- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: SMA - Spinal Muscular Atrophy
Total 38471 results
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Hospital Clinic of BarcelonaUnknownObesity | Gastrectomy | Gastric BypassSpain
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McGill University Health Centre/Research Institute...Not yet recruiting
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Wiktor Dega University Orthopedic and Rehabilitation...Recruiting
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Hospices Civils de LyonNot yet recruitingSpinal Muscular AtrophyFrance
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IRCCS Burlo GarofoloRecruiting
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Marco CapogrossoRoche-GenentechNot yet recruitingSpinal Muscular Atrophy | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy 4United States
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Bar-Chama, Natan, M.D.RecruitingFertility IssuesUnited States
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Kun SunRecruitingSpinal Muscular Atrophy 1China
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Robert Jones and Agnes Hunt Orthopaedic and District...University Hospital Birmingham NHS Foundation TrustRecruitingSpinal Muscular AtrophyUnited Kingdom
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GeneCradle IncRecruiting
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Fondazione Policlinico Universitario Agostino Gemelli...IRCCS Eugenio Medea; Azienda Ospedaliera Universitaria Policlinico "G. Martino... and other collaboratorsNot yet recruitingSpinal Muscular Atrophy
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Institut de Myologie, FranceRoche Pharma AGNot yet recruitingMuscular Atrophy, Spinal, Type II | Muscular Atrophy, Spinal, Type IIIFrance
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GeneCradle IncRecruitingSpinal Muscular AtrophyChina
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NMD Pharma A/SRecruitingSpinal Muscular AtrophyUnited States, Spain, Belgium, Denmark, Germany, Netherlands, Italy, Canada
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BiogenRecruitingMuscular Atrophy, SpinalUnited States
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Fondazione Policlinico Universitario Agostino Gemelli...University of Milan; Ospedale Pediatrico Bambino GesùRecruiting
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Fondazione Policlinico Universitario Agostino Gemelli...Recruiting
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Fondazione Policlinico Universitario Agostino Gemelli...Bambino Gesù Hospital and Research Institute; University of Messina; University... and other collaboratorsRecruitingSpinal Muscular AtrophyItaly
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Fondazione Policlinico Universitario Agostino Gemelli...University of Messina; Istituto Giannina Gaslini; University of Milan; Ospedale...Recruiting
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BiocadRecruitingSpinal Muscular Atrophy (SMA)Belarus, Russian Federation
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University Hospital, Strasbourg, FranceRecruitingFeasibility of Neonatal Screening for Spinal AmyotrophyFrance
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Holland Bloorview Kids Rehabilitation HospitalRecruiting
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Hangzhou Jiayin Biotech LtdRecruitingSpinal Muscular Atrophy Type IChina
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University of Castilla-La ManchaRecruiting
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Columbia UniversityGenentech, Inc.RecruitingSpinal Muscular AtrophyUnited States
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University of OxfordHoffmann-La Roche; Oxford University Hospitals NHS Trust; Novartis Gene TherapiesRecruiting
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Hospices Civils de LyonRecruitingSpinal Muscular AtrophyFrance
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BiogenRecruitingSpinal Muscular Atrophy (SMA)France
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Charles University, Czech RepublicRecruiting
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Novartis PharmaceuticalsRecruitingSpinal Muscular Atrophy (SMA)Spain, Canada, Taiwan, Belgium, Japan, Italy, Singapore, United Kingdom, France, Australia, Denmark, United States
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Genentech, Inc.RecruitingSpinal Muscular AtrophyUnited States, Puerto Rico
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Bakri ElsheikhGenentech, Inc.RecruitingSpinal Muscular AtrophyUnited States
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Hoffmann-La RocheRecruitingSpinal Muscular Atrophy (SMA)Belgium, United States, Croatia, Japan, Netherlands, Spain, Canada, Poland, United Kingdom, Italy, Portugal, Australia
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Bahçeşehir UniversityNot yet recruitingDuchenne Muscular Dystrophy | Spinal Muscular Atrophy | Healthy Individuals
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BiogenRecruiting
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University of GiessenRecruitingSpinal Muscular AtrophyGermany
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CHU de ReimsRecruitingSpinal Muscular AtrophyFrance
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Newcastle UniversityRoche Pharma AG; Biogen; Adult SMA REACH; SMA REACH UKRecruiting
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Assistance Publique - Hôpitaux de ParisRecruiting
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AveXis, Inc.United BioSource, LLCRecruitingSpinal Muscular Atrophy (SMA)Japan, United States, Korea, Republic of, Israel, Greece, Ireland, Portugal, Russian Federation, Taiwan
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Great Ormond Street Hospital for Children NHS Foundation...RecruitingSpinal Muscular AtrophyUnited Kingdom
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Kaohsiung Medical University Chung-Ho Memorial...The Chinese Foundation of Health; Taipei Institute of PathologyRecruiting
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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Hoffmann-La RocheCompletedMuscular Atrophy, SpinalBelgium, United States, China, Spain, Japan, Canada, France, Poland, Brazil, Croatia, Italy, Russian Federation, Turkey, Germany, Serbia, United Kingdom
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Synchron Medical, Inc.Active, not recruitingParalysis | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Spinal Cord Injuries | Neurologic Disorder | Spinal Muscular Atrophy | Cervical Spinal Cord Injury | Stroke, Lacunar | Paralysis; Stroke | Stroke Brainstem | Tetraplegic; Paralysis | Quadriplegia/TetraplegiaUnited States
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Scholar Rock, Inc.CompletedNeuromuscular Diseases | Neuromuscular Manifestations | Atrophy | Muscular Atrophy | Spinal Muscular Atrophy | Muscular Atrophy, Spinal | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type 2United States, Spain, Italy, Netherlands
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Scholar Rock, Inc.Active, not recruitingNeuromuscular Diseases | Neuromuscular Manifestations | Atrophy | Muscular Atrophy | Spinal Muscular Atrophy | Muscular Atrophy, Spinal | Spinal Muscular Atrophy Type 3 | SMA | Anti-myostatin | Spinal Muscular Atrophy Type IIUnited States, Spain, Belgium, Germany, Netherlands, Poland, Italy, France, United Kingdom