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Search clinical trials for: Niemann-Pick B patients
Total 487564 results
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SanofiPulse Infoframe Ltd.RecruitingNiemann-Pick Diseases | Acid Sphingomyelinase DeficiencyUnited States
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Fundación Española de Hematología y HemoterapíaRecruitingGaucher Disease | Acid SphingoMyelinase DeficiencySpain
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Cyclo Therapeutics, Inc.RecruitingNiemann-Pick Disease, Type C1United States, Spain, Israel, Taiwan, Brazil, Germany, Australia, Poland, Turkey, Italy, United Kingdom
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SanofiRecruitingAcid SphingoMyelinase Deficiency | Gaucher Disease, SplenomegalyFrance
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Azafaros A.G.Active, not recruitingNiemann-Pick Disease, Type C | GM2 GangliosidosisBrazil
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisUnited States, Argentina, Australia, Belgium, Brazil, Bulgaria, Chile, France, Germany, Italy, Japan, Netherlands, Portugal, Spain, Tunisia, Turkey, United Kingdom
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ZevraDenmarkAvailableNiemann-Pick Disease, Type CUnited States
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisUnited States, Belgium, Brazil, France, Germany, Italy, United Kingdom
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SanofiCompletedSphingomyelin LipidosisItaly, Czechia, Belgium, France, Portugal, Turkey, United States, Argentina, Brazil, Chile, Germany, Romania, Spain
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SanofiApproved for marketing
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ActelionCompleted
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisBrazil, France, Italy, United States, Germany, United Kingdom
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Cyclo Therapeutics, Inc.CompletedNiemann-Pick Disease, Type C1Israel, Sweden, United Kingdom
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Masonic Cancer Center, University of MinnesotaTerminatedSphingolipidoses | Niemann-Pick Disease, Type C | Krabbe Disease | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Hurler's Syndrome | Maroteaux-Lamy Syndrome | Wolman's Disease | Niemann-Pick Disease Type BUnited States
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National Eye Institute (NEI)CompletedNiemann Pick DiseasesUnited States, United Kingdom
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KemPharm Denmark A/SCompletedNiemann-Pick Disease, Type CSpain, France, United Kingdom, Switzerland, Denmark, Poland, Italy, Germany
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University Hospital, GrenobleTerminatedPsychiatric Adults PatientsFrance
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Genzyme, a Sanofi CompanyCompletedHuman Acid Sphingomyelinase DeficiencyUnited Kingdom, United States
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AldagenTerminatedMucopolysaccharidosis | Inborn Errors of Metabolism | Lysosomal Storage Disorders | Inherited Metabolic Diseases | Peroxisomal Storage DiseasesUnited States
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National Taiwan University HospitalCompleted
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Fairview University Medical CenterUnknownMucopolysaccharidosis I | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Metachromatic Leukodystrophy | Pulmonary Complications | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Mannosidosis | I Cell DiseaseUnited States
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Hacettepe UniversityRecruitingIdiopathic Parkinson DiseaseTurkey
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Universitat Politècnica de CatalunyaInstitut Català de la Salut; Consorci Hospitalari de Vic; EAP Vic (CAP Remei); Associació...RecruitingStroke | Physical Disability | Motor DisordersSpain
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West China HospitalRecruiting
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Sunshine Guojian Pharmaceutical (Shanghai) Co.,...RecruitingLocally Advanced, Recurrent or Metastatic MalignanciesChina
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DiaSorin Molecular LLCNot yet recruitingCoronavirus Disease 2019 | Influenza A | Respiratory Syncytial Virus (RSV) | Adenovirus | Influenza Type B | Enterovirus | Mycoplasma Pneumonia | Bordetella Parapertussis Infection | Chlamydia Pneumonia | Para Influenza | Bordetella Pertussis Infection, RespiratoryAustralia
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Ankara Yildirim Beyazıt UniversityNot yet recruitingParkinson's Disease | Freezing of GaitTurkey
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Cairo UniversityRecruitingMandibular FracturesEgypt
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Xiaojun ChenRecruitingObesity | Atypical Endometrial Hyperplasia | Progesterone ResistanceChina
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Ohio State University Comprehensive Cancer CenterNot yet recruitingMetastatic Renal Cell Carcinoma | Metastatic Cutaneous Melanoma | Stage IV Renal Cell Cancer AJCC v8 | Clinical Stage IV Cutaneous Melanoma AJCC v8United States
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Peking University People's HospitalNot yet recruitingChronic Myeloid LeukemiaChina
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University of Wisconsin, MadisonNot yet recruitingXerostomia | Graft-versus-host-disease | Sjogren's DiseaseUnited States
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Assiut UniversityNot yet recruiting
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GenVivo, Inc.Recruiting
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National Taiwan University HospitalNot yet recruitingStroke | Focused UltrasoundTaiwan
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Affiliated Hospital of Nantong UniversityRecruitingIschemic Stroke | Frailty | Exercise TherapyChina
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Affiliated Hospital of Nantong UniversityNot yet recruiting
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PHARMENTERPRISES LLCNot yet recruitingStudy to Evaluate the Efficacy and Safety of XC243 in Patients With Exacerbation of Chronic CystitisCystitisRussian Federation
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Kırklareli UniversityNot yet recruitingHemodialysis
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Alto NeuroscienceRecruitingAnhedonia | Major Depressive DisorderUnited States
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University of AarhusAarhus University Hospital; Vejle Hospital; Regionshospitalet Silkeborg; Physiotherapy...Not yet recruiting
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Lebanese UniversityRecruitingQuality of Life | Inflammatory Bowel Diseases | Crohn Disease | Ulcerative Colitis | Food Intolerance | Flare UpLebanon
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Fudan UniversityShanghai Zhongshan Hospital; RenJi Hospital; First Hospital of China Medical... and other collaboratorsNot yet recruitingRectal Cancer | RECTAL NEOPLASMS
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Hannover Medical SchoolBoehringer IngelheimNot yet recruitingAutosomal Dominant Polycystic Kidney
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Fundación Pública Andaluza para la Investigación...Recruiting
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Ulrich RotherRecruitingPeripheral Arterial Disease | Peripheral Vascular Diseases | Intermittent Claudication | Gluteal ClaudicationGermany
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Azienda Socio Sanitaria Territoriale degli Spedali...RecruitingAcute Lymphoblastic LeukemiaItaly
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Assistance Publique - Hôpitaux de ParisNot yet recruitingLimb Girdle Muscular Dystrophy
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Ioannis A. MalogiannisNational and Kapodistrian University of Athens; Attikon Hospital; University... and other collaboratorsRecruitingOther Mental ConditionsGreece
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Robert Bok, MD, PhDNational Cancer Institute (NCI)Not yet recruitingProstate CancerUnited States