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Search clinical trials for: Hemolytic Paroxysmal Nocturnal Hemoglobinuria
Total 2612 results
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Alexion Pharmaceuticals, Inc.Not yet recruitingPregnancy | Paroxysmal Nocturnal Hemoglobinuria (PNH) | Atypical Hemolytic Uremic Syndrome (aHUS) | Ultomiris-exposed Pregnant/ Postpartum | Generalized Myasthenia Gravis (gMG) | Neuromyelitis Optica Spectrum Disorder (NMOSD)
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Omeros CorporationRecruitingParoxysmal Nocturnal HemoglobinuriaSwitzerland, Germany, Ukraine, United Kingdom
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Longbio PharmaRecruitingParoxysmal Nocturnal Hemoglobinuria (PNH)China
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Chengdu Suncadia Medicine Co., Ltd.RecruitingParoxysmal Nocturnal HemoglobinuriaChina
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AstraZenecaRecruitingParoxysmal Nocturnal HemoglobinuriaChina
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Wuhan Createrna Science and Technology Co., LtdNot yet recruitingParoxysmal Nocturnal Hemoglobinuria (PNH)
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BioCryst PharmaceuticalsRecruitingParoxysmal Nocturnal HemoglobinuriaSouth Africa, Malaysia
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Wuhan Createrna Science and Technology Co., LtdRecruitingParoxysmal Nocturnal HemoglobinuriaChina
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Omeros CorporationRecruitingParoxysmal Nocturnal HemoglobinuriaGermany, Greece, Switzerland, United Kingdom
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Omeros CorporationRecruitingParoxysmal Nocturnal HemoglobinuriaUkraine
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ADARx Pharmaceuticals, Inc.ADARx Australia Pty LtdRecruitingParoxysmal Nocturnal Hemoglobinuria (PNH)Australia
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Swedish Orphan BiovitrumRecruitingParoxysmal Nocturnal HemoglobinuriaSpain
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Aplastic Anemia and MDS International FoundationNational Organization for Rare DisordersRecruiting
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Regeneron PharmaceuticalsRecruitingParoxysmal Nocturnal HemoglobinuriaTaiwan, Korea, Republic of, Turkey, Spain, Thailand, Singapore, Japan, Canada, Malaysia, Poland, Italy
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NovelMed TherapeuticsNot yet recruitingPNH - Paroxysmal Nocturnal Hemoglobinuria
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NovelMed TherapeuticsNot yet recruitingParoxysmal Nocturnal Hemoglobinuria
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NovelMed TherapeuticsNot yet recruitingParoxysmal Nocturnal Hemoglobinuria
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Novartis PharmaceuticalsRecruitingParoxysmal Nocturnal HemoglobinuriaFrance, Spain, Italy, Turkey, Germany, United States, Korea, Republic of, United Kingdom
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Kira Pharmacenticals (US), LLC.Not yet recruitingParoxysmal Nocturnal HemoglobinuriaChina
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Alexion Pharmaceuticals, Inc.RecruitingParoxysmal Nocturnal HemoglobinuriaItaly
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Regeneron PharmaceuticalsRecruitingParoxysmal Nocturnal HemoglobinuriaMexico, Korea, Republic of, Turkey, Italy, United Kingdom, Thailand, Poland, Singapore, Spain, Taiwan, Canada, Japan, United States, Malaysia, Greece, Romania, Hungary
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsRecruitingCongenital Amegakaryocytic Thrombocytopenia | Paroxysmal Nocturnal Hemoglobinuria | Shwachman-Diamond Syndrome | Bone Marrow Failure Syndrome | Congenital Pure Red Cell Aplasia | Hereditary Sideroblastic Anemia | Hematologic Neoplasm With Germline GATA2 Mutation | Hematologic Neoplasm With Germline... and other conditionsUnited States
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Apellis Pharmaceuticals, Inc.RecruitingParoxysmal Nocturnal Hemoglobinuria (PNH) | Paroxysmal HemoglobinuriaMalaysia, United States, Czechia, France, Netherlands, Serbia, Spain, Thailand, United Kingdom
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Novartis PharmaceuticalsRecruitingParoxysmal Nocturnal HemoglobinuriaUnited States, Korea, Republic of, Singapore, Germany, Taiwan, Italy, Turkey, France, Malaysia, Lithuania, Netherlands, United Kingdom, Japan, Czechia, Spain, China, Brazil
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Hoffmann-La RocheChugai PharmaceuticalRecruitingParoxysmal Nocturnal HemoglobinuriaUnited States, Korea, Republic of, Spain, Germany, Italy, Sweden, Netherlands, Japan, Belgium, Greece, Colombia, Saudi Arabia, Turkey, Poland, Ireland, Brazil, Canada, Czechia, Estonia, France, Hong Kong, Singapore, Taiwan, United Kingdom and more
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingParoxysmal Nocturnal Hemoglobinuria (PNH) | Severe Aplastic Anemia (SAA) | Hypo-Plastic Myelodysplastic Syndrome (MDS)United States
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Children's Hospital of PhiladelphiaRecruitingParoxysmal Nocturnal Hemoglobinuria | Acquired Aplastic Anemia | Inherited Bone Marrow Failure SyndromesUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingSickle Cell Disease | Severe Congenital Neutropenia | Paroxysmal Nocturnal Hemoglobinuria | Glanzmann Thrombasthenia | Shwachman-Diamond Syndrome | Diamond Blackfan Anemia | Transfusion Dependent Alpha- or Beta- Thalassemia | Non-Malignant Hematologic DisordersUnited States
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Alexion Pharmaceuticals, Inc.RecruitingParoxysmal Nocturnal HemoglobinuriaUnited States
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Alexion Pharmaceuticals, Inc.CompletedParoxysmal Nocturnal HemoglobinuriaItaly, Spain, Belgium, France, Turkey, Austria, Brazil, Netherlands, Australia, Finland, Russian Federation, Sweden, Canada, United States
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Novartis PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)China, Germany, Singapore, Korea, Republic of, Italy, United Kingdom, Malaysia, France
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Novartis PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)Italy, Japan, Taiwan, Germany, France, United Kingdom, Spain, Korea, Republic of, Czechia, Brazil, Netherlands, United States
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Roswell Park Cancer InstituteActive, not recruitingAcute Myeloid Leukemia | Polycythemia Vera | Myelofibrosis | Chronic Myelomonocytic Leukemia | Waldenstrom Macroglobulinemia | Acute Lymphoblastic Leukemia | Chronic Lymphocytic Leukemia | Secondary Acute Myeloid Leukemia | Sickle Cell Disease | Myelodysplastic Syndrome | Plasma Cell Myeloma | Chronic Granulomatous... and other conditionsUnited States
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Alexion Pharmaceuticals, Inc.Active, not recruitingParoxysmal Nocturnal HemoglobinuriaFrance, Italy, Spain, United States, Thailand, Korea, Republic of, United Kingdom, Israel, Czechia, Greece, Poland, Brazil, Japan, Canada, Malaysia
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Samsung Bioepis Co., Ltd.CompletedParoxysmal Nocturnal HemoglobinuriaKorea, Republic of, Taiwan, Malaysia, Thailand, Romania, India, Mexico, Ukraine
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SanofiCompletedParoxysmal Nocturnal HemoglobinuriaUnited States
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Lawson Health Research InstituteAlexion Pharmaceuticals, Inc.Active, not recruitingTransient Ischemic Attack | Paroxysmal Nocturnal Hemoglobinuria | Cerebral Vein Thrombosis | Embolic Stroke of Undetermined SourceCanada
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Hoffmann-La RocheActive, not recruiting
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Hoffmann-La RocheChugai PharmaceuticalActive, not recruitingParoxysmal Hemoglobinuria, NocturnalFrance, Korea, Republic of, Italy, Japan, Germany, Hungary, Netherlands
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Hoffmann-La RocheChugai PharmaceuticalActive, not recruitingParoxysmal Nocturnal HemoglobinuriaSpain, Korea, Republic of, France, Sweden, Thailand, Malaysia, China, Turkey, Netherlands, Japan, Australia, United Kingdom, Germany, Brazil, Romania, Argentina, Poland, Greece, Hong Kong, Lithuania, Mexico, Philippines, Portugal, Sin... and more
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BioCryst PharmaceuticalsTerminatedBCX9930 for Treatment of PNH in Subjects With Inadequate Response to C5 Inhibitor Therapy (REDEEM-1)Paroxysmal Nocturnal Hemoglobinuria (PNH)United Kingdom, Hungary, France, Italy, Spain
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BioCryst PharmaceuticalsTerminatedParoxysmal Nocturnal Hemoglobinuria (PNH)Malaysia, South Africa, Korea, Republic of
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BioCryst PharmaceuticalsActive, not recruitingParoxysmal Nocturnal HemoglobinuriaUnited Kingdom, Hungary, France, Spain, Malaysia, South Africa, Korea, Republic of
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AKARI TherapeuticsEnrolling by invitationParoxysmal Nocturnal Hemoglobinuria (PNH)United States
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Novartis PharmaceuticalsAvailableParoxysmal Nocturnal Hemoglobinuria (PNH) | C3 Glomerulopathy (C3G)
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Alexion Pharmaceuticals, Inc.CompletedParoxysmal Nocturnal HemoglobinuriaFrance, Italy, Spain, United States, Taiwan, Thailand, Korea, Republic of, Japan, Malaysia, Brazil, Germany, Israel, Czechia, Netherlands, Greece, United Kingdom, Canada, Poland
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Chengdu Suncadia Medicine Co., Ltd.Active, not recruitingParoxysmal Nocturnal HemoglobinuriaChina
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Alexion Pharmaceuticals, Inc.AstraZenecaActive, not recruitingParoxysmal Nocturnal HemoglobinuriaChina
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Novartis PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH) With Signs of Active HemolysisItaly, Germany, France
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Novartis PharmaceuticalsCompletedParoxysmal Nocturnal HemoglobinuriaTaiwan, Singapore, Korea, Republic of, Malaysia