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Search clinical trials for: Heredodegenerative Disorders, Nervous System
Total 246685 results
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Ionis Pharmaceuticals, Inc.Not yet recruitingMethyl CpG Binding Protein 2 (MECP2) Duplication Syndrome
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Hospices Civils de LyonNot yet recruitingWilson DiseaseFrance
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AstraZenecaRecruitingCarpal Tunnel Syndrome | Amyloidosis | Polyneuropathy | Hereditary Transthyretin AmyloidosisRussian Federation
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Poitiers University HospitalRecruiting
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SpinogenixAvance Clinical Pty Ltd.Not yet recruiting
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Avidity Biosciences, Inc.Not yet recruitingMyotonic Dystrophy | Myotonic Disorders | Myotonia | Myotonic Dystrophy Type 1 (DM1) | Myotonic Dystrophy 1 | Myotonic Muscular Dystrophy | DM1 | Dystrophy Myotonic | Steinert Disease | Steinert
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Nido Biosciences, Inc.RecruitingSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseKorea, Republic of, Denmark, Italy, United Kingdom
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Johns Hopkins UniversityNational Center for Complementary and Integrative Health (NCCIH); Bowdoin CollegeRecruitingTourette Syndrome | Tic Disorders | Tourette's Disorder | Persistent Tic Disorder | Chronic Motor Tic Disorder | Chronic Vocal Tic Disorder | Persistent Motor Tic Disorder | Persistent Vocal Tic DisorderUnited States
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Istanbul University - Cerrahpasa (IUC)Not yet recruitingCarpal Tunnel Syndrome | Entrapment Neuropathy | Median Nerve EntrapmentTurkey
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Steminent US, Inc.Not yet recruitingSpinocerebellar Ataxias
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GRIN Therapeutics, Inc.RecruitingTuberous Sclerosis Complex | Focal Cortical DysplasiaSpain, United Kingdom, Australia, Belgium, Canada, Italy, Poland
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University College, LondonLondon School of Hygiene and Tropical Medicine; King's College London; University... and other collaboratorsRecruitingTourette Syndrome | Deep Brain StimulationUnited Kingdom
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University of UtahRecruitingClinical Characteristics and Temporal Properties of Individual Tics in Persistent Tic Disorder (PTD)Tourette Syndrome | Tic Disorders | Tics | Tourette Syndrome in Children | Tourette Syndrome in Adolescence | Vocal Tic | Motor Tic | Tics/TremorUnited States
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Shanghai Ninth People's Hospital Affiliated to...RecruitingNeurofibromatosis 1 | Plexiform NeurofibromaChina
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The First Affiliated Hospital of Zhejiang Chinese...RecruitingInflammatory Response | Tourette Syndrome in Children | Food IntoleranceChina
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IRCCS Eugenio MedeaRecruiting
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AstraZenecaRecruiting
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Chang Gung UniversityRecruiting
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AstraZenecaNot yet recruitingNeurofibromatosis 1 | Neurofibroma, Plexiform
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Xuanwu Hospital, BeijingNot yet recruiting
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IRCCS Fondazione Stella MarisAzienda USL Toscana Nord Ovest; University of Dublin, Trinity College; Meyer...Recruiting
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John Paul II Hospital, KrakowRecruitingTransthyretin AmyloidosisPoland
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Children's Hospital ColoradoUniversity of Colorado, Denver; University of Pennsylvania; University of Alabama... and other collaboratorsRecruiting
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Huntington Study GroupRoche Products LimitedRecruitingHuntington DiseaseUnited States
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AstraZenecaRecruitingTransthyretin Amyloidosis Cardiomyopathy, Heart Failure With Preserved Ejection FractionRussian Federation
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Jirair Krikor BedoyanUltragenyx Pharmaceutical IncRecruitingPyruvate Dehydrogenase Complex DeficiencyUnited States
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Rett Syndrome Research TrustNot yet recruitingRett SyndromeUnited States
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Craig EricksonHealx LimitedRecruitingFragile X SyndromeUnited States
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Maastricht University Medical CenterRecruitingQuality of Life | Tuberous Sclerosis | Basal Cell Nevus Syndrome | Cutis Laxa | Epidermolysis Bullosa | Ichthyosis | Ectodermal Dysplasia | Albinism | Birt-Hogg-Dube Syndrome | Palmoplantar KeratosesNetherlands
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ENCellRecruitingCharcot-Marie-Tooth Disease Type 1AKorea, Republic of
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Noema Pharma AGNot yet recruiting
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University of California, Los AngelesRecruitingTuberous SclerosisUnited States
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Massachusetts General HospitalJohns Hopkins UniversityNot yet recruitingNeurofibromatosis 1 | Neurofibromas, CutaneousUnited States
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Marco CapogrossoRoche-GenentechNot yet recruitingSpinal Muscular Atrophy | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy 4United States
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ARTHEx Biotech S.L.Not yet recruitingMyotonic Dystrophy 1
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John ElfarNot yet recruitingCarpal Tunnel Syndrome | Compression Neuropathy
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IRCCS Fondazione Stella MarisRecruitingFragile X SyndromeItaly
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Steen Hvitfeldt PoulsenNovo Nordisk A/SRecruitingQuality of Life | Transthyretin Amyloidosis | Transthyretin Amyloid Cardiomyopathy | Wild-Type Transthyretin-Related (ATTR)AmyloidosisDenmark
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Specila hospital for cerebral palsy and developmental...FRAXA Research FoundationRecruitingFragile X SyndromeSerbia
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Karolinska InstitutetRecruitingTourette Syndrome | Chronic Tic DisorderSweden
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Université de SherbrookeCanadian Institutes of Health Research (CIHR); Centre de recherche du Centre... and other collaboratorsNot yet recruiting
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Central Hospital, Nancy, FranceRecruiting
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Université du Québec à ChicoutimiMcGill University; Université de Sherbrooke; University of Alberta; University... and other collaboratorsRecruitingAutosomal Recessive Spastic Ataxia of Charlevoix-Saguenay | Spastic Paraplegia 7Canada
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Université de SherbrookeCanadian Institutes of Health Research (CIHR); Centre de recherche du Centre... and other collaboratorsNot yet recruitingFragile X Syndrome
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Massachusetts General HospitalPatient-Centered Outcomes Research InstituteNot yet recruitingNeurofibromatosis 1United States
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PTC TherapeuticsRecruitingHuntington DiseaseAustralia, France, Germany, Netherlands, United Kingdom, Spain, Austria, Canada, Italy, New Zealand
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingAutism Spectrum Disorder | Autistic Disorder | Fragile X Syndrome | Asperger SyndromeUnited States
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingCerebral Adrenoleukodystrophy (CALD)United States
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National Cancer Institute (NCI)Not yet recruitingNeurofibromatosis 1 | Nerve Sheath NeoplasmsUnited States
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Samsung Medical CenterNot yet recruitingCharcot-Marie-Tooth Disease, Type 1