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Search clinical trials for: Genetic Disorders
Total 153412 results
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Washington University School of MedicineAlzheimer's Association; Eisai Inc.Not yet recruitingDementia | Alzheimer's Disease | Alzheimer's Disease, FamilialUnited States, Australia, United Kingdom
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Shanghai Ninth People's Hospital Affiliated to...RecruitingNeurofibromatosis 1 | Plexiform NeurofibromaChina
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The First Affiliated Hospital of Zhejiang Chinese...RecruitingInflammatory Response | Tourette Syndrome in Children | Food IntoleranceChina
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Regeneron PharmaceuticalsIntellia TherapeuticsNot yet recruiting
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IRCCS Eugenio MedeaRecruiting
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University of PennsylvaniaNot yet recruitingParkinson Disease | Alzheimer Disease | ALS | Polyneuropathies | Frontotemporal Dementia | Pheochromocytoma | Thoracic Aortic Aneurysm | Paraganglioma | Genetic Predisposition | Cardiomyopathy Non-ischemic
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IRCCS Eugenio MedeaRecruitingMuscular Dystrophies | Becker Muscular Dystrophy | Limb Girdle Muscular Dystrophy | Facio-Scapulo-Humeral DystrophyItaly
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Fondazione Policlinico Universitario Agostino Gemelli...Recruiting
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Enzyre B.V.Indiana Hemophilia & Thrombosis CenterNot yet recruiting
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Chugai PharmaceuticalNot yet recruitingAntiphospholipid Syndrome (APS) | Immune Thrombocytopenia (ITP) | Dermatomyositis (DM) | Bullous Pemphigoid (BP) | Behçet's Syndrome (BS) | Immune-mediated Necrotizing Myopathy (IMNM)United States, Japan
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SensorionNot yet recruitingOtorhinolaryngologic Diseases | Ear Diseases | Hearing Disorders | Deafness | Hearing Loss, Sensorineural | Congenital Deafness | DFNB9 | OTOF Gene MutationFrance
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Hospices Civils de LyonNot yet recruiting
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingDuchenne Muscular Dystrophy | Natural History | Motor Function; RetardationItaly
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Harmony Biosciences, LLCRecruiting
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Dan BingNot yet recruitingCongenital Hearing Loss | Congenital Deafness
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AstraZenecaRecruiting
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National Cancer Institute (NCI)Not yet recruitingLeukemia, Lymphocytic, Chronic, B-Cell | B-Cell Chronic Lymphocytic Leukemia | B-Lymphocytic Leukemia, ChronicUnited States
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Chang Gung UniversityRecruiting
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University of MalagaNot yet recruitingMuscular Dystrophy | Duchenne Muscular Dystrophy | Becker Muscular DystrophySpain
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Fondazione SISA (Societa Italiana per lo Studio...RecruitingFamilial Hypercholesterolemia | Genetic DisorderItaly
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Seoul National University HospitalNot yet recruitingMuscular Dystrophy, Duchenne | Upper Extremity | Orthotic DevicesKorea, Republic of
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AstraZenecaNot yet recruitingNeurofibromatosis 1 | Neurofibroma, Plexiform
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Xuanwu Hospital, BeijingNot yet recruiting
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Assistance Publique - Hôpitaux de ParisVaincre la MucoviscidoseNot yet recruiting
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IRCCS Eugenio MedeaRecruitingEpilepsy | Angelman Syndrome | Dup15q SyndromeItaly
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Institut de Myologie, FranceAssociation Française contre les Myopathies (AFM), ParisNot yet recruitingMerosin Deficient Congenital Muscular DystrophyFrance
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CHU de ReimsRecruitingPrimary Immunodeficiency | Common Variable Immunodeficiency | Igg Subclass Deficiency | Selective IgM DeficiencyFrance
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SensorionNot yet recruitingSensorineural Hearing Loss, BilateralFrance
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Hasan Kalyoncu UniversityRecruitingDown SyndromeTurkey
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University Hospital, BonnSwedish Orphan BiovitrumRecruitingHaemophilia A | Synovitis | Hemophilia Arthropathy | SonographyGermany
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Equilibra Bioscience LLCRecruitingHemophilia A | Hemophilia B | Healthy ParticipantsUnited States
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Fondazione IRCCS Ca' Granda, Ospedale Maggiore...Federico II University; Istituto Auxologico Italiano; Università degli Studi...RecruitingBeckwith-Wiedemann SyndromeItaly
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IRCCS Fondazione Stella MarisAzienda USL Toscana Nord Ovest; University of Dublin, Trinity College; Meyer...Recruiting
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John Paul II Hospital, KrakowRecruitingTransthyretin AmyloidosisPoland
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Children's Hospital ColoradoUniversity of Colorado, Denver; University of Pennsylvania; University of Alabama... and other collaboratorsRecruiting
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Fondation Ophtalmologique Adolphe de RothschildNot yet recruitingAlbinism, Ocular
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Roswell Park Cancer InstituteNot yet recruitingRecurrent Mantle Cell Lymphoma | Recurrent Diffuse Large B-Cell Lymphoma | Refractory Diffuse Large B-Cell Lymphoma | Refractory Chronic Lymphocytic Leukemia | Refractory Mantle Cell Lymphoma | Recurrent High Grade B-Cell Lymphoma | Recurrent Transformed Follicular Lymphoma to Diffuse Large B-Cell... and other conditionsUnited States
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Huntington Study GroupRoche Products LimitedNot yet recruiting
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AstraZenecaRecruitingTransthyretin Amyloidosis Cardiomyopathy, Heart Failure With Preserved Ejection FractionRussian Federation
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Jirair Krikor BedoyanUltragenyx Pharmaceutical IncRecruitingPyruvate Dehydrogenase Complex DeficiencyUnited States
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Washington University School of MedicineNational Cancer Institute (NCI); The Foundation for Barnes-Jewish HospitalRecruitingMultiple Myeloma | Rectal Cancer | Cholangiocarcinoma | Colon CancerUnited States
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Rett Syndrome Research TrustNot yet recruitingRett SyndromeUnited States
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IRCCS Eugenio MedeaRecruiting
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IRCCS San RaffaeleRecruiting
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GCS Ramsay Santé pour l'Enseignement et la RechercheNot yet recruiting
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Assistance Publique - Hôpitaux de ParisNot yet recruitingAutism Spectrum DisorderFrance
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Centre Hospitalier Sud FrancilienNot yet recruiting
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Mahidol UniversityNot yet recruitingBMI | Metabolic Syndrome | Insulin Resistance | NAFLD | Genetic Polymorphism | Cardiovascular Disease (CVD) | MASLD | Daily Step Count
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Craig EricksonHealx LimitedRecruitingFragile X SyndromeUnited States