Search clinical trials for: Sandhoff disease
Total 382303 results
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SphinCS Lyso Gemeinnutzige UG (Haftungsbeschrankt)RecruitingGangliosidoses | Galactosialidosis | Sialidosis | GM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff Disease | Morquio B Disease | Gm2-Gangliosidosis, Variant B1 | GM2 Activator DeficiencyGermany
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Tehran University of Medical SciencesMashhad University of Medical Sciences; Kashan University of Medical SciencesRecruitingEffects of Miglustat Therapy on Infantile Type of Sandhoff and Taysachs Diseases (EMTISTD) (EMTISTD)Supportive Care | GM2 GangliosidosisIran, Islamic Republic of
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University of PittsburghRecruitingLysosomal Storage Diseases | Leukodystrophy | Niemann-Pick Diseases | Batten Disease | Gaucher Disease | Krabbe Disease | Alpha-Mannosidosis | Osteopetrosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | GM1 Gangliosidoses | MPS I | MPS II | Vanishing White Matter Disease | Multiple Sulfatase Deficiency... and other conditionsUnited States
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Joanne Kurtzberg, MDThe Marcus FoundationRecruitingMucopolysaccharidosis II | Brain Diseases, Metabolic, Inborn | Adrenoleukodystrophy | Batten Disease | Leukodystrophy, Metachromatic | Leukodystrophy, Globoid Cell | Alpha-Mannosidosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | Neimann Pick Disease | Sanfilippo MucopolysaccharidosesUnited States
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsRecruitingGM2 Gangliosidosis | GM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff Disease | Late Onset Tay-Sachs DiseaseUnited States
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National Human Genome Research Institute (NHGRI)RecruitingMyoclonus | Neurological Regression | Cherry Red Spot | Brain AtrophyUnited States
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IntraBio IncCompletedGM2 Gangliosidosis | Tay-Sachs Disease | Sandhoff DiseaseUnited States, Germany, Spain, United Kingdom
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Genzyme, a Sanofi CompanyActive, not recruitingTay-Sachs Disease | Sandhoff DiseaseUnited States, Argentina, Czechia, Portugal, Russian Federation, Turkey, United Kingdom, Brazil, France, Germany, Italy, Japan, Spain
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Terence FlotteMassachusetts General Hospital; University of Massachusetts, WorcesterActive, not recruitingTay-Sachs Disease | Sandhoff DiseaseUnited States
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Azafaros A.G.Active, not recruitingGM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff DiseaseUnited States, Brazil, France, Germany, Italy, United Kingdom
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Dr. Anupam SehgalTaysha Gene Therapies, Inc.; GlycoNetActive, not recruitingInfantile GM2 Gangliosidosis (Disorder)Canada
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Talaris Therapeutics Inc.Duke UniversityTerminatedNiemann-Pick Disease | Alpha-mannosidosis | Tay Sachs Disease | Sandhoff Disease | Metachromatic Leukodystrophy (MLD) | Hurler-Scheie Syndrome | Hurler Syndrome (MPS I) | Hunter Syndrome (MPS II) | Sanfilippo Syndrome (MPS III) | Krabbe Disease (Globoid Leukodystrophy) | Adrenoleukodystrophy (ALD and AMN) | Pelizaeus...United States
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Idorsia Pharmaceuticals Ltd.CompletedGM2 Gangliosidosis | GM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff Disease | Gaucher Disease, Type 2 | AB Variant Gangliosidosis GM2United States, Spain, Germany, Italy, Belgium, Brazil, France, Portugal, Switzerland, United Kingdom
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsTerminatedTay-Sachs Disease | Sandhoff Disease | GM1 Gangliosidoses | GM2 GangliosidosesUnited States
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Masonic Cancer Center, University of MinnesotaCompletedWolman Disease | Adrenoleukodystrophy | Metachromatic Leukodystrophy | Sanfilippo Syndrome | GM1 Gangliosidosis | Globoid Cell Leukodystrophy | Tay Sachs Disease | Sandhoffs Disease | I-Cell DiseaseUnited States
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Masonic Cancer Center, University of MinnesotaCompletedNiemann-Pick Disease | Wolman Disease | Adrenoleukodystrophy | Batten Disease | Metachromatic Leukodystrophy | GM1 Gangliosidosis | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Tay Sachs Disease | Sandhoff DiseaseUnited States
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Masonic Cancer Center, University of MinnesotaCompletedLysosomal Storage Disease | Peroxisomal DisorderUnited States
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Joanne Kurtzberg, MDAldagenWithdrawnLysosomal Storage Diseases | Inborn Errors of MetabolismUnited States
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The Hospital for Sick ChildrenActelionCompletedGangliosidoses GM2Canada
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedTay Sachs Disease | Sandhoff Disease | Late Onset Tay Sachs DiseaseUnited States
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AldagenTerminatedMucopolysaccharidosis | Inborn Errors of Metabolism | Lysosomal Storage Disorders | Inherited Metabolic Diseases | Peroxisomal Storage DiseasesUnited States
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Exsar CorporationThe Hospital for Sick Children; NYU Langone Health; University Hospitals Cleveland...WithdrawnG(M2) Ganglioside | Tay-Sachs Disease Ganglioside | Sandhoff Disease GangliosideUnited States, Canada
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The Hospital for Sick ChildrenCompletedGangliosidoses, GM2 | Tay-Sachs Disease | Sandhoff DiseaseCanada
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Children's National Research InstituteActelionCompletedSandhoff Disease | GM2 Gangliosidoses | Tay-SachsUnited States
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Manchester University NHS Foundation TrustNorth West Ambulance Service nhs foundation trustNot yet recruitingCardiac Arrest
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Pham Ngoc Thach University of MedicineRecruitingThe Incidence And Risk Factors Of Recurrent Febrile Seizures And Epilepsy Following Febrile SeizuresEpilepsy in Children | Febrile SeizuresVietnam
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Nanfang Hospital, Southern Medical UniversityNot yet recruitingGastrointestinal Disease
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University of ZurichRecruitingCerebrovascular Disorders | Quality of Life | Stress | Transient Ischemic Attack | Caregiver Burden | Sexual Behavior | Stroke, Acute | Intracerebral Hemorrhage | Incontinence, Urinary | Cortisol ExcessSwitzerland
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IRCCS San RaffaeleNot yet recruitingEosinophilic Esophagitis
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Meshalkin Research Institute of Pathology of CirculationRecruitingPain, Postoperative | Opioid Analgesic ConsumptionRussian Federation
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CHU de ReimsNot yet recruiting
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The Fourth Affiliated Hospital of Zhejiang University...Not yet recruitingRehabilitation | Cerebral Infarction | BiofeedbackChina
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Golden Jubilee National HospitalNot yet recruitingPulmonary Hypertension | InteroceptionUnited Kingdom
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Novartis PharmaceuticalsNot yet recruiting
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Mansoura UniversityNot yet recruitingPost-mastectomy Pain Syndrome
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Columbia UniversityNot yet recruiting
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Mohammad Farris Iman Leong Bin AbdullahNot yet recruitingInsomnia | Major Depressive Disorder
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Radboud University Medical CenterNot yet recruitingPheochromocytoma | Paraganglioma
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Hirabai Cowasji Jehangir Medical Research InstituteRecruiting
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Craig HospitalUniversity of Colorado, BoulderRecruitingCardiovascular Diseases | Endothelial Dysfunction | Spinal Cord InjuriesUnited States
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Association APPROCHESociété Neuradom; IMT Atlantique BrestRecruitingIschemic Stroke | Hemorrhagic Unilateral Cortico-subcortical Hemispheric StrokeFrance
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University of VermontEunice Kennedy Shriver National Institute of Child Health and Human Development...Not yet recruitingEmergencies | Infant Conditions | Child, Only | Infant Morbidity | Chronic Condition | Children With Medical Complexity | Utilization, Health CareUnited States
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San Diego State UniversityNot yet recruitingDehydration | Heat Stress
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University of Texas Southwestern Medical CenterNot yet recruiting
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WestatNational Institute on Drug Abuse (NIDA); Eunice Kennedy Shriver National Institute... and other collaboratorsNot yet recruiting
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Medical University of ViennaRecruitingSpeech Disorders | Assessment, Self | Measurement, Psychological StressAustria
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Alcon ResearchNot yet recruitingOcular RednessUnited States
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University of NairobiViiV Healthcare; Mylan LaboratoriesNot yet recruiting
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Shanghai Chest HospitalRecruitingNon Small Cell Lung CancerChina
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Miami Cancer Research Center, Inc.RecruitingThyroid Cancer | RAI-Refractory Thyroid CancerUnited States