- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: cone-rod dystrophy
Total 1178 results
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PfizerActive, not recruitingDuchenne Muscular DystrophyUnited States, Spain, Belgium, Korea, Republic of, Taiwan, Canada, Australia, Germany, Japan, France, Italy, United Kingdom, Russian Federation, Israel, Switzerland
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PfizerActive, not recruitingMuscular Dystrophy, DuchenneUnited States, Australia
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National Eye Institute (NEI)Active, not recruitingRetinitis Pigmentosa | Inherited Ophthalmic DiseasesUnited States
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University of the Incarnate WordNational Eye Institute (NEI)CompletedColor Vision Defects | Color Blindness | Color Blindness, Red | Color Blindness, GreenUnited States
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PTC TherapeuticsCompletedNonsene Mutation Duchenne Muscular DystrophyUnited States
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Université de SherbrookeCentre de recherche du Centre hospitalier universitaire de Sherbrooke; Interdisciplinary... and other collaboratorsEnrolling by invitationUrinary Incontinence | Myotonic Dystrophy Type 1Canada
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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University of Southern CaliforniaLimbix Health, Inc.; BehaVR, Inc.CompletedBack Pain | Complex Regional Pain SyndromesUnited States
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Sarepta Therapeutics, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Korea, Republic of, Italy, United Kingdom, Canada, Poland, Spain, France, Germany, Belgium, Australia, Czechia, Serbia, Greece, Argentina, Bulgaria, Denmark, Hungary, India, Ireland, Israel, Mexico, Russian Federation, ...
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Nanoscope Therapeutics Inc.CompletedEye Diseases | Retinal Degeneration | Retinal Diseases | Retinitis Pigmentosa | Retinitis | Eye Diseases, Hereditary | Retinal DystrophiesUnited States, Puerto Rico
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Massachusetts Eye and Ear InfirmaryCompletedFuchs' Endothelial DystrophyUnited States
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Sarepta Therapeutics, Inc.Hansa Biopharma ABActive, not recruitingDuchenne Muscular DystrophySpain
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FibroGenTerminatedDuchenne Muscular DystrophyUnited States, Belgium, Israel, Spain, Canada, Australia, Switzerland, United Kingdom, France, China, Netherlands, Italy, Austria, Czechia
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Fulcrum TherapeuticsActive, not recruitingFacioscapulohumeral Muscular Dystrophy (FSHD)United States, Spain, Italy, Denmark, Canada, Germany, France, Netherlands, United Kingdom
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Xiamen Ophthalmology Center Affiliated to Xiamen...Active, not recruitingBietti's Crystalline DystrophyChina
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Gaziosmanpasa Research and Education HospitalCompletedDuchenne or Becker Muscular DystrophyTurkey
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Daiichi Sankyo Co., Ltd.Orphan Disease Treatment Institute Co., Ltd.Completed
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Institut National de la Santé Et de la Recherche...CompletedDiabetes | Age-related Macular Degeneration | Retinal Dystrophies | Arterial Hypertension | Traumatic Retinopathy | Toxic RetinopathiesFrance
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Sahra ŞirvanEnrolling by invitationDuchenne Muscular DystrophyTurkey
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Wave Life Sciences Ltd.Active, not recruitingDuchenne Muscular DystrophyJordan, United Kingdom
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Uppsala UniversityCompletedChronic Pain | Complex Regional Pain SyndromesSweden
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Hacettepe UniversityCompleted
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Spark TherapeuticsActive, not recruitingInherited Retinal Dystrophy Due to RPE65 Mutations
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Sheffield Children's NHS Foundation TrustSheffield Hallam University; National Institute for Health Research, United... and other collaboratorsActive, not recruiting
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Fondazione Serena Onlus - Centro Clinico NeMO MilanoAzienda Ospedaliera Città della Salute e della Scienza di Torino; Fondazione... and other collaboratorsActive, not recruiting
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Stanford UniversityWithdrawnComplex Regional Pain SyndromesUnited States
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Centre Hospitalier Universitaire de NiceWithdrawn
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Eye Hospital Pristina KosovoEnrolling by invitationMacular Corneal DystrophyKosovo
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Istituto Auxologico ItalianoFondazione Serena Onlus - Centro Clinico NeMO MilanoCompletedMyotonic Dystrophy 1Italy
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.Active, not recruitingDuchenne Muscular DystrophyKorea, Republic of, Chile, Japan, China, United Kingdom, Netherlands, Spain, Norway, Russian Federation, Australia, Greece, Italy, New Zealand, Turkey, Mexico, Czechia, Canada
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Sarepta Therapeutics, Inc.Active, not recruitingLimb-Girdle Muscular Dystrophy, Type 2EUnited States
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The Cleveland ClinicCompletedComplex Regional Pain SyndromeUnited States
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Centre Hospitalier Universitaire de NiceActive, not recruitingMuscular Dystrophy | FacioscapulohumeralFrance
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Columbia UniversityMuscular Dystrophy Association; Stevens Institute of TechnologyCompletedDuchenne Muscular Dystrophy | Spinal Muscular Atrophy Type 3United States
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Cyprus University of TechnologyThe Cyprus Foundation for Muscular Dystrophy ResearchCompletedMultiple SclerosisCyprus
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Avidity Biosciences, Inc.Enrolling by invitationDuchenne Muscular Dystrophy | DMD | Exon 44 | DuchenneUnited States
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University of PittsburghRespirtech, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Harmony Biosciences, LLCActive, not recruitingMyotonic Dystrophy 1 | Excessive Daytime SleepinessUnited States, Canada
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Avidity Biosciences, Inc.CompletedMyotonic Dystrophy | Myotonic Disorders | Myotonic Dystrophy Type 1 (DM1) | Myotonic Dystrophy 1 | Myotonic Muscular Dystrophy | DM1 | Dystrophy Myotonic | Steinert DiseaseUnited States
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Nemours Children's ClinicCompletedMuscular Dystrophy | Spinal Muscular Atrophy | Arthrogryposis
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Istituti Clinici Scientifici Maugeri SpAAzienda Ospedaliero, Universitaria PisanaEnrolling by invitationComplex Regional Pain Syndromes | Neuropathic Pain | Failed Back Surgery Syndrome | Limb IschemiaItaly
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Alkeus Pharmaceuticals, Inc.Enrolling by invitationStargardt Disease | Stargardt Macular Degeneration | Stargardt Macular Dystrophy | Autosomal Recessive Stargardt Disease 1 (ABCA4-related)United States
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NYU Langone HealthNational Eye Institute (NEI)Active, not recruitingFuch's Dystrophy | Corneal Disorders | Prior SurgeryUnited States
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Spark TherapeuticsActive, not recruitingConfirmed Biallelic RPE65 Mutation-associated Retinal DystrophyUnited States
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Columbia UniversityUniversitat Autonoma de Barcelona; Instituto de Salud Carlos III; University... and other collaboratorsActive, not recruitingThymidine Kinase 2 Deficiency | Mitochondrial DNA Depletion Syndrome 2 Myopathic TypeUnited States
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PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, Duchenne | Musculoskeletal DiseaseUnited States, Taiwan, India, Korea, Republic of, Thailand, Australia, Brazil, Bulgaria, Canada, China, Hong Kong, Malaysia, Mexico, Poland, Puerto Rico, Russian Federation, Turkey, Japan
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Hospital of South West JutlandActive, not recruitingBariatric Surgery Candidate | Male Hypogonadism | Muscle LossDenmark
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Çağtay MadenCompleted
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ItalfarmacoCompletedDuchenne and Becker Muscular Dystrophy | Polycytemia VeraCanada
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Innostellar Biotherapeutics Co.,LtdActive, not recruitingInherited Retinal Dystrophy Associated With RPE65 MutationsChina