- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: thérapie génique
Total 26146 results
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University of FloridaLacerta TherapeuticsCompletedPompe DiseaseUnited States
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Adverum Biotechnologies, Inc.Completed
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National Cancer Institute (NCI)CompletedMelanoma | Cervical Cancer | Breast Cancer | Renal Cancer | Urothelial CancerUnited States
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Neurocrine BiosciencesVoyager TherapeuticsCompletedBrain Diseases | Central Nervous System Diseases | Nervous System Diseases | Parkinson's Disease | Parkinsonian Disorders | Movement Disorders | Neurodegenerative Diseases | Idiopathic Parkinson's Disease | Basal Ganglia DiseaseUnited States
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Xalud Therapeutics, Inc.WithdrawnOsteoarthritis, SpineAustralia
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Holostem Terapie Avanzate s.r.l.Paracelsus Medical UniversityTerminated
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Henry Ford Health SystemActive, not recruitingProstate CancerUnited States
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Holostem Terapie Avanzate s.r.l.Paracelsus Medical UniversityTerminatedRecessive Dystrophic Epidermolysis BullosaAustria
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National Cancer Institute (NCI)TerminatedLymphoma, B-Cell | Chronic Lymphocytic Leukemia | Lymphoma, Non-hodgkins | B-Cell Chronic Lymphocytic LeukemiaUnited States
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Genenta ScienceIRCCS San RaffaeleTerminated
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King Khaled Eye Specialist HospitalKing Faisal Specialist Hospital & Research CenterCompletedRetinitis Pigmentosa | Retinal DiseaseSaudi Arabia
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Institut National de la Santé Et de la Recherche...Assistance Publique - Hôpitaux de Paris; European Leukodystrophy AssociationActive, not recruitingMetachromatic LeukodystrophyFrance
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Ultragenyx Pharmaceutical IncCompletedHemophilia BUnited States, United Kingdom
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Assistance Publique - Hôpitaux de ParisEuroFancolenCompleted
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Cogent Biosciences, Inc.Terminated
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Novartis PharmaceuticalsCompletedUnilateral Severe to Profound Hearing Loss OR Bilateral Severe to Profound Hearing LossUnited States
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Assistance Publique - Hôpitaux de ParisCompletedX-linked Severe Combined ImmunodeficiencyFrance
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Great Ormond Street Hospital for Children NHS Foundation...Orchard TherapeuticsCompletedAdenosine Deaminase Deficiency | Severe Combined Immunodeficiencies (SCID)United Kingdom
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IRCCS San RaffaeleFondazione TelethonActive, not recruiting
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REGENXBIO Inc.Enrolling by invitation
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Mie UniversityFiverings Co., Ltd.; Shionogi; Takara Bio Inc.; Statcom Co. Ltd.Completed
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Nanoscope Therapeutics Inc.CompletedRetinal Degeneration | Retinal Diseases | Retinitis PigmentosaIndia
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GenethonInstitute of Child Health; Great Ormond Street Hospital for Children NHS Foundation...Completed
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Hemera BiosciencesWithdrawnGeographic Atrophy | Dry Age-related Macular Degeneration | Gene Therapy | Intravitreal Injection
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Donald B. Kohn, M.D.National Institutes of Health (NIH); FDA Office of Orphan Products DevelopmentCompletedSevere Combined ImmunodeficiencyUnited States
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CG Oncology, Inc.TerminatedCarcinoma in Situ | Transitional Cell Carcinoma | Bladder Cancer | Carcinoma in Situ Concurrent With Papillary TumorsUnited States
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Janssen Research & Development, LLCCompletedDry Age-related Macular DegenerationUnited States
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National Cancer Institute (NCI)CompletedMelanoma | Breast Cancer | Non-Small Cell Lung Cancer | Meningioma | Hepatocellular CancerUnited States
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GenSight BiologicsCompletedLeber Hereditary Optic NeuropathyUnited States, France, Italy, Spain, United Kingdom
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REGENXBIO Inc.CompletedHomozygous Familial Hypercholesterolemia (HoFH)United States
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National Cancer Institute (NCI)WithdrawnMetastatic HPV-16 Positive Squamous Cell Anal CancerUnited States
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AnGes USA, Inc.CompletedVascular Diseases | Peripheral Arterial Disease | Critical Limb IschemiaUnited States
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Sangamo TherapeuticsAlzheimer's Disease Cooperative Study (ADCS)CompletedAlzheimer's DiseaseUnited States
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Triple-Gene, LLCIntrexon Corporation; Precigen, IncCompletedCardiovascular Diseases | Heart Failure | Heart-Assist DeviceUnited States
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BiogenCompletedGlioblastoma Multiforme | Gliosarcoma | Anaplastic Astrocytoma | Oligoastrocytoma, MixedUnited States
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Loyola UniversityNational Cancer Institute (NCI)Active, not recruiting
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STZ eyetrialUniversity Hospital TuebingenCompleted
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Huazhong University of Science and TechnologyShiyan Taihe HospitalActive, not recruitingLeber Hereditary Optic NeuropathyChina
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United BioSource, LLCAveXis, Inc.Approved for marketing
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Bin LiUnknownAcute LHON | Onset Within Three Months | Onset Between 3 to 6 Months | Onset Between 6 to 12 Months | Onset Between 12 to 24 Months | Onset Between 24 to 60 Months | Onset Over 60 MonthsChina
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Rocket Pharmaceuticals Inc.Enrolling by invitationFanconi Anemia | Fanconi Anemia Complementation Group ASpain
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Shenzhen Geno-Immune Medical InstituteShenzhen Children's Hospital; Shenzhen Hospital of Southern Medical UniversityUnknown
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MultiVir, Inc.UnknownLymphoma | Solid TumorUnited States
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National Cancer Institute (NCI)TerminatedMelanoma | Colon Cancer | Gastrointestinal Cancer | Hepatocellular Cancer | Genitourinary CancerUnited States
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Sangamo TherapeuticsCompletedIdiopathic Parkinson's DiseaseUnited States
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University of Massachusetts, WorcesterNational Heart, Lung, and Blood Institute (NHLBI); University of Florida; National... and other collaboratorsCompletedAlpha 1-Antitrypsin DeficiencyUnited States
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Cogent Biosciences, Inc.TerminatedSolid Tumor | HER-2 Protein OverexpressionUnited States
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Cogent Biosciences, Inc.Seagen Inc.TerminatedMultiple Myeloma | Refractory Multiple Myeloma | Multiple Myeloma in RelapseUnited States
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University of PennsylvaniaNational Cancer Institute (NCI); BiogenCompletedPleural Mesothelioma | Metastatic Pleural EffusionsUnited States