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Search clinical trials for: Mitochondrial Neurogastrointestinal Encephalopathy (MNGIE)
Total 1306 results
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Michio Hirano, MDNational Institute of Neurological Disorders and Stroke (NINDS); Cornell UniversityWithdrawnMitochondrial Neurogastrointestinal Encephalomyopathy (MNGIE)
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Entrada Therapeutics, Inc.SuspendedMitochondrial Neurogastrointestinal EncephalomyopathyUnited States, Turkey
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Hospital Universitari Vall d'Hebron Research InstituteRecruitingMNGIE | DysmotilitySpain
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Columbia UniversityNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMitochondrial NeuroGastroIntestinal Encephalopathy (MNGIE)United States
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Masonic Cancer Center, University of MinnesotaRecruitingHurler Syndrome | Sphingolipidoses | Peroxisomal Disorders | Metachromatic Leukodystrophy | Alpha-Mannosidosis | Hunter Syndrome | Mucopolysaccharidosis Disorders | Maroteaux Lamy Syndrome | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Glycoprotein Metabolic Disorders | Recessive Leukodystrophies | Globoid... and other conditionsUnited States
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Columbia UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationMitochondrial Disease | Mitochondrial Disorders | Melas | Kearns Sayer | NARP | MNGIE | LHON | Mitochondrial Depletion Syndrome | Leigh's DiseaseUnited States
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Horizon Pharma USA, Inc.Terminated
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Columbia UniversityNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMitochondrial Diseases | Mitochondrial Disorders | Mitochondrial Genetic Disorders | Disorder of Mitochondrial Respiratory Chain Complexes | Deletion and Duplication of Mitochondrial DNAUnited States, Canada
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LMU KlinikumUniversity of Pisa; German Federal Ministry of Education and Research; European...RecruitingMitochondrial Diseases | MDS | Mitochondrial Myopathies | MELAS Syndrome | MIDD | Kearns-Sayre Syndrome | MERRF Syndrome | Barth Syndrome | Leigh Syndrome | MNGIE | LHON | Pearson Syndrome | NARP Syndrome | Coenzyme Q10 Deficiency | SANDO | SCAE | MIRAS | CPEOAustria, Germany, Italy
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Horizon Pharma USA, Inc.CompletedInherited Mitochondrial Disease, Including Leigh SyndromeUnited States
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Omeicos Therapeutics GmbHRecruitingPrimary Mitochondrial DiseaseGermany, Italy
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University of California, San DiegoNew York University; Heinrich-Heine University, Duesseldorf; Universität TübingenRecruitingGenetic Disease | Mitochondrial Encephalomyopathies | Neonatal Encephalopathy | Mutation | Hereditary Spastic Paraplegia | White Matter Disease | Spastic ParaplegiaUnited States
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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McGill University Health Centre/Research Institute...RecruitingMitochondrial Diseases | Mitochondrial Encephalomyopathy | Mitochondrial Encephalopathy | Mitochondrial DNA Depletion | Mitochondrial Metabolism DisordersCanada
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The University of Texas Health Science Center,...RecruitingLeigh Disease | Leigh Syndrome | Leigh's Necrotizing Encephalopathy | Subacute Necrotizing Encephalomyopathy | Subacute Necrotizing EncephalomyelopathyUnited States
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National Human Genome Research Institute (NHGRI)RecruitingMitochondrial Disorders | Leigh Disease | Oxidative Phosphorylation Deficiencies | Electron Transport Chain Disorders, MitochondrialUnited States
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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PTC TherapeuticsCompletedMitochondrial Diseases | Drug Resistant Epilepsy | Leigh Disease | Leigh Syndrome | Mitochondrial Encephalopathy (MELAS) | Pontocerebellar Hypoplasia Type 6 (PCH6) | Alpers Disease | Alpers SyndromeUnited States, Spain, United Kingdom, Canada, France, Italy, Poland, Sweden, Japan
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St George's, University of LondonNeovii BiotechWithdrawnMitochondrial Diseases | Inborn Errors of Metabolism | Metabolic Disease
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Jesús González de la Aleja TejeraCompleted
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Michio HiranoSanthera PharmaceuticalsCompletedMELAS SyndromeUnited States
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Columbia UniversityWithdrawnChronic Fatigue SyndromeUnited States
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Ivan de Kouchkovsky, MDNot yet recruitingProstate Cancer | High Risk Prostate CarcinomaUnited States
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Resolution Therapeutics LimitedRecruiting
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Imagine InstituteNot yet recruitingDevelopmental and Epileptic Encephalopathy
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University of ExeterInnovate UK; Mitocholine LtdRecruitingCognitive Function | Exercise PerformanceUnited Kingdom
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Nanfang Hospital, Southern Medical UniversityRecruitingDecompensated Cirrhosis | Overt Hepatic Encephalopathy | CMV ReactivationChina
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University of BolognaNot yet recruiting
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CoMind Technologies LimitedLindus HealthNot yet recruitingStroke | Encephalitis | Traumatic Brain Injury | Intracerebral Hemorrhage | Hydrocephalus | Encephalopathy | Intracranial Pressure | Autoregulation | Intracranial Pressure Changes
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingHepatic Encephalopathy | DysbiosisItaly
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Fundación Iniciativa para las Neurociencias (FINCE)Not yet recruitingSTXBP1 Encephalopathy With EpilepsySpain
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Jirair Krikor BedoyanUltragenyx Pharmaceutical IncRecruitingPyruvate Dehydrogenase Complex DeficiencyUnited States
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Kaohsiung Veterans General Hospital.Recruiting
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Texas Tech UniversityNot yet recruiting
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Sir Ganga Ram HospitalRecruiting
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The University of QueenslandNot yet recruitingAtaxia TelangiectasiaAustralia
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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University Gustave EiffelHospices Civils de LyonRecruitingNeurocognitive DisordersFrance
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Niguarda HospitalIstituto di Fisiologia Clinica CNRRecruitingCoronary Artery DiseaseItaly
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First Affiliated Hospital Xi'an Jiaotong UniversityXi'an TCM Hospital of EncephalopathyRecruitingAutism Spectrum DisorderChina
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University College, LondonMoorfields Eye Hospital NHS Foundation TrustRecruiting
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Number 2 Children's Hospital, Ho Chi Minh CityRecruitingChild Development | Epilepsy; Seizure | Gene Abnormality | Early Onset DisorderVietnam
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Bispebjerg HospitalNot yet recruitingInflammation | Muscle Strain, Multiple Sites
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Assistance Publique - Hôpitaux de ParisNot yet recruitingCerebral Palsy | Encephalopathy | Traumatic Head Injury | Cerebral MalformationFrance
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National Institute on Aging (NIA)RecruitingHealthy VolunteersUnited States
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University of East AngliaThe Norfolk and Norwich University Hospitals NHS Foundation Trust; The Quadram...Not yet recruiting
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Changping LaboratoryFujian Maternity and Child Health Hospital; Jining Medical University; Xi'an... and other collaboratorsNot yet recruitingAutism Spectrum Disorder
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CereMark Pharma, LLCNot yet recruitingAlzheimer Disease | Chronic Traumatic Encephalopathy
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University Hospital, GrenobleRecruitingHepatic EncephalopathyFrance
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Assistance Publique - Hôpitaux de ParisRecruiting