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Search clinical trials for: Liver gene transfer
Total 273418 results
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St. Jude Children's Research HospitalNot yet recruiting
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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Vastra Gotaland RegionMiltenyi Biomedicine GmbHRecruitingMetastatic Cutaneous Melanoma | Metastatic Uveal MelanomaSweden
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Rennes University HospitalRecruiting
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Nanjing Medical UniversityNot yet recruiting
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Vertos Medical, Inc.RecruitingLumbar Spinal StenosisUnited States
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Galaxy Pharma (Pvt) LimitedOva IVF & Reproductive Health Clinics, KarachiRecruitingSecondary Infertility | Primary Infertility | Low Responders | Mild to Moderate Male Factor InfertilityPakistan
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National Cancer Institute (NCI)RecruitingBreast Cancer | Lung Cancer | Prostate Cancer | Colon Cancer | Liver CancerUnited States
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Ultragenyx Pharmaceutical IncActive, not recruitingWilson DiseaseUnited States, Canada, Spain, Portugal, United Kingdom
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Human Development Research Foundation, PakistanUniversity of Liverpool; Shifa Tameer-e-Millat UniversityActive, not recruitingDepression, Postpartum | Perinatal DepressionPakistan
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Martin JaničkoF.D. Roosevelt Teaching Hospital with Policlinic Banska BystricaWithdrawnLiver Failure | CirrhosisSlovakia
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Adverum Biotechnologies, Inc.CompletedAlpha 1-Antitrypsin DeficiencyUnited States
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Daniel BenjaminEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedHeart Failure | Epilepsy | Pain | Pneumonia | Sepsis | Inflammation | Hypertension | Chronic Kidney Diseases | Hemophilia | Schizophrenia | Central Nervous System Infections | Nosocomial Pneumonia | Insomnia | Anxiety | Bipolar Disorder | Neutropenia | Staphylococcal Infections | Bradycardia | Seizures | Urinary Tract Infections | Pulmonary... and other conditionsUnited States, Canada, United Kingdom, Israel, Singapore
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City of Hope Medical CenterNational Cancer Institute (NCI)TerminatedSarcoma | Lymphoma | Kidney Cancer | Unspecified Childhood Solid Tumor, Protocol Specific | Testicular Germ Cell Tumor | Ovarian Cancer | Brain and Central Nervous System Tumors | Neuroblastoma | Liver Cancer | Extragonadal Germ Cell Tumor | Childhood Germ Cell TumorUnited States
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University of Campania "Luigi Vanvitelli"Completed
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Eiger BioPharmaceuticalsAnkara UniversityCompletedChronic Hepatitis D InfectionTurkey
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Adverum Biotechnologies, Inc.Completed
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Liverpool School of Tropical MedicineCenters for Disease Control and Prevention; Kenya Medical Research Institute; Safe Water and AIDS Project (SWAP), KenyaCompletedHIV Infections | Quality of Life | Adolescent Behavior | Reproductive Health | Herpesvirus Infection | Woman AbuseKenya
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Osijek University HospitalJosip Juraj Strossmayer University of OsijekCompletedRespiratory Failure | Renal Failure | Abdominal Surgery | Liver Dysfunction | Multiorgan FailureCroatia
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Liverpool School of Tropical MedicineLondon School of Hygiene and Tropical Medicine; University of Bergen; Kamuzu... and other collaboratorsCompletedMalaria in Pregnancy | Adherence, TreatmentKenya
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University of Massachusetts, WorcesterNational Heart, Lung, and Blood Institute (NHLBI); University of Florida; National... and other collaboratorsCompletedAlpha 1-Antitrypsin DeficiencyUnited States
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GiveWellNew Incentives; All Babies are Equal InitiativeCompletedHepatitis B | Measles | Pertussis | Tetanus | Diphtheria | Tuberculosis | Pneumonia, Bacterial | Yellow Fever | Polio | Rotavirus Infections | Haemophilus Influenzae Type b InfectionNigeria
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Aga Khan UniversityUnknownHyperglycemia | Anemia | Dyslipidemias | Oxidative Stress | Liver Dysfunction | Hemoglobin SCPakistan
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Applied Genetic Technologies CorpNational Heart, Lung, and Blood Institute (NHLBI)CompletedAlpha-1 Antitrypsin DeficiencyUnited States, Ireland
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Astellas Pharma IncCompletedor Peripheral Nerve Injury (PNI) | Peripheral Neuropathic Pain (PNP) Due to Postherpetic Neuralgia (PHN)Belgium, Czechia, Denmark, Ireland, Norway, Slovakia, United Kingdom
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Assiut UniversityUnknownLiver Cirrhosis | Iron Deficiency, Anaemia in Children
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Southwest Hospital, ChinaUnknownHepatocellular CarcinomaChina
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Jinan University GuangzhouGuagnzhou Qiaokang HospitalUnknownAdoptive Treatment for Hepatitis B With γδT CellsChina
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University of Massachusetts, WorcesterNational Heart, Lung, and Blood Institute (NHLBI); University of Florida; National... and other collaboratorsCompletedAlpha 1-Antitrypsin DeficiencyUnited States
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Kamada, Ltd.CompletedType 1 Diabetes MellitusIsrael
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Institut National de la Santé Et de la Recherche...Assistance Publique - Hôpitaux de Paris; Cardiff University; Karolinska Institutet and other collaboratorsWithdrawnBronchopulmonary DysplasiaBelgium, France, Germany, Hungary, Italy, Luxembourg, Netherlands, Sweden, United Kingdom
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Shineway Pharmaceutical Co.,LtdUnknownHBeAg Positive Chronic Hepatitis B
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Digna Biotech S.L.University of Navarra; Porphyria Centre Sweden; UniQure N.V.; Nationales Centrum...CompletedAcute Intermittent PorphyriaSpain
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US Department of Veterans AffairsCompletedAlcohol Dependence | Chronic Hepatitis CUnited States
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University of Southern CaliforniaWithdrawn
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Children's Cancer and Leukaemia GroupUnknownBrain and Central Nervous System TumorsUnited Kingdom, Ireland
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Janssen Infectious Diseases BVBAVertex Pharmaceuticals IncorporatedCompletedHepatitis C, ChronicUnited States, Australia, United Kingdom, Germany, France, Spain, Belgium, Netherlands, Canada, Brazil, Puerto Rico, Poland, Sweden, Switzerland, Israel
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BiogenCompletedColorectal Carcinoma | MetastasesUnited States
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Assiut UniversityNot yet recruitingLiver Toxicity, Chemically-Induced
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Eli Lilly and CompanyNot yet recruitingOverweight and ObesityUnited States, Canada, Australia, Germany, Mexico, Argentina, Brazil, Hungary, Austria, India, Poland, Slovakia, Spain, Netherlands, Turkey, Czechia, United Kingdom, Denmark, Puerto Rico, France, Israel
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IpsenNot yet recruiting
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Milton S. Hershey Medical CenterNot yet recruitingMelanoma | Breast Cancer | Head and Neck Cancer | Gastric Cancer | Colorectal Cancer | Pancreatic Cancer | Lung Cancer | Liver Cancer | Genito-Urinary CancerUnited States
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Assembly BiosciencesNot yet recruiting
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Taipei Veterans General Hospital, TaiwanRecruitingCarcinoma, HepatocellularTaiwan
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Medical University of WarsawRecruiting
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University Health Network, TorontoGlaxoSmithKlineNot yet recruitingAutoimmune Hepatitis
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City of Hope Medical CenterRecruitingCholangiocarcinoma | Cholangiocarcinoma, Intrahepatic | Cholangiocarcinoma Resectable | Cholangiocarcinoma; LiverUnited States, Japan
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Resolution Therapeutics LimitedRecruiting