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- US Clinical Trials Registry
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Search clinical trials for: Mutant TTR
Total 725 results
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Brigham and Women's HospitalUnknown
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Boston UniversityCorino Therapeutics, Inc.CompletedTransthyretin Amyloidosis | Amyloidosis, Leptomeningeal, Transthyretin-RelatedUnited States
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Sun Yat-sen UniversityRecruiting
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Shanghai Pharmaceuticals Holding Co., LtdNot yet recruitingBiliary Tract or Colorectal Cancer With Her2-positive/MutatedChina
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Daping Hospital and the Research Institute of Surgery...Not yet recruitingNon Small Cell Lung Cancer | Non Small Cell Lung Cancer Stage IIIB | EGFR Gene Mutation | Non-small Cell Lung Cancer Stage IV
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Suzhou Genhouse Bio Co., Ltd.Zhejiang Cancer HospitalNot yet recruitingKRAS G12C Mutant Solid Tumors
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University Hospital, BrestNot yet recruiting
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RenJi HospitalNot yet recruitingSystemic Lupus Erythematosus
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Jiangsu HengRui Medicine Co., Ltd.Not yet recruitingAdvanced KRAS G12D Mutant Solid TumorsChina
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Zhejiang Cancer HospitalRecruitingHER2 Gene Mutation | Bile Duct Adenocarcinoma Non-ResectableChina
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Huashan HospitalNot yet recruiting
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Tianjin Medical University Cancer Institute and...RecruitingNon-small Cell Lung Cancer | EGFR Activating Mutation | EGFR-TKI Resistant Mutation | Cell Cycle DeregulationChina
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Alnylam PharmaceuticalsRecruitingHereditary Amyloidosis, Transthyretin-Related | Asymptomatic Carrier StateFrance
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Neonc Technologies, Inc.Not yet recruitingHigh Grade Glioma | Pineocytoma | Diffuse Midline Glioma, H3 K27M-Mutant | Spinal Cord Tumor | Pediatric Tumor of CNS | Pediatric Tumor of Brain | Pediatric Tumor of Brain Stem | Choroid Plexus Carcinoma, Childhood
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Hunan Province Tumor HospitalNot yet recruitingNon-small Cell Lung CancerChina
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Erasca, Inc.RecruitingAdvanced or Metastatic NRAS-mutant MelanomaUnited States
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Merck Sharp & Dohme LLCRecruiting
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Jonsson Comprehensive Cancer CenterNot yet recruitingDiffuse Hemispheric Glioma, H3 G34-MutantUnited States
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University of Southern CaliforniaNational Cancer Institute (NCI)Not yet recruitingMetastatic Colorectal Adenocarcinoma | Stage IV Colorectal Cancer AJCC v8United States
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Henan Cancer HospitalRecruitingNon-Squamous Non-Small Cell Lung CancerChina
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Fudan UniversityNot yet recruitingLung Cancer | Minimal Residual Disease | EGFR Gene Mutation
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Restor3DNot yet recruitingAvascular Necrosis of the Talus | Talar Osteochondral Defect of Ankle | Talar Dysfunction
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Suzhou Genhouse Bio Co., Ltd.Shanghai East Hospital; Shandong Tumor HospitalRecruitingAdvanced Solid Tumors With MAPK Signal Pathway MutantChina
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OX2 TherapeuticsRecruitingDiffuse Midline Glioma, H3 K27M-Mutant | Recurrent High Grade GliomaUnited States
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Guangdong Provincial People's HospitalRecruitingNon Small Cell Lung Cancer | EGFR Gene MutationChina
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M.D. Anderson Cancer CenterNot yet recruitingMyeloproliferative Neoplasm | Myelodysplastic Neoplasm | Pathway Mutant Myelodysplastic SyndromesUnited States
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Shandong UniversityNot yet recruiting
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University of FloridaOligo Nation, IncNot yet recruitingRecurrent Oligodendroglioma | Progressive OligodendrogliomaUnited States
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Yonsei UniversityNot yet recruitingNon Small Cell Lung CancerKorea, Republic of
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Suzhou Zelgen Biopharmaceuticals Co.,LtdRecruitingKRAS G12C Mutant Advanced Solid TumorsChina
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Sun Yat-sen UniversityNot yet recruiting
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Immuneering CorporationRecruitingPancreas Adenocarcinoma | Non-small Cell Lung Cancer | Advanced Solid Tumor (Phase 1) | Malignant Melanoma (Cutaneous)United States
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MapKure, LLCRecruitingColorectal Cancer | Pancreatic Ductal Cancer | Advanced or Metastatic RAS Mutant Colorectal and Pancreatic Ductal CancersUnited States
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Therapex Co., LtdNot yet recruitingCarcinoma, Non-Small-Cell Lung | EGFR Mutant Advanced Non-Small Cell Lung Cancer
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Alexion Pharmaceuticals, Inc.RecruitingTransthyretin Amyloid CardiomyopathyUnited States, Spain, United Kingdom, Norway, Israel, Korea, Republic of, Belgium, France, Germany, Italy, Japan, China, Australia, Argentina, Austria, Taiwan, Switzerland, Canada, Sweden, Poland, Denmark, Turkey, Brazil, Netherlands, G... and more
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InxMed (Shanghai) Co., Ltd.InventisBio Co., LtdRecruiting
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Terns, Inc.Not yet recruitingChronic Myeloid Leukemia | Chronic Myeloid Leukemia, Chronic PhaseUnited States
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Rigel PharmaceuticalsNationwide Children's HospitalNot yet recruitingAstrocytoma | High Grade Glioma | Oligodendroglioma | Diffuse Intrinsic Pontine Glioma | Diffuse Midline Glioma, H3 K27M-Mutant | WHO Grade III Glioma | Metastatic Brain Tumor | Spinal Tumor | Astrocytoma, Grade III | Astrocytoma, Grade IV | IDH1 Mutation | WHO Grade IV Glioma | Thalamus Tumor | IDH1 R132 | IDH1 R132C | IDH1 R132H and other conditionsUnited States, Australia, United Kingdom, Canada, Germany, Netherlands
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Intellia TherapeuticsRegeneron PharmaceuticalsRecruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Australia, United Kingdom, New Zealand, Canada
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Revolution Medicines, Inc.RecruitingColorectal Cancer | Pancreatic Ductal Adenocarcinoma | Non-Small Cell Lung Cancer (NSCLC)United States, Puerto Rico
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Jasper GerritsenMassachusetts General Hospital; Universitaire Ziekenhuizen KU Leuven; University... and other collaboratorsRecruitingGlioblastoma | Brain Neoplasms | Astrocytoma, Grade III | High-grade Glioma | Astrocytoma, Grade IV | Glioblastoma, IDH-mutant | Glioblastoma, IDH-wildtype | Glioblastoma Multiforme, Adult | Brain Neoplasm, Primary | Brain Neoplasm, Malignant | Astrocytoma, Malignant | Brain Neoplasms, AdultUnited States, Germany, Belgium, Switzerland, Netherlands
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Samsung Medical CenterNot yet recruitingNon-Small Cell Lung Cancer MetastaticKorea, Republic of
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Rigshospitalet, DenmarkKarolinska University Hospital; Aarhus University Hospital; Sahlgrenska University... and other collaboratorsNot yet recruitingDiffuse Intrinsic Pontine Glioma | Diffuse Midline Glioma, H3 K27M-Mutant | Diffuse Glioma | Pontine Tumors | Brain Tumor, Pediatric | Thalamic Tumor
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Jonathan RiessNational Cancer Institute (NCI)Not yet recruitingMetastatic Lung Non-Small Cell Carcinoma | Stage IV Lung Cancer AJCC v8 | Recurrent Lung Non-Small Cell CarcinomaUnited States
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Neonc Technologies, Inc.RecruitingMelanoma | Renal Cell Carcinoma | Cervical Cancer | Small Cell Lung Cancer | Gastric Cancer | Colorectal Cancer | Esophageal Cancer | Non-small Cell Lung Cancer | Head and Neck Squamous Cell Carcinoma | Esophageal Squamous Cell Carcinoma | Urothelial Carcinoma | Merkel Cell Carcinoma | Gastroesophageal Junction... and other conditionsUnited States
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Revolution Medicines, Inc.RecruitingAdvanced Solid Tumors | Non-small Cell Lung Cancer (NSCLC) | Pancreatic Ductal Adenocarcinoma (PDAC) | Colorectal Cancer (CRC)United States
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Yonsei UniversityNot yet recruitingNon Small Cell Lung CancerKorea, Republic of
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Shanghai Kechow Pharma, Inc.Not yet recruitingColorectal Cancer Metastatic
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Shanghai Kechow Pharma, Inc.Not yet recruiting
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Kura Oncology, Inc.RecruitingNeoplasms by Histologic Type | Acute Myeloid Leukemia | Leukemia | Leukemia, Myeloid | Leukemia, Myeloid, Acute | AML | Acute Leukemia | Hematologic Malignancy | NPM1 Mutation | AML With Mutated NPM1 | KMT2Ar | MLL RearrangementUnited States