnrolling by invitationCommon Variable Immunodeficiency | Interstitial Lung Disease Due to Systemic DiseaseUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingCastleman Disease | Lymphangioleiomyomatosis | Digestive System Carcinoma | Malignant Neoplasm | Recurrent Breast Carcinoma | Recurrent Thyroid Gland Carcinoma | Metastatic Urothelial Carcinoma | Malignant Female Reproductive System Neoplasm | Neurofibromatosis Type 2 | Recurrent Adult Soft Tissue Sarcoma and other conditionsUnited States
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Vertex Pharmaceuticals IncorporatedActive, not recruitingAlpha-1 Antitrypsin DeficiencyUnited States, United Kingdom, Germany, Ireland
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ViiV HealthcareGlaxoSmithKline; Janssen PharmaceuticalsCompleted
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CSL BehringActive, not recruitingAlpha-1 Antitrypsin DeficiencyFrance
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Swiss Distance University of Applied SciencesETH Zurich (Switzerland); Instituto de Investigacion Nutricional, PeruActive, not recruitingIron Deficiency Anemia | Iron Deficiency (Without Anemia) | Altitude HypoxiaPeru
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National Taiwan University HospitalCompletedCOVID-19 | Vitamin D Deficiency | Acne VulgarisTaiwan
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TJ Biopharma Co., Ltd.CompletedPediatric Growth Hormone DeficiencyChina
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RevimmuneC.R.O. ReSolution Latin America S.A.TerminatedCOVID-19 | LymphocytopeniaBrazil
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RevimmuneM.D. Anderson Cancer Center; Memorial Sloan Kettering Cancer Center; Cancer Research... and other collaboratorsTerminatedCOVID-19 | LymphocytopeniaUnited States
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Landspitali University HospitalMayo Clinic; National Institute of Diabetes and Digestive and Kidney Diseases...CompletedAdenine Phosphoribosyltransferase DeficiencyIceland
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ViiV HealthcareJanssen PharmaceuticalsCompletedHIV InfectionsGermany, Netherlands, France, Belgium, Spain
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National Institute of Allergy and Infectious Diseases...University of Pittsburgh; PPDCompletedPrimary Immunodeficiency | PIDUnited States
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Centre for the AIDS Programme of Research in South...Johns Hopkins University; National Institute of Allergy and Infectious Diseases... and other collaboratorsActive, not recruitingHIV/AIDS | Tuberculosis, PulmonarySouth Africa
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyCompleted
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyActive, not recruitingAlpha 1-Antitrypsin DeficiencyUnited Kingdom, United States, Ireland, Belgium, New Zealand, Spain, Netherlands, Portugal, Canada, Australia, France, Austria, Germany, Sweden
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Gary M Brittenham, MDActive, not recruitingRespiratory Tract Infections | Respiratory Tract Diseases | Respiration Disorders | Lung Diseases | Nutrition Disorders | Vitamin D Deficiency | Asthma | Sickle Cell Disease | Anemia, Sickle Cell | Anemia, Hemolytic, Congenital | Acute Chest Syndrome | Deficiency Diseases VitaminUnited States
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Maximilian DiehnVarian Medical SystemsCompletedStage IA Non-Small Cell Lung Carcinoma | Stage IB Non-Small Cell Lung CarcinomaUnited States
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Barts & The London NHS TrustCompletedBronchiectasis | Common Variable Immunodeficiency | Granulomatous Disease | Immunoglobulin TreatmentUnited Kingdom
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National Cancer Institute (NCI)Active, not recruitingMetastatic Lung Non-Small Cell Carcinoma | Stage IV Lung Cancer AJCC v8 | Metastatic Malignant Neoplasm in the BrainUnited States
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Hospital Infantil Universitario Niño Jesús, Madrid...Universitat Autonoma de Barcelona; Instituto de Investigación Sanitaria de... and other collaboratorsCompletedFanconi AnemiaSpain
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National Cancer Institute (NCI)CompletedAcute Myeloid Leukemia Arising From Previous Myelodysplastic Syndrome | Recurrent Adult Acute Myeloid Leukemia | Adult Acute Myeloid Leukemia in Remission | Myelodysplastic Syndrome With Excess Blasts | Adult Acute Monocytic Leukemia | Adult Acute Myeloid Leukemia With Inv(16)(p13.1q22); CBFB-MYH11 and other conditionsUnited States, Israel, Peru
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Zhejiang UniversityCompleted
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TakedaEnrolling by invitationAlpha1-Antitrypsin DeficiencyUnited Kingdom, Germany, United States, Austria, Portugal
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Vertex Pharmaceuticals IncorporatedCompleted
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National Institute of Allergy and Infectious Diseases...Gilead Sciences; ViiV HealthcareActive, not recruitingHIV InfectionsBrazil, United States, South Africa, Peru, Thailand, Argentina, Vietnam
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Gritstone bio, Inc.Completed
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Vertex Pharmaceuticals IncorporatedCompleted
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Grifols Therapeutics LLCEnrolling by invitationPulmonary Emphysema in Alpha-1 Antitrypsin DeficiencyUnited States, New Zealand, Denmark, Australia, Finland, Estonia, Canada, Poland, Russian Federation, Sweden, France
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Grifols Therapeutics LLCActive, not recruitingPulmonary Emphysema in Alpha-1 PI DeficiencyUnited States, Australia, Denmark, New Zealand, Estonia, Poland, Russian Federation, Sweden, Brazil, Canada, France, Finland
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Merck Sharp & Dohme LLCActive, not recruitingHIV InfectionUnited States, Australia, Austria, Canada, Finland, France, Germany, Italy, Japan, Puerto Rico, Spain
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Columbia UniversityNational Heart, Lung, and Blood Institute (NHLBI); Alpha-1 FoundationActive, not recruitingAlpha 1-Antitrypsin Deficiency | Genetic DiseaseUnited States
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Gilead SciencesActive, not recruitingHIV Infections | Acquired Immune Deficiency Syndrome (AIDS)United States, Thailand, Uganda, South Africa, Zimbabwe
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Gilead SciencesActive, not recruitingHIV-1-infectionUnited States, Spain, France, Taiwan, Japan, Thailand, Dominican Republic, Germany, Canada, Italy, South Africa
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Longboard PharmaceuticalsAvailableDravet Syndrome | Lennox Gastaut Syndrome | Developmental and Epileptic EncephalopathiesUnited States
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Khon Kaen HospitalCompletedTuberculosis | PulmonaryThailand
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Rocket Pharmaceuticals Inc.Enrolling by invitationLeukocyte Adhesion DeficiencySpain, United States, United Kingdom
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Zagazig UniversityCompletedVitamin D Deficiency | Sickle Cell Disease | Bone Mineral Density | Health Related Quality of Life | Hand Grip StrengthEgypt
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M.D. Anderson Cancer CenterActive, not recruitingMetastatic Lung Non-Small Cell Carcinoma | Stage IVA Lung Cancer AJCC v8 | Stage IVB Lung Cancer AJCC v8 | Stage IV Lung Cancer AJCC v8 | Stage IIIC Lung Cancer AJCC v8 | Recurrent Lung Non-Small Cell CarcinomaUnited States
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GlaxoSmithKlineCompletedPulmonary Disease, Chronic ObstructiveJapan
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University Children's Hospital, ZurichCompletedDiagnosis | Childhood Pneumonia | Mycoplasma Pneumonia | Antibody-secreting Cells | Enzyme-linked Immunospot (ELISpot)
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TakedaActive, not recruitingPrimary Immunodeficiency Diseases (PID)Japan
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New York State Psychiatric InstituteNational Institute on Drug Abuse (NIDA); Columbia University; Alliance for Postive... and other collaboratorsCompletedCovid-19 | Substance Use | Opioid UseUnited States
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National Cancer Institute (NCI)CompletedBrain Stem Glioma | Childhood Spinal Cord Neoplasm | Childhood Cerebral Anaplastic Astrocytoma | Cerebral Astrocytoma | Childhood Cerebellar Anaplastic AstrocytomaUnited States, Canada
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Children's Hospital of Orange CountyActive, not recruitingNeuronal Ceroid-Lipofuscinoses | Neuronal Ceroid Lipofuscinosis CLN2 | Spinocerebellar Ataxia, Autosomal Recessive 7United States
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Yale UniversityNational Institute of Allergy and Infectious Diseases (NIAID); Robert Leet...Active, not recruitingMultiple Sclerosis | Autoimmune Blistering Disease | B-Cell DeficiencyUnited States
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Lumos PharmaEnrolling by invitationGrowth Hormone DeficiencyUnited States, Australia