Search clinical trials for: LGMD2E

Total 7 results

Sarepta Therapeutics, Inc.

Recruiting

A Trial to Learn More About an Experimental Gene Therapy Called Bidridistrogene Xeboparvovec (SRP-9003) as a Possible Treatment for Limb Girdle Muscular Dystrophy 2E/R4 (EMERGENE)

Limb-girdle Muscular Dystrophy

United States
Sarepta Therapeutics, Inc.

Recruiting

A Study of the Natural History of Participants With LGMD2E/R4, LGMD2D/R3, LGMD2C/R5, and LGMD2A/R1 ≥ 4 Years of Age, Who Are Managed in Routine Clinical Practice

Limb-girdle Muscular Dystrophy

United States, Brazil, Belgium, Canada, Germany, Italy, Spain, Sweden, Turkey, United Kingdom
Nationwide Children's Hospital
Myonexus Therapeutics

Recruiting

Limb Girdle Muscular Dystrophy Type 2E Recruitment Study

Limb-Girdle Muscular Dystrophy, Type 2E

United States
Sarepta Therapeutics, Inc.

Active, not recruiting

Gene Delivery Clinical Trial of SRP-9003 (Bidridistrogene Xeboparvovec) for Participants With Limb-Girdle Muscular Dystrophy, Type 2E (LGMD2E) (Beta-Sarcoglycan Deficiency)

Limb-Girdle Muscular Dystrophy, Type 2E

United States
Virginia Commonwealth University
Muscular Dystrophy Association

Active, not recruiting

Long-Term Development of Muscular Dystrophy Outcome Assessments (GRASP-01-005)

LGMD2E | LGMD2I | LGMD2A | LGMD2B | LGMD2C | LGMD1B | LGMD1C | LGMD1D | LGMD1E | LGMD1F | LGMD1G | LGMD1H | LGMD2D | LGMD2F | LGMD2G | LGMD2J | LGMD2K | LGMD2L | LGMD2M | LGMD2N | LGMD2O | LGMD2P | LGMD2Q | LGMD2S | LGMD2T | LGMD2U | LGMD2W | LGMD2X | LGMD2Y

United States
Sarepta Therapeutics, Inc.

Active, not recruiting

A Gene Transfer Single Dose Study to Evaluate the Safety, Tolerability and Efficacy of SRP-9003 in Non-Ambulatory and Ambulatory Participants With Limb Girdle Muscular Dystrophy, Type 2E/R4 (Beta-Sarcoglycan [β-SG] Deficiency)

Limb Girdle Muscular Dystrophy

United States
Fondazione IRCCS Ca' Granda, Ospedale Maggiore...

Completed

Clinical Determinants of Disease Progression in Patients With Limb Girdle Muscular Distrophy Type 2E (NeuroLGMD2E)

LGMD2E

Italy

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